共 29 条
[1]
Suppressing transthyretin production in mice, monkeys and humans using 2nd-Generation antisense oligonucleotides
[J].
Ackermann, Elizabeth J.
;
Guo, Shuling
;
Benson, Merrill D.
;
Booten, Sheri
;
Freier, Sue
;
Hughes, Steven G.
;
Kim, Tae-Won
;
Kwoh, T. Jesse
;
Matson, John
;
Norris, Dan
;
Yu, Rosie
;
Watt, Andy
;
Monia, Brett P.
.
AMYLOID-JOURNAL OF PROTEIN FOLDING DISORDERS,
2016, 23 (03)
:148-157

Ackermann, Elizabeth J.
论文数: 0 引用数: 0
h-index: 0
机构:
Ionis Pharmaceut, 2855 Gazelle Court, Carlsbad, CA 92010 USA Ionis Pharmaceut, 2855 Gazelle Court, Carlsbad, CA 92010 USA

Guo, Shuling
论文数: 0 引用数: 0
h-index: 0
机构:
Ionis Pharmaceut, 2855 Gazelle Court, Carlsbad, CA 92010 USA Ionis Pharmaceut, 2855 Gazelle Court, Carlsbad, CA 92010 USA

Benson, Merrill D.
论文数: 0 引用数: 0
h-index: 0
机构:
Indiana Univ Sch Med, Dept Pathol & Lab Med, Indianapolis, IN 46202 USA Ionis Pharmaceut, 2855 Gazelle Court, Carlsbad, CA 92010 USA

Booten, Sheri
论文数: 0 引用数: 0
h-index: 0
机构:
Ionis Pharmaceut, 2855 Gazelle Court, Carlsbad, CA 92010 USA Ionis Pharmaceut, 2855 Gazelle Court, Carlsbad, CA 92010 USA

Freier, Sue
论文数: 0 引用数: 0
h-index: 0
机构:
Ionis Pharmaceut, 2855 Gazelle Court, Carlsbad, CA 92010 USA Ionis Pharmaceut, 2855 Gazelle Court, Carlsbad, CA 92010 USA

Hughes, Steven G.
论文数: 0 引用数: 0
h-index: 0
机构:
Ionis Pharmaceut, 2855 Gazelle Court, Carlsbad, CA 92010 USA Ionis Pharmaceut, 2855 Gazelle Court, Carlsbad, CA 92010 USA

Kim, Tae-Won
论文数: 0 引用数: 0
h-index: 0
机构:
Ionis Pharmaceut, 2855 Gazelle Court, Carlsbad, CA 92010 USA Ionis Pharmaceut, 2855 Gazelle Court, Carlsbad, CA 92010 USA

Kwoh, T. Jesse
论文数: 0 引用数: 0
h-index: 0
机构:
Ionis Pharmaceut, 2855 Gazelle Court, Carlsbad, CA 92010 USA Ionis Pharmaceut, 2855 Gazelle Court, Carlsbad, CA 92010 USA

Matson, John
论文数: 0 引用数: 0
h-index: 0
机构:
Ionis Pharmaceut, 2855 Gazelle Court, Carlsbad, CA 92010 USA Ionis Pharmaceut, 2855 Gazelle Court, Carlsbad, CA 92010 USA

Norris, Dan
论文数: 0 引用数: 0
h-index: 0
机构:
Ionis Pharmaceut, 2855 Gazelle Court, Carlsbad, CA 92010 USA Ionis Pharmaceut, 2855 Gazelle Court, Carlsbad, CA 92010 USA

Yu, Rosie
论文数: 0 引用数: 0
h-index: 0
机构:
Ionis Pharmaceut, 2855 Gazelle Court, Carlsbad, CA 92010 USA Ionis Pharmaceut, 2855 Gazelle Court, Carlsbad, CA 92010 USA

Watt, Andy
论文数: 0 引用数: 0
h-index: 0
机构:
Ionis Pharmaceut, 2855 Gazelle Court, Carlsbad, CA 92010 USA Ionis Pharmaceut, 2855 Gazelle Court, Carlsbad, CA 92010 USA

