[1] Amer Univ Beirut, Med Ctr, Dept Internal Med, Beirut, Lebanon
[2] Mahidol Univ, Siriraj Hosp, Bangkok, Thailand
[3] Univ Paris, Imagine Inst, INSERM, U1163, Paris, France
[4] Hop Necker Enfants Malad, Assistance Publ Hop Paris, Dept Hematol, Paris, France
[5] UCL, Univ Coll London Hosp, London, England
[6] Univ Turin, Dept Clin & Biol Sci, Turin, Italy
[7] Univ Toronto, Univ Hlth Network, Div Med Oncol & Hematol, Div Hematol, Toronto, ON, Canada
[8] Childrens Hosp Los Angeles, Childrens Ctr Canc & Blood Dis, Los Angeles, CA 90027 USA
[9] USC Keck Sch Med, Los Angeles, CA USA
[10] Laikon Gen Hosp, Thalassemia & Sickle Cell Ctr, Athens, Greece
[11] Sousse Univ, Farhat Hached Teaching Hosp, Sousse, Tunisia
[12] Natl & Kapodistrian Univ Athens, Dept Pediat 1, Athens, Greece
[13] Celgene Int Sarl, Boudry, Switzerland
[14] Bristol Myers Squibb, Princeton, NJ USA
[15] Acceleron Pharma, Cambridge, MA USA
[16] Univ Milan, Fdn IRCCS Ca Granda Policlin Hosp, Milan, Italy