Outrageous prices of orphan drugs: a call for collaboration

被引：121

作者：

Luzzatto, Lucio ^{[1
]}

Hyry, Hanna I. ^{[2
]}

Schieppati, Arrigo ^{[3
]}

Costa, Enrico ^{[4
]}

Simoens, Steven ^{[5
]}

Schaefer, Franz ^{[6
]}

Roos, Jonathan C. P. ^{[2
]}

Merlini, Giampaolo ^{[7
]}

Kaariainen, Helena ^{[8
]}

Garattini, Silvio ^{[9
]}

Hollak, Carla E. ^{[10
]}

Remuzzi, Giuseppe ^{[11
,12
,13
]}

机构：

[1] Muhimbili Univ Hlth & Allied Sci, Dar Es Salaam, Tanzania

[2] Univ Cambridge, Dept Med, Cambridge, England

[3] Azienda Sociosanit Terr Papa Giovanni XXIII, Rare Dis Unit, Bergamo, Italy

[4] Azienda Osped Univ Integrata, Osped Policlin GB Rossi, Serv Pharm, Verona, Italy

[5] Katholieke Univ Leuven, Dept Pharmaceut & Pharmacol Sci, Leuven, Belgium

[6] Heidelberg Univ, Ctr Pediat & Adolescent Med, Pediat Nephrol Div, Heidelberg, Germany

[7] Univ Pavia, Fdn IRCCS Policlin San Matteo, Dept Mol Med, Pavia, Italy

[8] Natl Inst Hlth & Welf, Genom & Biomarkers Unit, Helsinki, Finland

[9] IRCCS Ist Ric Farmacol Mario Negri, Milan, Italy

[10] Acad Med Ctr, Dept Endocrinol & Metab, Amsterdam, Netherlands

[11] IRCCS Ist Ric Farmacol Mario Negri, I-24126 Bergamo, Italy

[12] Azienda Sociosanit Terr Papa Giovanni XXIII, Unit Nephrol & Dialysis, Bergamo, Italy

[13] Univ Milan, Dept Biomed & Clin Sci, Milan, Italy

来源：

关键词：

RARE DISEASES; CANCERS;

D O I：

10.1016/S0140-6736(18)31069-9

中图分类号：

R5 [内科学];

学科分类号：

1002 ; 100201 ;

摘要：

引用

页码：791 / 794

页数：4

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