Monia, Brett P.
论文数: 0 引用数: 0
h-index: 0
机构:
Ionis Pharmaceut, 2855 Gazelle Court, Carlsbad, CA 92010 USA Ionis Pharmaceut, 2855 Gazelle Court, Carlsbad, CA 92010 USA
[2]
Patisiran, an RNAi Therapeutic, for Hereditary Transthyretin Amyloidosis
[J].
Adams, D.
;
Gonzalez-Duarte, A.
;
O'Riordan, W. D.
;
Yang, C. -C.
;
Ueda, M.
;
Kristen, A. V.
;
Tournev, I.
;
Schmidt, H. H.
;
Coelho, T.
;
Berk, J. L.
;
Lin, K. -P.
;
Vita, G.
;
Attarian, S.
;
Plante-Bordeneuve, V.
;
Mezei, M. M.
;
Campistol, J. M.
;
Buades, J.
;
Brannagan, T. H., III
;
Kim, B. J.
;
Oh, J.
;
Parman, Y.
;
Sekijima, Y.
;
Hawkins, P. N.
;
Solomon, S. D.
;
Polydefkis, M.
;
Dyck, P. J.
;
Gandhi, P. J.
;
Goyal, S.
;
Chen, J.
;
Strahs, A. L.
;
Nochur, S. V.
;
Sweetser, M. T.
;
Garg, P. P.
;
Vaishnaw, A. K.
;
Gollob, J. A.
;
Suhr, O. B.
.
NEW ENGLAND JOURNAL OF MEDICINE,
2018, 379 (01)
:11-21

Adams, D.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Paris Sud, CHU Bicetre, AP HP, INSERM Unite 1195,Natl Reference Ctr Familial Amy, Le Kremlin Bicetre, France Univ Paris Sud, CHU Bicetre, AP HP, INSERM Unite 1195,Natl Reference Ctr Familial Amy, Le Kremlin Bicetre, France

Gonzalez-Duarte, A.
论文数: 0 引用数: 0
h-index: 0
机构:
Natl Inst Med Sci & Nutr Salvador Zubiran, Mexico City, DF, Mexico Univ Paris Sud, CHU Bicetre, AP HP, INSERM Unite 1195,Natl Reference Ctr Familial Amy, Le Kremlin Bicetre, France

O'Riordan, W. D.
论文数: 0 引用数: 0
h-index: 0
机构:
eStudySite, Dept Clin Res, San Diego, CA USA Univ Paris Sud, CHU Bicetre, AP HP, INSERM Unite 1195,Natl Reference Ctr Familial Amy, Le Kremlin Bicetre, France

Yang, C. -C.
论文数: 0 引用数: 0
h-index: 0
机构:
Natl Taiwan Univ Hosp, Dept Neurol, Taipei, Taiwan Univ Paris Sud, CHU Bicetre, AP HP, INSERM Unite 1195,Natl Reference Ctr Familial Amy, Le Kremlin Bicetre, France

Ueda, M.
论文数: 0 引用数: 0
h-index: 0
机构: Univ Paris Sud, CHU Bicetre, AP HP, INSERM Unite 1195,Natl Reference Ctr Familial Amy, Le Kremlin Bicetre, France

Kristen, A. V.
论文数: 0 引用数: 0
h-index: 0
机构:
Heidelberg Univ, Dept Cardiol, Heidelberg, Germany Univ Paris Sud, CHU Bicetre, AP HP, INSERM Unite 1195,Natl Reference Ctr Familial Amy, Le Kremlin Bicetre, France

Tournev, I.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Multiprofile Hosp Act Treatment, Sofia, Bulgaria Univ Paris Sud, CHU Bicetre, AP HP, INSERM Unite 1195,Natl Reference Ctr Familial Amy, Le Kremlin Bicetre, France

Schmidt, H. H.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Klinikum Munster, Med Klin B Gastroenterol & Hepatol, Munster, Germany Univ Paris Sud, CHU Bicetre, AP HP, INSERM Unite 1195,Natl Reference Ctr Familial Amy, Le Kremlin Bicetre, France

Coelho, T.
论文数: 0 引用数: 0
h-index: 0
机构:
Hosp Santo Antonio, Ctr Hosp Porto, Porto, Portugal Univ Paris Sud, CHU Bicetre, AP HP, INSERM Unite 1195,Natl Reference Ctr Familial Amy, Le Kremlin Bicetre, France

Berk, J. L.
论文数: 0 引用数: 0
h-index: 0
机构:
Boston Med Ctr, Dept Med, Amyloidosis Ctr, Boston, MA USA Univ Paris Sud, CHU Bicetre, AP HP, INSERM Unite 1195,Natl Reference Ctr Familial Amy, Le Kremlin Bicetre, France

