Development of Gene Transfer Technology

被引：3

作者：

Mulligan, Richard C. ^{[1
]}

机构：

[1] Harvard Univ, Sch Med, Dept Genet, Boston, MA 02115 USA

来源：

HUMAN GENE THERAPY | 2014年 / 25卷 / 12期

关键词：

HEMATOPOIETIC STEM-CELLS; BETA-GLOBIN GENE; RETROVIRUS PACKAGING CELLS; THYMIDINE KINASE GENE; LEUKEMIA-VIRUS; TRANSMISSIBLE RETROVIRUS; EXPRESSION; CONSTRUCTION; THERAPY; GENERATION;

D O I：

10.1089/hum.2014.2543

中图分类号：

Q81 [生物工程学（生物技术）]; Q93 [微生物学];

学科分类号：

071005 ; 0836 ; 090102 ; 100705 ;

摘要：

[No abstract available]

引用

页码：995 / 1002

页数：8

共 41 条

[1] Programmable ligand-controlled riboregulators of eukaryotic gene expression [J].

Bayer, TS ;

Smolke, CD .

NATURE BIOTECHNOLOGY, 2005, 23 (03) :337-343

[2] Safe mobilization of CD34+ cells in adults with β-thalassemia and validation of effective globin gene transfer for clinical investigation [J].

Boulad, Farid ;

Wang, Xiuyan ;

Qu, Jinrong ;

Taylor, Clare ;

Ferro, Leda ;

Karponi, Garyfalia ;

Bartido, Shirley ;

Giardina, Patricia ;

Heller, Glenn ;

Prockop, Susan E. ;

Maggio, Aurelio ;

Sadelain, Michel ;

Riviere, Isabelle .

BLOOD, 2014, 123 (10) :1483-1486

[3] Hematopoietic Stem Cell Gene Therapy: Progress on the Clinical Front [J].

Cavazzana, Marina .

HUMAN GENE THERAPY, 2014, 25 (03) :165-170

[4] Gene therapy of human severe combined immunodeficiency (SCID)-X1 disease [J].

Cavazzana-Calvo, M ;

Hacein-Bey, S ;

Basile, CD ;

Gross, F ;

Yvon, E ;

Nusbaum, P ;

Selz, F ;

Hue, C ;

Certain, S ;

Casanova, JL ;

Bousso, P ;

Le Deist, F ;

Fischer, A .

SCIENCE, 2000, 288 (5466) :669-672

[5] Transfusion independence and HMGA2 activation after gene therapy of human β-thalassaemia [J].

Cavazzana-Calvo, Marina ;

Payen, Emmanuel ;

Negre, Olivier ;

Wang, Gary ;

Hehir, Kathleen ;

Fusil, Floriane ;

Down, Julian ;

Denaro, Maria ;

Brady, Troy ;

Westerman, Karen ;

Cavallesco, Resy ;

Gillet-Legrand, Beatrix ;

Caccavelli, Laure ;

Sgarra, Riccardo ;

Maouche-Chretien, Leila ;

Bernaudin, Francoise ;

Girot, Robert ;

Dorazio, Ronald ;

Mulder, Geert-Jan ;

Polack, Axel ;

Bank, Arthur ;

Soulier, Jean ;

Larghero, Jerome ;

Kabbara, Nabil ;

Dalle, Bruno ;

Gourmel, Bernard ;

Socie, Gerard ;

Chretien, Stany ;

Cartier, Nathalie ;

Aubourg, Patrick ;

Fischer, Alain ;

Cornetta, Kenneth ;

Galacteros, Frederic ;

Beuzard, Yves ;

Gluckman, Eliane ;

Bushman, Frederick ;

Hacein-Bey-Abina, Salima ;

Leboulch, Philippe .

NATURE, 2010, 467 (7313) :318-U94

[6] REGULATED EXPRESSION OF A COMPLETE HUMAN BETA-GLOBIN GENE ENCODED BY A TRANSMISSIBLE RETROVIRUS VECTOR [J].

CONE, RD ;

WEBERBENAROUS, A ;

BAORTO, D ;

MULLIGAN, RC .

MOLECULAR AND CELLULAR BIOLOGY, 1987, 7 (02) :887-897

[7] SAFE AND EFFICIENT GENERATION OF RECOMBINANT RETROVIRUSES WITH AMPHOTROPIC AND ECOTROPIC HOST RANGES [J].

DANOS, O ;

MULLIGAN, RC .

PROCEEDINGS OF THE NATIONAL ACADEMY OF SCIENCES OF THE UNITED STATES OF AMERICA, 1988, 85 (17) :6460-6464

[8]

DRANOFF G, 1994, STEM CELLS, V12, P173

[9] VACCINATION WITH IRRADIATED TUMOR-CELLS ENGINEERED TO SECRETE MURINE GRANULOCYTE-MACROPHAGE COLONY-STIMULATING FACTOR STIMULATES POTENT, SPECIFIC, AND LONG-LASTING ANTITUMOR IMMUNITY [J].

DRANOFF, G ;

JAFFEE, E ;

LAZENBY, A ;

GOLUMBEK, P ;

LEVITSKY, H ;

BROSE, K ;

JACKSON, V ;

HAMADA, H ;

PARDOLL, D ;

MULLIGAN, RC .

PROCEEDINGS OF THE NATIONAL ACADEMY OF SCIENCES OF THE UNITED STATES OF AMERICA, 1993, 90 (08) :3539-3543

[10] LINEAGE-SPECIFIC EXPRESSION OF A HUMAN BETA-GLOBIN GENE IN MURINE BONE-MARROW TRANSPLANT RECIPIENTS RECONSTITUTED WITH RETROVIRUS-TRANSDUCED STEM-CELLS [J].

DZIERZAK, EA ;

PAPAYANNOPOULOU, T ;

MULLIGAN, RC .

NATURE, 1988, 331 (6151) :35-41

← 1 2 3 4 5 →