Retroviral-mediated expression of beta-glucuronidase (GUSB) from autologous fibroblasts in mucopolysaccharidosis (MPS) VII dogs.

被引：0

作者：

Haskins, M ^{[1
]}

Polsky, A ^{[1
]}

Parente, M ^{[1
]}

Weil, M ^{[1
]}

Hasson, C ^{[1
]}

O'Malley, T ^{[1
]}

Sands, M ^{[1
]}

Harel, N ^{[1
]}

Reilly, J ^{[1
]}

Wang, P ^{[1
]}

Wolfe, J ^{[1
]}

机构：

[1] Univ Penn, Sch Vet Med, Philadelphia, PA 19104 USA

来源：

AMERICAN JOURNAL OF HUMAN GENETICS | 1997年 / 61卷 / 04期

关键词：

D O I：

暂无

中图分类号：

Q3 [遗传学];

学科分类号：

071007 ; 090102 ;

摘要：

2080

引用

页码：A355 / A355

页数：1

共 13 条

[1] Studies on the molecular basis of beta-glucuronidase deficiency in mucopolysaccharidosis-VII (MPS VII) in the retinal pigment epithelium
Ray, J
DeSanto, CM
Sun, W
Haskins, M
Aguirre, G
INVESTIGATIVE OPHTHALMOLOGY & VISUAL SCIENCE, 1996, 37 (03) : 1757 - 1757
[2] QUANTITATION AND BIOSYNTHESIS OF BETA-GLUCURONIDASE CROSS-REACTIVE MATERIAL IN FIBROBLASTS FROM PATIENTS WITH MUCOPOLYSACCHARIDOSIS-VII
SUKEGAWA, K
ORII, T
JOURNAL OF INHERITED METABOLIC DISEASE, 1985, 8 (03) : 145 - 146
[3] Decreased lysosomal storage in the adult MPS VII mouse brain in the vicinity of grafts of retroviral vector-corrected fibroblasts secreting high levels of beta-glucuronidase
Taylor, RM
Wolfe, JH
NATURE MEDICINE, 1997, 3 (07) : 771 - 774
[4] Neonatal delivery of a retroviral vector expressing canine β-glucuronidase results in long-term gene expression and marked improvement in the clinical manifestations in mucopolysaccharidosis VII dogs.
Xu, LF
Ponder, KP
Melniczek, JR
Weil, MA
Haskins, ME
BLOOD, 2001, 98 (11) : 693A - 693A
[5] In vitro retroviral vector-mediated transfer of the rat beta-glucuronidase cDNA into canine fetal liver cells and weanling MPS VII bone marrow cells
Casal, ML
Haskins, ME
Wolfe, JH
MOLECULAR BIOLOGY OF HEMATOPOIESIS 5, 1996, : 331 - 337
[6] Adenovirus-mediated gene transfer and expression of human beta-glucuronidase gene in the liver, spleen, and central nervous system in mucopolysaccharidosis type VII mice
Ohashi, T
Watabe, K
Uehara, K
Sly, WS
Vogler, C
Eto, Y
PROCEEDINGS OF THE NATIONAL ACADEMY OF SCIENCES OF THE UNITED STATES OF AMERICA, 1997, 94 (04) : 1287 - 1292
[7] TRANSPLANTATION OF BETA-GLUCURONIDASE (GUSB)-EXPRESSING IMMORTALIZED NEURAL PROGENITORS FOR GENE-TRANSFER INTO CNS OF THE MUCOPOLYSACCARIDOSIS (MPS) VII-MOUSE, A MODEL OF A NEUROVISCERAL LYSOSOMAL STORAGE DISEASE
SNYDER, EY
TAYLOR, RM
WOLFE, JH
JOURNAL OF CELLULAR BIOCHEMISTRY, 1994, : 246 - 246
[8] HERPESVIRUS VECTOR GENE-TRANSFER AND EXPRESSION OF BETA-GLUCURONIDASE IN THE CENTRAL-NERVOUS-SYSTEM OF MPS-VII MICE
WOLFE, JH
DESHMANE, SL
FRASER, NW
NATURE GENETICS, 1992, 1 (05) : 379 - 384
[9] HIGH-LEVEL EXPRESSION AND EXPORT OF BETA-GLUCURONIDASE FROM MURINE MUCOPOLYSACCHARIDOSIS-VII CELLS CORRECTED BY A DOUBLE-COPY RETROVIRUS VECTOR
WOLFE, JH
KYLE, JW
SANDS, MS
SLY, WS
MARKOWITZ, DG
PARENTE, MK
GENE THERAPY, 1995, 2 (01) : 70 - 78
[10] Hydrodynamic intravenous administration of naked DNA (Sleeping Beauty transposon) for expression of human beta-glucuronidase in a murine model of mucopolysaccharidosis type VII
Aronovich, EL
Belur, L
Bell, B
Liu, GY
Frandsen, JL
Gunther, R
Koniar, B
Erickson, DCC
Hackett, PB
McIvor, RS
Whitley, CB
MOLECULAR THERAPY, 2003, 7 (05) : S85 - S86

← 1 2 →