Activity of daily life in patients with Hunter syndrome: Impact of enzyme replacement therapy and hematopoietic stem cell transplantation

被引：0
作者：
Tomatsu, Shunji [1 ]
Tanjuakio, Julian [1 ]
Suzuki, Yasuyuki [2 ]
Patel, Pravin [1 ]
Yasuda, Eriko [1 ]
Kubaski, Francyne [1 ,3 ]
Mason, Robert W. [1 ]
Orii, Tadao [2 ]
机构：
[1] Nemours Alfred I duPont Hosp Children, Wilmington, DE USA
[2] Gifu Univ, Gifu, Japan
[3] Univ Delaware, Newark, DE USA
来源：
MOLECULAR GENETICS AND METABOLISM | 2015年 / 114卷 / 02期
关键词：
D O I：
10.1016/j.ymgme.2014.12.262
中图分类号：
R5 [内科学];
学科分类号：
1002 ; 100201 ;
摘要：
259
引用
收藏
页码：S115 / S115
页数：1
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