Innovation in the field of thrombocytopenias: achievements since the beginning of the century and promises for the future

被引：6

作者：

Balduini, Carlo L. ^{[1
]}

Noris, Patrizia

机构：

[1] IRCCS Policlin San Matteo Fdn, Dept Internal Med, Pavia, Italy

来源：

HAEMATOLOGICA | 2016年 / 101卷 / 01期

关键词：

INHERITED THROMBOCYTOPENIAS; ELTROMBOPAG; THROMBOPOIETIN; GENERATION; PLATELETS; MUTATIONS;

D O I：

10.3324/haematol.2015.138149

中图分类号：

R5 [内科学];

学科分类号：

1002 ; 100201 ;

摘要：

引用

页码：2 / 4

页数：3

共 20 条

[1] Outcomes Following Gene Therapy in Patients With Severe Wiskott-Aldrich Syndrome [J].

Abina, Salima Hacein-Bey ;

Gaspar, H. Bobby ;

Blondeau, Johanna ;

Caccavelli, Laure ;

Charrier, Sabine ;

Buckland, Karen ;

Picard, Capucine ;

Six, Emmanuelle ;

Himoudi, Nourredine ;

Gilmour, Kimberly ;

McNicol, Anne-Marie ;

Hara, Havinder ;

Xu-Bayford, Jinhua ;

Rivat, Christine ;

Touzot, Fabien ;

Mavilio, Fulvio ;

Lim, Annick ;

Treluyer, Jean-Marc ;

Heritier, Sebastien ;

Lefrere, Francois ;

Magalon, Jeremy ;

Pengue-Koyi, Isabelle ;

Honnet, Geraldine ;

Blanche, Stephane ;

Sherman, Eric A. ;

Male, Frances ;

Berry, Charles ;

Malani, Nirav ;

Bushman, Frederic D. ;

Fischer, Alain ;

Thrasher, Adrian J. ;

Galy, Anne ;

Cavazzana, Marina .

JAMA-JOURNAL OF THE AMERICAN MEDICAL ASSOCIATION, 2015, 313 (15) :1550-1563

[2] Inherited thrombocytopenias frequently diagnosed in adults [J].

Balduini, C. L. ;

Savoia, A. ;

Seri, M. .

JOURNAL OF THROMBOSIS AND HAEMOSTASIS, 2013, 11 (06) :1006-1019

[3] Inherited thrombocytopenias The evolving spectrum [J].

Balduini, C. L. ;

Pecci, A. ;

Noris, P. .

HAMOSTASEOLOGIE, 2012, 32 (04) :259-+

[4] Feasibility of romiplostim discontinuation in adult thrombopoietin-receptor agonist responsive patients with primary immune thrombocytopenia. an observational retrospective report in real life clinical practice [J].

Carpenedo, Monica ;

Cantoni, Silvia ;

Coccini, Veronica ;

Fedele, Marilena ;

Morra, Enrica ;

Pogliani, Enrico Maria .

HEMATOLOGY REPORTS, 2015, 7 (01) :1-4

[5] Programmable 3D silk bone marrow niche for platelet generation ex vivo and modeling of megakaryopoiesis pathologies [J].

Di Buduo, Christian A. ;

Wray, Lindsay S. ;

Tozzi, Lorenzo ;

Malara, Alessandro ;

Chen, Ying ;

Ghezzi, Chiara E. ;

Smoot, Daniel ;

Sfara, Carla ;

Antonelli, Antonella ;

Spedden, Elise ;

Bruni, Giovanna ;

Staii, Cristian ;

De Marco, Luigi ;

Magnani, Mauro ;

Kaplan, David L. ;

Balduini, Alessandra .

BLOOD, 2015, 125 (14) :2254-2264

[6] First Successful Use of Eltrombopag Before Surgery in a Child With MYH9-Related Thrombocytopenia [J].

Favier, Remi ;

Feriel, Joffrey ;

Favier, Marie ;

Denoyelle, Francoise ;

Martignetti, John A. .

PEDIATRICS, 2013, 132 (03) :E793-E795

[7] Scalable Generation of Universal Platelets from Human Induced Pluripotent Stem Cells [J].

Feng, Qiang ;

Shabrani, Namrata ;

Thon, Jonathan N. ;

Huo, Hongguang ;

Thiel, Austin ;

Machlus, Kellie R. ;

Kim, Kyungho ;

Brooks, Julie ;

Li, Feng ;

Luo, Chenmei ;

Kimbrel, Erin A. ;

Wang, Jiwu ;

Kim, Kwang-Soo ;

Italiano, Joseph ;

Cho, Jaehyung ;

Lu, Shi-Jiang ;

Lanza, Robert .

STEM CELL REPORTS, 2014, 3 (05) :817-831

[8] Effects of eltrombopag on platelet count and platelet activation in Wiskott-Aldrich syndrome/X-linked thrombocytopenia [J].

Gerrits, Anja J. ;

Leven, Emily A. ;

Frelinger, Andrew L., III ;

Brigstocke, Sophie L. ;

Berny-Lang, Michelle A. ;

Mitchell, W. Beau ;

Revel-Vilk, Shoshana ;

Tamary, Hannah ;

Carmichael, Sabrina L. ;

Barnard, Marc R. ;

Michelson, Alan D. ;

Bussel, James B. .

BLOOD, 2015, 126 (11) :1367-1378

[9] Thrombopoiesis [J].

Kaushansky, Kenneth .

SEMINARS IN HEMATOLOGY, 2015, 52 (01) :4-11

[10] Thrombocytopenia caused by the development of antibodies to thrombopoietin [J].

Li, JZ ;

Yang, C ;

Xia, YP ;

Bertino, A ;

Glaspy, J ;

Roberts, M ;

Kuter, DJ .

BLOOD, 2001, 98 (12) :3241-3248

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