Safety and Efficacy Evaluation for an Ex Vivo Selection Free CRISPR/Cas9 Based Gene Therapy for HAX1 Associated Congenital Neutropenia

被引：0

作者：

Ritter, Malte Ulrich ^{[1
]}

Nasri, Masoud ^{[1
]}

Dannenmann, Benjamin ^{[1
]}

Kaufmann, Masako Monika ^{[2
]}

Zeidler, Karl Alexander ^{[3
]}

Secker, Benjamin ^{[1
]}

Amend, Diana ^{[1
]}

Haaf, Jeremy ^{[1
]}

Zeidler, Cornelia ^{[4
]}

Kliminakou, Maksim ^{[1
]}

Cathomen, Toni ^{[2
]}

Welte, Karl Heinirch ^{[5
]}

Skokowa, Julia ^{[1
]}

机构：

[1] Univ Klinikum Tuebingen, Translat Onkol, Innere Med 2, Tubingen, Germany

[2] Univ Freiburg Klinikum, Inst Transfus Med & Gene Therapy, Freiburg, Germany

[3] Univ Klinikum Tuebingen, Allgemeine Padiatrie Haematol & Onkol, Kinderheilkunde 1, Tubingen, Germany

[4] Hannover Med Sch, Abt Mol Hamatopoese, Klin Padiat Hamatol & Onkol, Hannover, Germany

[5] Univ Klinikum Tuebingen, Mol Haematopoese, Kinderheilkunde 1, Tubingen, Germany

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D O I：

暂无

中图分类号：

Q81 [生物工程学（生物技术）]; Q93 [微生物学];

学科分类号：

071005 ; 0836 ; 090102 ; 100705 ;

摘要：

361

引用

页码：172 / 172

页数：1