Lin, K. -P.
论文数: 0 引用数: 0
h-index: 0
机构:
Taipei Vet Gen Hosp, Dept Neurol, Taipei, Taiwan Univ Paris Sud, CHU Bicetre, AP HP, INSERM Unite 1195,Natl Reference Ctr Familial Amy, Le Kremlin Bicetre, France

Vita, G.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Hosp Messina, Dept Clin & Expt Med, Messina, Italy Univ Paris Sud, CHU Bicetre, AP HP, INSERM Unite 1195,Natl Reference Ctr Familial Amy, Le Kremlin Bicetre, France

Attarian, S.
论文数: 0 引用数: 0
h-index: 0
机构:
Hop La Timone, Dept Neuromuscular Disorders & ALS, Marseille, France Univ Paris Sud, CHU Bicetre, AP HP, INSERM Unite 1195,Natl Reference Ctr Familial Amy, Le Kremlin Bicetre, France

Plante-Bordeneuve, V.
论文数: 0 引用数: 0
h-index: 0
机构:
CHU Henri Mondor, AP HP, Amyloid Network, Dept Neurol, Creteil, France Univ Paris Sud, CHU Bicetre, AP HP, INSERM Unite 1195,Natl Reference Ctr Familial Amy, Le Kremlin Bicetre, France

Mezei, M. M.
论文数: 0 引用数: 0
h-index: 0
机构:
Vancouver Gen Hosp, Dept Neurol, Vancouver, BC, Canada
Vancouver Gen Hosp, Dept Med, Vancouver, BC, Canada Univ Paris Sud, CHU Bicetre, AP HP, INSERM Unite 1195,Natl Reference Ctr Familial Amy, Le Kremlin Bicetre, France

Campistol, J. M.
论文数: 0 引用数: 0
h-index: 0
机构:
Hosp Clin Barcelona, Dept Nephrol, Barcelona, Spain Univ Paris Sud, CHU Bicetre, AP HP, INSERM Unite 1195,Natl Reference Ctr Familial Amy, Le Kremlin Bicetre, France

Buades, J.
论文数: 0 引用数: 0
h-index: 0
机构:
Balear Isl Hlth Res Inst, Palma de Mallorca, Spain
Hosp Son Llatzer, Palma de Mallorca, Spain Univ Paris Sud, CHU Bicetre, AP HP, INSERM Unite 1195,Natl Reference Ctr Familial Amy, Le Kremlin Bicetre, France

Brannagan, T. H., III
论文数: 0 引用数: 0
h-index: 0
机构:
Columbia Univ, Dept Neurol, Coll Phys & Surg, New York, NY USA Univ Paris Sud, CHU Bicetre, AP HP, INSERM Unite 1195,Natl Reference Ctr Familial Amy, Le Kremlin Bicetre, France

Kim, B. J.
论文数: 0 引用数: 0
h-index: 0
机构:
Sungkyunkwan Univ, Sch Med, Samsung Med Ctr, Seoul, South Korea Univ Paris Sud, CHU Bicetre, AP HP, INSERM Unite 1195,Natl Reference Ctr Familial Amy, Le Kremlin Bicetre, France

Oh, J.
论文数: 0 引用数: 0
h-index: 0
机构:
Konkuk Univ, Med Ctr, Dept Neurol, Seoul, South Korea Univ Paris Sud, CHU Bicetre, AP HP, INSERM Unite 1195,Natl Reference Ctr Familial Amy, Le Kremlin Bicetre, France

Parman, Y.
论文数: 0 引用数: 0
h-index: 0
机构:
Istanbul Univ, Dept Neurol, Istanbul, Turkey Univ Paris Sud, CHU Bicetre, AP HP, INSERM Unite 1195,Natl Reference Ctr Familial Amy, Le Kremlin Bicetre, France

Sekijima, Y.
论文数: 0 引用数: 0
h-index: 0
机构:
Shinshu Univ, Dept Med Neurol & Rheumatol, Matsumoto, Nagano, Japan Univ Paris Sud, CHU Bicetre, AP HP, INSERM Unite 1195,Natl Reference Ctr Familial Amy, Le Kremlin Bicetre, France

Hawkins, P. N.
论文数: 0 引用数: 0
h-index: 0
机构:
UCL, Div Med, London, England Univ Paris Sud, CHU Bicetre, AP HP, INSERM Unite 1195,Natl Reference Ctr Familial Amy, Le Kremlin Bicetre, France

