Directed Evolution of AAV for Retinal Gene Therapy

被引:0
作者
Tekinsoy, Muge D. [1 ]
Planul, Arthur [1 ]
Zin, Emilia [1 ]
Simon, Cardillia J. [1 ]
Desrosiers, Melissa [1 ]
Fradot, Valerie [1 ]
Nemoto, Takahiro [1 ]
Robert, Camille [1 ]
Jaillard, Celine [1 ]
Bertin, Stephane [1 ,2 ]
Sahel, Jose-Alain [1 ,2 ]
Ferrari, Ulisse [1 ]
Dalkara, Deniz [1 ]
机构
[1] Sorbonne Univ, INSERM, CNRS, Inst Vis, Paris, France
[2] CHNO Quinze Vingts, INSERM DGOS CIC 1423, Paris, France
关键词
D O I
暂无
中图分类号
Q81 [生物工程学(生物技术)]; Q93 [微生物学];
学科分类号
071005 ; 0836 ; 090102 ; 100705 ;
摘要
121
引用
收藏
页码:65 / 65
页数:1
相关论文
共 50 条
[21]   Delivering efficient liver-directed AAV-mediated gene therapy [J].
J Baruteau ;
S N Waddington ;
I E Alexander ;
P Gissen .
Gene Therapy, 2017, 24 :263-264
[22]   Tissue-Directed Transgene Engineering for AAV and Lentivector Gene Therapy Approaches [J].
Brown, Harrison C. ;
Zakas, Phillip M. ;
George, Stephan N. ;
Parker, Ernest T. ;
Spencer, H. Trent ;
Doering, Christopher B. .
MOLECULAR THERAPY, 2016, 24 :S287-S287
[23]   Delivering efficient liver-directed AAV-mediated gene therapy [J].
Baruteau, J. ;
Waddington, S. N. ;
Alexander, I. E. ;
Gissen, P. .
GENE THERAPY, 2017, 24 (05) :263-264
[24]   AAV-Directed Liver Gene Therapy for Crigler-Najjar Syndrome [J].
Collaud, Fanny ;
Ronzitti, Giuseppe ;
Bortolussi, Giulia ;
Guianvarc'h, Laurence ;
Veron, Philippe ;
Charles, Severine ;
Vidal, Patrice ;
Sola, Marcelo Simon ;
Leborgne, Christian ;
Rundwasser, Stephanie ;
Dejoint, Ludivine ;
Goncalves, Delphine ;
Van Wittenberghe, Laetitia ;
Martin, Samia ;
Le Bec, Christine ;
Bosma, Piter J. ;
Muro, Andres F. ;
Hebben, Matthias ;
Mingozzi, Federico .
MOLECULAR THERAPY, 2018, 26 (05) :385-385
[25]   AAV Mediated Liver Directed Gene Therapy for Gyrate Atrophy of the Choroid and Retina [J].
Boffa, Iolanda ;
Marrocco, Elena ;
Caterino, Marianna ;
Ruoppolo, Margherita ;
Auricchio, Alberto ;
Pierri, Nicola Brunetti .
MOLECULAR THERAPY, 2022, 30 (04) :247-247
[26]   Selection of Optimal AAV Serotypes as Clinical Candidates for AAV-Mediated, Liver-Directed Gene Therapy [J].
Wang, Lili ;
Wang, Huan ;
Bell, Peter ;
McCarter, Robert J. ;
Calcedo, Roberto ;
Wilson, James M. .
MOLECULAR THERAPY, 2009, 17 :S279-S279
[27]   AAV-Mediated Gene Therapy in Mouse Models of Recessive Retinal Degeneration [J].
Pang, J. -J. ;
Lei, L. ;
Dai, X. ;
Shi, W. ;
Liu, X. ;
Dinculescu, A. ;
McDowell, J. H. .
CURRENT MOLECULAR MEDICINE, 2012, 12 (03) :316-330
[28]   AAV-mediated gene therapy for retinal disorders: from mouse to man [J].
Buch, P. K. ;
Bainbridge, J. W. ;
Ali, R. R. .
GENE THERAPY, 2008, 15 (11) :849-857
[29]   AAV-Mediated Gene Therapy for Retinal Disorders in Large Animal Models [J].
Stieger, Knut ;
Lheriteau, Elsa ;
Moullier, Philippe ;
Rolling, Fabienne .
ILAR JOURNAL, 2009, 50 (02) :206-224
[30]   AAV-mediated gene therapy for retinal disorders: from mouse to man [J].
P K Buch ;
J W Bainbridge ;
R R Ali .
Gene Therapy, 2008, 15 :849-857