How to create state-of-the-art genetic model systems: strategies for optimal CRISPR-mediated genome editing

被引:36
作者
Bollen, Yannik [1 ,2 ,3 ]
Post, Jasmin [1 ,2 ]
Koo, Bon-Kyoung [4 ]
Snippert, Hugo J. G. [1 ,2 ]
机构
[1] Univ Utrecht, Univ Med Ctr Utrecht, Ctr Mol Med, Mol Canc Res, Utrecht, Netherlands
[2] Oncode Inst, Utrecht, Netherlands
[3] Univ Twente, MIRA Inst, Med Cell BioPhys, Enschede, Netherlands
[4] Austrian Acad Sci IMBA, Inst Mol Biotechnol, Vienna, Austria
关键词
PLURIPOTENT STEM-CELLS; STRAND BREAK REPAIR; HOMOLOGY-DIRECTED REPAIR; TARGETED INTEGRATION; CAS9; PROTEIN; COLORECTAL-CANCER; CYSTIC-FIBROSIS; BETA-GLOBIN; EASI-CRISPR; GUIDE RNA;
D O I
10.1093/nar/gky571
中图分类号
Q5 [生物化学]; Q7 [分子生物学];
学科分类号
071010 ; 081704 ;
摘要
Model systems with defined genetic modifications are powerful tools for basic research and translational disease modelling. Fortunately, generating state-of-the-art genetic model systems is becoming more accessible to non-geneticists due to advances in genome editing technologies. As a consequence, solely relying on (transient) overexpression of (mutant) effector proteins is no longer recommended since scientific standards increasingly demand genetic modification of endogenous loci. In this review, we provide up-to-date guidelines with respect to homology-directed repair (HDR)-mediated editing of mammalian model systems, aimed at assisting researchers in designing an efficient genome editing strategy.
引用
收藏
页码:6435 / 6454
页数:20
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