Solomon, S. D.
论文数: 0 引用数: 0
h-index: 0
机构:
Harvard Med Sch, Boston, MA USA Univ Paris Sud, CHU Bicetre, AP HP, INSERM Unite 1195,Natl Reference Ctr Familial Amy, Le Kremlin Bicetre, France

Polydefkis, M.
论文数: 0 引用数: 0
h-index: 0
机构:
Johns Hopkins Bayview Med Ctr Baltimore, Baltimore, MD USA Univ Paris Sud, CHU Bicetre, AP HP, INSERM Unite 1195,Natl Reference Ctr Familial Amy, Le Kremlin Bicetre, France

Dyck, P. J.
论文数: 0 引用数: 0
h-index: 0
机构:
Mayo Clin, Dept Neurol, Rochester, MN USA Univ Paris Sud, CHU Bicetre, AP HP, INSERM Unite 1195,Natl Reference Ctr Familial Amy, Le Kremlin Bicetre, France

Gandhi, P. J.
论文数: 0 引用数: 0
h-index: 0
机构:
Alnylam Pharmaceut, Cambridge, MA USA Univ Paris Sud, CHU Bicetre, AP HP, INSERM Unite 1195,Natl Reference Ctr Familial Amy, Le Kremlin Bicetre, France

Goyal, S.
论文数: 0 引用数: 0
h-index: 0
机构:
Alnylam Pharmaceut, Cambridge, MA USA Univ Paris Sud, CHU Bicetre, AP HP, INSERM Unite 1195,Natl Reference Ctr Familial Amy, Le Kremlin Bicetre, France

Chen, J.
论文数: 0 引用数: 0
h-index: 0
机构:
Alnylam Pharmaceut, Cambridge, MA USA Univ Paris Sud, CHU Bicetre, AP HP, INSERM Unite 1195,Natl Reference Ctr Familial Amy, Le Kremlin Bicetre, France

Strahs, A. L.
论文数: 0 引用数: 0
h-index: 0
机构:
Alnylam Pharmaceut, Cambridge, MA USA Univ Paris Sud, CHU Bicetre, AP HP, INSERM Unite 1195,Natl Reference Ctr Familial Amy, Le Kremlin Bicetre, France

Nochur, S. V.
论文数: 0 引用数: 0
h-index: 0
机构:
Alnylam Pharmaceut, Cambridge, MA USA Univ Paris Sud, CHU Bicetre, AP HP, INSERM Unite 1195,Natl Reference Ctr Familial Amy, Le Kremlin Bicetre, France

Sweetser, M. T.
论文数: 0 引用数: 0
h-index: 0
机构:
Alnylam Pharmaceut, Cambridge, MA USA Univ Paris Sud, CHU Bicetre, AP HP, INSERM Unite 1195,Natl Reference Ctr Familial Amy, Le Kremlin Bicetre, France

Garg, P. P.
论文数: 0 引用数: 0
h-index: 0
机构:
Alnylam Pharmaceut, Cambridge, MA USA Univ Paris Sud, CHU Bicetre, AP HP, INSERM Unite 1195,Natl Reference Ctr Familial Amy, Le Kremlin Bicetre, France

Vaishnaw, A. K.
论文数: 0 引用数: 0
h-index: 0
机构:
Alnylam Pharmaceut, Cambridge, MA USA Univ Paris Sud, CHU Bicetre, AP HP, INSERM Unite 1195,Natl Reference Ctr Familial Amy, Le Kremlin Bicetre, France

Gollob, J. A.
论文数: 0 引用数: 0
h-index: 0
机构:
Alnylam Pharmaceut, Cambridge, MA USA Univ Paris Sud, CHU Bicetre, AP HP, INSERM Unite 1195,Natl Reference Ctr Familial Amy, Le Kremlin Bicetre, France

Suhr, O. B.
论文数: 0 引用数: 0
h-index: 0
机构:
Umea Univ, Dept Publ Hlth & Clin Med, Umea, Sweden Univ Paris Sud, CHU Bicetre, AP HP, INSERM Unite 1195,Natl Reference Ctr Familial Amy, Le Kremlin Bicetre, France
[3]
ALBERS JW, 1995, ANN NEUROL, V38, P478
[4]
Novel pharmacotherapies for cardiac amyloidosis
[J].
Alexander, Kevin M.
;
Singh, Avinainder
;
Falk, Rodney H.
.
PHARMACOLOGY & THERAPEUTICS,
2017, 180
:129-138

