[1] Univ Penn, Sch Med, Dept Genet, Philadelphia, PA 19104 USA
[2] Ohio State Univ, Dept Neurol, Columbus, OH 43210 USA
[3] Univ Penn, Sch Med, Inst Human Gene Therapy, Philadelphia, PA 19104 USA
[4] Univ Iowa, Coll Med, Dept Pathol, Iowa City, IA 52242 USA
[5] Univ Iowa, Coll Med, Howard Hughes Med Inst, Dept Physiol, Iowa City, IA 52242 USA
[6] Univ Iowa, Coll Med, Howard Hughes Med Inst, Dept Biophys, Iowa City, IA 52242 USA
[7] Univ Iowa, Coll Med, Howard Hughes Med Inst, Dept Neurol, Iowa City, IA 52242 USA