Non-Viral Gene Delivery of Human FVIII to Hemophilia A Mice and Non-Human Primates

被引：0

作者：

Stanton, Matthew G. ^{[1
]}

Klatte, Deb ^{[1
]}

Chiocco, Matt ^{[1
]}

Hamm, Luke ^{[1
]}

Nelson, Elizabeth ^{[1
]}

Feinstein, Greg ^{[1
]}

Gallagher, Nolan ^{[1
]}

Su, Jie ^{[1
]}

Milstead, Andrew ^{[1
]}

Bush, Di ^{[1
]}

Monds, Russell ^{[1
]}

Parsonnet, Nicholas ^{[1
]}

Penvose, Ashley ^{[1
]}

LaGoy, Sarah ^{[1
]}

Hansen, Erik ^{[1
]}

Kittel, Jonathan ^{[1
]}

Lymar, Anastasia ^{[1
]}

Vu, Kati ^{[1
]}

Joyce, Michelle Rodriguez ^{[1
]}

Malakian, Karl ^{[1
]}

Moffitt, Jeff ^{[1
]}

机构：

[1] Generat Bio, Cambridge, MA USA

来源：

MOLECULAR THERAPY | 2021年 / 29卷 / 04期

关键词：

D O I：

暂无

中图分类号：

Q81 [生物工程学（生物技术）]; Q93 [微生物学];

学科分类号：

071005 ; 0836 ; 090102 ; 100705 ;

摘要：

694

引用

页码：337 / 337

页数：1

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