Alexander, Kevin M.
论文数: 0 引用数: 0
h-index: 0
机构:
Harvard Med Sch, Cardiac Amyloidosis Program, Div Cardiol, Dept Med,Heart & Vasc Ctr,Brigham & Womens Hosp, Boston, MA USA Harvard Med Sch, Cardiac Amyloidosis Program, Div Cardiol, Dept Med,Heart & Vasc Ctr,Brigham & Womens Hosp, Boston, MA USA

Singh, Avinainder
论文数: 0 引用数: 0
h-index: 0
机构:
Harvard Med Sch, Cardiac Amyloidosis Program, Div Cardiol, Dept Med,Heart & Vasc Ctr,Brigham & Womens Hosp, Boston, MA USA Harvard Med Sch, Cardiac Amyloidosis Program, Div Cardiol, Dept Med,Heart & Vasc Ctr,Brigham & Womens Hosp, Boston, MA USA

Falk, Rodney H.
论文数: 0 引用数: 0
h-index: 0
机构:
Harvard Med Sch, Cardiac Amyloidosis Program, Div Cardiol, Dept Med,Heart & Vasc Ctr,Brigham & Womens Hosp, Boston, MA USA Harvard Med Sch, Cardiac Amyloidosis Program, Div Cardiol, Dept Med,Heart & Vasc Ctr,Brigham & Womens Hosp, Boston, MA USA
[5]
Guideline of transthyretin-related hereditary amyloidosis for clinicians
[J].
Ando, Yukio
;
Coelho, Teresa
;
Berk, John L.
;
Cruz, Marcia Waddington
;
Ericzon, Bo-Goran
;
Ikeda, Shu-ichi
;
Lewis, W. David
;
Obici, Laura
;
Plante-Bordeneuve, Violaine
;
Rapezzi, Claudio
;
Said, Gerard
;
Salvi, Fabrizio
.
ORPHANET JOURNAL OF RARE DISEASES,
2013, 8

Ando, Yukio
论文数: 0 引用数: 0
h-index: 0
机构:
Kumamoto Univ, Grad Sch Med Sci, Dept Neurol, Chuo Ku, Kumamoto 8608556, Japan
Kumamoto Univ, Grad Sch Med Sci, Dept Neurol, Kumamoto 8600811, Japan Kumamoto Univ, Grad Sch Med Sci, Dept Neurol, Chuo Ku, Kumamoto 8608556, Japan

Coelho, Teresa
论文数: 0 引用数: 0
h-index: 0
机构:
Hosp Santo Antonio, Dept Neurol, Oporto, Portugal Kumamoto Univ, Grad Sch Med Sci, Dept Neurol, Chuo Ku, Kumamoto 8608556, Japan

Berk, John L.
论文数: 0 引用数: 0
h-index: 0
机构:
Boston Univ, Dept Med, Amyloid Treatment & Res Program, Boston, MA 02215 USA Kumamoto Univ, Grad Sch Med Sci, Dept Neurol, Chuo Ku, Kumamoto 8608556, Japan

Cruz, Marcia Waddington
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Fed Rio de Janeiro, Hosp Univ Clementino Fraga Filho, Dept Neurol, Rio De Janeiro, Brazil Kumamoto Univ, Grad Sch Med Sci, Dept Neurol, Chuo Ku, Kumamoto 8608556, Japan

Ericzon, Bo-Goran
论文数: 0 引用数: 0
h-index: 0
机构:
Karolinska Univ Hosp, Div Transplantat Surg, Stockholm, Sweden Kumamoto Univ, Grad Sch Med Sci, Dept Neurol, Chuo Ku, Kumamoto 8608556, Japan

Ikeda, Shu-ichi
论文数: 0 引用数: 0
h-index: 0
机构:
Shinshu Univ, Dept Med, Matsumoto, Nagano 390, Japan Kumamoto Univ, Grad Sch Med Sci, Dept Neurol, Chuo Ku, Kumamoto 8608556, Japan

Lewis, W. David
论文数: 0 引用数: 0
h-index: 0
机构:
Lahey Clin Med Ctr, Dept Transplantat, Burlington, MA 01803 USA Kumamoto Univ, Grad Sch Med Sci, Dept Neurol, Chuo Ku, Kumamoto 8608556, Japan

