Unconditioned unrelated donor bone marrow transplantation for IL7Rα- and Artemis-deficient SCID

被引:9
作者
Dvorak, C. C. [1 ]
Patel, K. [1 ]
Puck, J. M. [1 ]
Wahlstrom, J. [1 ]
Dorsey, M. J. [1 ]
Adams, R. [2 ]
Facchino, J. [1 ]
Cowan, M. J. [1 ]
机构
[1] Univ Calif San Francisco, Dept Pediat, Div Pediat Allergy Immunol & Bone Marrow Transpla, Benioff Childrens Hosp, San Francisco, CA 94143 USA
[2] Phoenix Childrens Hosp, Ctr Canc & Blood Disorders, Blood & Marrow Transplantat Div, Phoenix, AZ USA
关键词
SEVERE COMBINED IMMUNODEFICIENCY; CELL TRANSPLANTATION; OUTCOMES; RECONSTITUTION; ALEMTUZUMAB; DISEASE;
D O I
10.1038/bmt.2017.74
中图分类号
Q6 [生物物理学];
学科分类号
071011 ;
摘要
引用
收藏
页码:1036 / 1038
页数:3
相关论文
共 11 条
  • [1] Post-Transplantation B Cell Function in Different Molecular Types of SCID
    Buckley, Rebecca H.
    Win, Chan M.
    Moser, Barry K.
    Parrott, Roberta E.
    Sajaroff, Elisa
    Sarzotti-Kelsoe, Marcella
    [J]. JOURNAL OF CLINICAL IMMUNOLOGY, 2013, 33 (01) : 96 - 110
  • [2] Transplantation of hematopoietic stem cells in human severe combined immunodeficiency: longterm outcomes
    Buckley, Rebecca H.
    [J]. IMMUNOLOGIC RESEARCH, 2011, 49 (1-3) : 25 - 43
  • [3] Megadose CD34+ cell grafts improve recovery of T cell engraftment but not B cell immunity in patients with severe combined immunodeficiency disease undergoing haplocompatible nonmyeloablative transplantation
    Dvorak, Christopher C.
    Hung, Giun-Yi
    Horn, Biljana
    Dunn, Elizabeth
    Oon, Ching-Ying
    Cowan, Morton J.
    [J]. BIOLOGY OF BLOOD AND MARROW TRANSPLANTATION, 2008, 14 (10) : 1125 - 1133
  • [4] Comparison of outcomes of hematopoietic stem cell transplantation without chemotherapy conditioning by using matched sibling and unrelated donors for treatment of severe combined immunodeficiency
    Dvorak, Christopher C.
    Hassan, Amel
    Slatter, Mary A.
    Hoenig, Manfred
    Lankester, Arjan C.
    Buckley, Rebecca H.
    Pulsipher, Michael A.
    Davis, Jeffrey H.
    Guengoer, Tayfun
    Gabriel, Melissa
    Bleesing, Jacob H.
    Bunin, Nancy
    Sedlacek, Petr
    Connell, James A.
    Crawford, David F.
    Notarangelo, Luigi D.
    Pai, Sung-Yun
    Hassid, Jake
    Veys, Paul
    Gennery, Andrew R.
    Cowan, Morton J.
    [J]. JOURNAL OF ALLERGY AND CLINICAL IMMUNOLOGY, 2014, 134 (04) : 935 - U263
  • [5] A trial of alemtuzumab adjunctive therapy in allogeneic hematopoietic cell transplantation with minimal conditioning for severe combined immunodeficiency
    Dvorak, Christopher C.
    Horn, Biljana N.
    Puck, Jennifer M.
    Adams, Stuart
    Veys, Paul
    Czechowicz, Agnieszka
    Cowan, Morton J.
    [J]. PEDIATRIC TRANSPLANTATION, 2014, 18 (06) : 609 - 616
  • [6] B-cell reconstitution for SCID: Should a conditioning regimen be used in SCID treatment?
    Haddad, Elie
    Leroy, Sandrine
    Buckley, Rebecca H.
    [J]. JOURNAL OF ALLERGY AND CLINICAL IMMUNOLOGY, 2013, 131 (04) : 994 - 1000
  • [7] Transplantation Outcomes for Severe Combined Immunodeficiency, 2000-2009
    Pai, Sung-Yun
    Logan, Brent R.
    Griffith, Linda M.
    Buckley, Rebecca H.
    Parrott, Roberta E.
    Dvorak, Christopher C.
    Kapoor, Neena
    Hanson, Imelda C.
    Filipovich, Alexandra H.
    Jyonouchi, Soma
    Sullivan, Kathleen E.
    Small, Trudy N.
    Burroughs, Lauri
    Skoda-Smith, Suzanne
    Haight, Ann E.
    Grizzle, Audrey
    Pulsipher, Michael A.
    Chan, Ka Wah
    Fuleihan, Ramsay L.
    Haddad, Elie
    Loechelt, Brett
    Aquino, Victor M.
    Gillio, Alfred
    Davis, Jeffrey
    Knutsen, Alan
    Smith, Angela R.
    Moore, Theodore B.
    Schroeder, Marlis L.
    Goldman, Frederick D.
    Connelly, James A.
    Porteus, Matthew H.
    Xiang, Qun
    Shearer, William T.
    Fleisher, Thomas A.
    Kohn, Donald B.
    Puck, Jennifer M.
    Notarangelo, Luigi D.
    Cowan, Morton J.
    O'Reilly, Richard J.
    [J]. NEW ENGLAND JOURNAL OF MEDICINE, 2014, 371 (05) : 434 - 446
  • [8] SCID patients with ARTEMIS vs RAG deficiencies following HCT: increased risk of late toxicity in ARTEMIS-deficient SCID
    Schuetz, Catharina
    Neven, Benedicte
    Dvorak, Christopher C.
    Leroy, Sandrine
    Ege, Markus J.
    Pannicke, Ulrich
    Schwarz, Klaus
    Schulz, Ansgar S.
    Hoenig, Manfred
    Sparber-Sauer, Monika
    Gatz, Susanne A.
    Denzer, Christian
    Blanche, Stephane
    Moshous, Despina
    Picard, Capucine
    Horn, Biljana N.
    de Villartay, Jean-Pierre
    Cavazzana, Marina
    Debatin, Klaus-Michael
    Friedrich, Wilhelm
    Fischer, Alain
    Cowan, Morton J.
    [J]. BLOOD, 2014, 123 (02) : 281 - 289
  • [9] Establishing diagnostic criteria for severe combined immunodeficiency disease (SCID), leaky SCID, and Omenn syndrome: The Primary Immune Deficiency Treatment Consortium experience
    Shearer, William T.
    Dunn, Elizabeth
    Notarangelo, Luigi D.
    Dvorak, Christopher C.
    Puck, Jennifer M.
    Logan, Brent R.
    Griffith, Linda M.
    Kohn, Donald B.
    O'Reilly, Richard J.
    Fleisher, Thomas A.
    Pai, Sung-Yun
    Martinez, Caridad A.
    Buckley, Rebecca H.
    Cowan, Morton J.
    [J]. JOURNAL OF ALLERGY AND CLINICAL IMMUNOLOGY, 2014, 133 (04) : 1092 - 1098
  • [10] Targeting of Natural Killer Cells by Rabbit Antithymocyte Globulin and Campath-1H: Similar Effects Independent of Specificity
    Stauch, Diana
    Dernier, Annelie
    Marchese, Elizabeth Sarmiento
    Kunert, Kristina
    Volk, Hans-Dieter
    Pratschke, Johann
    Kotsch, Katja
    [J]. PLOS ONE, 2009, 4 (03):