Reduction of BCL11A in hematopoietic stem cells through gene editing: new strategy to ameliorate the severe β-globin disorders sickle cell disease

被引：0
作者：
Hong, Weiqi [1 ]
Huang, Mengyuan [1 ]
Wei, Yuquan [1 ]
Wei, Xiawei [1 ]
机构：
[1] Sichuan Univ, Lab Aging Res & Canc Drug Target, Natl Clin Res Ctr Geriatr, State Key Lab Biotherapy,West China Hosp, Chengdu 610041, Sichuan, Peoples R China
来源：
SCIENCE BULLETIN | 2019年 / 64卷 / 21期
关键词：
CRISPR/CAS9; SYSTEM; TECHNOLOGY;
D O I：
10.1016/j.scib.2019.09.002
中图分类号：
O [数理科学和化学]; P [天文学、地球科学]; Q [生物科学]; N [自然科学总论];
学科分类号：
07 ; 0710 ; 09 ;
摘要：
引用
收藏
页码：1562 / 1564
页数：3
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