Obici, Laura
论文数: 0 引用数: 0
h-index: 0
机构:
Fdn IRCCS Policlin San Matteo, Amyloidosis Res & Treatment Ctr, Pavia, Italy Kumamoto Univ, Grad Sch Med Sci, Dept Neurol, Chuo Ku, Kumamoto 8608556, Japan

Plante-Bordeneuve, Violaine
论文数: 0 引用数: 0
h-index: 0
机构:
CHU Henri Mondor, Dept Neurol, F-94010 Creteil, France Kumamoto Univ, Grad Sch Med Sci, Dept Neurol, Chuo Ku, Kumamoto 8608556, Japan

论文数: 引用数:
h-index:
机构:

Said, Gerard
论文数: 0 引用数: 0
h-index: 0
机构:
Hop La Pitie Salpetriere, Dept Neurol, Paris, France Kumamoto Univ, Grad Sch Med Sci, Dept Neurol, Chuo Ku, Kumamoto 8608556, Japan

Salvi, Fabrizio
论文数: 0 引用数: 0
h-index: 0
机构:
Ist Sci Neurol Bologna, Dept Neurol, Bologna, Italy Kumamoto Univ, Grad Sch Med Sci, Dept Neurol, Chuo Ku, Kumamoto 8608556, Japan
[6]
Long-term safety and efficacy of tafamidis for the treatment of hereditary transthyretin amyloid polyneuropathy: results up to 6 years
[J].
Barroso, Fabio A.
;
Judge, Daniel P.
;
Ebede, Ben
;
Li, Huihua
;
Stewart, Michelle
;
Amass, Leslie
;
Sultan, Marla B.
.
AMYLOID-JOURNAL OF PROTEIN FOLDING DISORDERS,
2017, 24 (03)
:194-204

Barroso, Fabio A.
论文数: 0 引用数: 0
h-index: 0
机构:
FLENI, Dept Neurol, Inst Neurol Res Raul Carrea, Montaneses 2325,C1428AQK, Buenos Aires, DF, Argentina FLENI, Dept Neurol, Inst Neurol Res Raul Carrea, Montaneses 2325,C1428AQK, Buenos Aires, DF, Argentina

Judge, Daniel P.
论文数: 0 引用数: 0
h-index: 0
机构:
Johns Hopkins Univ, Ctr Inherited Heart Dis, Baltimore, MD USA FLENI, Dept Neurol, Inst Neurol Res Raul Carrea, Montaneses 2325,C1428AQK, Buenos Aires, DF, Argentina

Ebede, Ben
论文数: 0 引用数: 0
h-index: 0
机构:
Pfizer Inc, New York, NY USA FLENI, Dept Neurol, Inst Neurol Res Raul Carrea, Montaneses 2325,C1428AQK, Buenos Aires, DF, Argentina

Li, Huihua
论文数: 0 引用数: 0
h-index: 0
机构:
Pfizer Inc, New York, NY USA FLENI, Dept Neurol, Inst Neurol Res Raul Carrea, Montaneses 2325,C1428AQK, Buenos Aires, DF, Argentina

Stewart, Michelle
论文数: 0 引用数: 0
h-index: 0
机构:
Pfizer Inc, New York, NY USA FLENI, Dept Neurol, Inst Neurol Res Raul Carrea, Montaneses 2325,C1428AQK, Buenos Aires, DF, Argentina

Amass, Leslie
论文数: 0 引用数: 0
h-index: 0
机构:
Pfizer Inc, New York, NY USA FLENI, Dept Neurol, Inst Neurol Res Raul Carrea, Montaneses 2325,C1428AQK, Buenos Aires, DF, Argentina

Sultan, Marla B.
论文数: 0 引用数: 0
h-index: 0
机构:
Pfizer Inc, New York, NY USA FLENI, Dept Neurol, Inst Neurol Res Raul Carrea, Montaneses 2325,C1428AQK, Buenos Aires, DF, Argentina
[7]
Repurposing Diflunisal for Familial Amyloid Polyneuropathy A Randomized Clinical Trial
[J].
Berk, John L.
;
Suhr, Ole B.
;
Obici, Laura
;
Sekijima, Yoshiki
;
Zeldenrust, Steven R.
;
Yamashita, Taro
;
Heneghan, Michael A.
;
Gorevic, Peter D.
;
Litchy, William J.
;
Wiesman, Janice F.
;
Nordh, Erik
;
Corato, Manuel
;
Lozza, Alessandro
;
Cortese, Andrea
;
Robinson-Papp, Jessica
;
Colton, Theodore
;
Rybin, Denis V.
;
Bisbee, Alice B.
;
Ando, Yukio
;
Ikeda, Shu-ichi
;
Seldin, David C.
;
Merlini, Giampaolo
;
Skinner, Martha
;
Kelly, Jeffery W.
;
Dyck, Peter J.
.
JAMA-JOURNAL OF THE AMERICAN MEDICAL ASSOCIATION,
2013, 310 (24)
:2658-2667

