This review illustrates how measurements of clinical status in patients with myasthenia gravis have evolved from clinical descriptions and estimates of mortality rates to more sophisticated evaluative instruments, including numerical rating scales that measure strength, endurance, quality of life, and activities of daily living. The rationale and use of weighting and the importance of patient-reported outcomes are also discussed. The measurement of the steroid-sparing effect of an immunosuppressant is also reviewed. Muscle Nerve 42: 5-13, 2010
机构:
Univ Autonoma Barcelona, Hosp Santa Creu & St Pau, Neuromuscular Dis Unit, Dept Neurol, Barcelona 08025, SpainUniv Autonoma Barcelona, Hosp Santa Creu & St Pau, Neuromuscular Dis Unit, Dept Neurol, Barcelona 08025, Spain
Diaz-Manera, Jordi
Rojas-Garcia, Ricard
论文数: 0引用数: 0
h-index: 0
机构:
Univ Autonoma Barcelona, Hosp Santa Creu & St Pau, Neuromuscular Dis Unit, Dept Neurol, Barcelona 08025, SpainUniv Autonoma Barcelona, Hosp Santa Creu & St Pau, Neuromuscular Dis Unit, Dept Neurol, Barcelona 08025, Spain
Rojas-Garcia, Ricard
Illa, Isabel
论文数: 0引用数: 0
h-index: 0
机构:
Univ Autonoma Barcelona, Hosp Santa Creu & St Pau, Neuromuscular Dis Unit, Dept Neurol, Barcelona 08025, SpainUniv Autonoma Barcelona, Hosp Santa Creu & St Pau, Neuromuscular Dis Unit, Dept Neurol, Barcelona 08025, Spain