Berk, John L.
论文数: 0 引用数: 0
h-index: 0
机构:
Boston Univ, Sch Med, Dept Med, Amyloidosis Ctr, Boston, MA 02118 USA
Boston Univ, Sch Med, Dept Neurol, Amyloidosis Ctr, Boston, MA 02118 USA Boston Univ, Sch Med, Dept Med, Amyloidosis Ctr, Boston, MA 02118 USA

Suhr, Ole B.
论文数: 0 引用数: 0
h-index: 0
机构:
Umea Univ, Dept Publ Hlth & Clin Med, Umea, Sweden Boston Univ, Sch Med, Dept Med, Amyloidosis Ctr, Boston, MA 02118 USA

Obici, Laura
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Pavia, Fdn IRCCS Policlin San Matteo, Amyloidosis Res & Treatment Ctr, I-27100 Pavia, Italy
Univ Pavia, Dept Mol Med, I-27100 Pavia, Italy Boston Univ, Sch Med, Dept Med, Amyloidosis Ctr, Boston, MA 02118 USA

Sekijima, Yoshiki
论文数: 0 引用数: 0
h-index: 0
机构:
Shinshu Univ, Sch Med, Dept Med, Matsumoto, Nagano 390, Japan Boston Univ, Sch Med, Dept Med, Amyloidosis Ctr, Boston, MA 02118 USA

Zeldenrust, Steven R.
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Mayo Clin, Dept Med, Rochester, MN USA
Mayo Clin, Dept Neurol, Rochester, MN USA Boston Univ, Sch Med, Dept Med, Amyloidosis Ctr, Boston, MA 02118 USA

Yamashita, Taro
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Kumamoto Univ, Grad Sch Med Sci, Dept Neurol, Kumamoto, Japan Boston Univ, Sch Med, Dept Med, Amyloidosis Ctr, Boston, MA 02118 USA

Heneghan, Michael A.
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Kings Coll Hosp Fdn Trust, Inst Liver Studies, London, England Boston Univ, Sch Med, Dept Med, Amyloidosis Ctr, Boston, MA 02118 USA

Gorevic, Peter D.
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Mt Sinai Sch Med, Dept Med, New York, NY USA
Mt Sinai Sch Med, Dept Neurol, New York, NY USA Boston Univ, Sch Med, Dept Med, Amyloidosis Ctr, Boston, MA 02118 USA

Litchy, William J.
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Mayo Clin, Dept Med, Rochester, MN USA
Mayo Clin, Dept Neurol, Rochester, MN USA Boston Univ, Sch Med, Dept Med, Amyloidosis Ctr, Boston, MA 02118 USA

Wiesman, Janice F.
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Boston Univ, Sch Med, Dept Med, Amyloidosis Ctr, Boston, MA 02118 USA
Boston Univ, Sch Med, Dept Neurol, Amyloidosis Ctr, Boston, MA 02118 USA Boston Univ, Sch Med, Dept Med, Amyloidosis Ctr, Boston, MA 02118 USA

Nordh, Erik
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Umea Univ, Dept Publ Hlth & Clin Med, Umea, Sweden Boston Univ, Sch Med, Dept Med, Amyloidosis Ctr, Boston, MA 02118 USA

Corato, Manuel
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Ist Clin Humanitas, Rozzano, Italy Boston Univ, Sch Med, Dept Med, Amyloidosis Ctr, Boston, MA 02118 USA

Lozza, Alessandro
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Fdn IRCCS, C Mondino Natl Inst Neurol, Pavia, Italy Boston Univ, Sch Med, Dept Med, Amyloidosis Ctr, Boston, MA 02118 USA

Cortese, Andrea
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Fdn IRCCS, C Mondino Natl Inst Neurol, Pavia, Italy Boston Univ, Sch Med, Dept Med, Amyloidosis Ctr, Boston, MA 02118 USA

Robinson-Papp, Jessica
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Mt Sinai Sch Med, Dept Med, New York, NY USA
Mt Sinai Sch Med, Dept Neurol, New York, NY USA Boston Univ, Sch Med, Dept Med, Amyloidosis Ctr, Boston, MA 02118 USA

Colton, Theodore
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Boston Univ, Sch Publ Hlth, Dept Epidemiol, Boston, MA USA Boston Univ, Sch Med, Dept Med, Amyloidosis Ctr, Boston, MA 02118 USA

Rybin, Denis V.
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Boston Univ, Sch Publ Hlth, Data Coordinating Ctr, Boston, MA USA Boston Univ, Sch Med, Dept Med, Amyloidosis Ctr, Boston, MA 02118 USA

Bisbee, Alice B.
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Boston Univ, Sch Publ Hlth, Data Coordinating Ctr, Boston, MA USA Boston Univ, Sch Med, Dept Med, Amyloidosis Ctr, Boston, MA 02118 USA

Ando, Yukio
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Kumamoto Univ, Grad Sch Med Sci, Dept Neurol, Kumamoto, Japan Boston Univ, Sch Med, Dept Med, Amyloidosis Ctr, Boston, MA 02118 USA

Ikeda, Shu-ichi
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Shinshu Univ, Sch Med, Dept Med, Matsumoto, Nagano 390, Japan Boston Univ, Sch Med, Dept Med, Amyloidosis Ctr, Boston, MA 02118 USA

Seldin, David C.
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Boston Univ, Sch Med, Dept Med, Amyloidosis Ctr, Boston, MA 02118 USA
Boston Univ, Sch Med, Dept Neurol, Amyloidosis Ctr, Boston, MA 02118 USA Boston Univ, Sch Med, Dept Med, Amyloidosis Ctr, Boston, MA 02118 USA

Merlini, Giampaolo
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机构:
Univ Pavia, Fdn IRCCS Policlin San Matteo, Amyloidosis Res & Treatment Ctr, I-27100 Pavia, Italy
Univ Pavia, Dept Mol Med, I-27100 Pavia, Italy Boston Univ, Sch Med, Dept Med, Amyloidosis Ctr, Boston, MA 02118 USA

Skinner, Martha
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Boston Univ, Sch Med, Dept Med, Amyloidosis Ctr, Boston, MA 02118 USA
Boston Univ, Sch Med, Dept Neurol, Amyloidosis Ctr, Boston, MA 02118 USA Boston Univ, Sch Med, Dept Med, Amyloidosis Ctr, Boston, MA 02118 USA

Kelly, Jeffery W.
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Scripps Res Inst, Dept Chem, La Jolla, CA 92037 USA
Scripps Res Inst, Dept Mol & Expt Med, La Jolla, CA 92037 USA
Scripps Res Inst, Skaggs Inst Chem Biol, La Jolla, CA 92037 USA Boston Univ, Sch Med, Dept Med, Amyloidosis Ctr, Boston, MA 02118 USA

Dyck, Peter J.
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机构:
Mayo Clin, Dept Med, Rochester, MN USA
Mayo Clin, Dept Neurol, Rochester, MN USA Boston Univ, Sch Med, Dept Med, Amyloidosis Ctr, Boston, MA 02118 USA
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Kelly, Jeffery W.
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Pfizer, Cambridge, MA USA Hosp Santo Antonio, Oporto, Portugal

Chan, Jason
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机构:
Kinet Concepts Inc, San Antonio, TX USA Hosp Santo Antonio, Oporto, Portugal

Packman, Jeff
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机构:
Pfizer, Cambridge, MA USA Hosp Santo Antonio, Oporto, Portugal

Wilson, Amy
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h-index: 0
机构:
Pfizer, Cambridge, MA USA Hosp Santo Antonio, Oporto, Portugal

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Kwoh, T. Jesse
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Ionis Pharmaceut Inc, 2855 Gazelle Court, Carlsbad, CA 92010 USA Ionis Pharmaceut Inc, 2855 Gazelle Court, Carlsbad, CA 92010 USA

Cai, Danlin
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Ionis Pharmaceut Inc, 2855 Gazelle Court, Carlsbad, CA 92010 USA Ionis Pharmaceut Inc, 2855 Gazelle Court, Carlsbad, CA 92010 USA

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