Treatment of Lysosomal Storage Diseases: Lessons for Other Genetic Disorders

被引:0
|
作者
Clarke, L. [1 ]
机构
[1] Univ British Columbia, Vancouver, BC, Canada
关键词
D O I
暂无
中图分类号
Q [生物科学];
学科分类号
07 ; 0710 ; 09 ;
摘要
S19
引用
收藏
页码:361 / 361
页数:1
相关论文
共 50 条
  • [1] Principle of protection and treatment of rare genetic diseases in Brazil: the case of lysosomal storage disorders
    Boy, Raquel
    Schramm, Fermin Roland
    CADERNOS DE SAUDE PUBLICA, 2009, 25 (06): : 1276 - 1284
  • [2] Lysosomal storage diseases as disorders of autophagy
    Settembre, Carmine
    Fraldi, Alessandro
    Rubinsztein, David C.
    Ballabio, Andrea
    AUTOPHAGY, 2008, 4 (01) : 113 - 114
  • [3] Mucopolysaccharidoses and Other Lysosomal Storage Diseases
    Lampe, Christina
    Bellettato, Cinzia Maria
    Karabul, Nesrin
    Scarpa, Maurizio
    RHEUMATIC DISEASE CLINICS OF NORTH AMERICA, 2013, 39 (02) : 431 - +
  • [4] Treatment for Lysosomal Storage Disorders
    Sheth, Jayesh
    Nair, Aadhira
    CURRENT PHARMACEUTICAL DESIGN, 2020, 26 (40) : 5110 - 5118
  • [5] Enzyme replacement therapy in lysosomal storage diseases: lessons from the treatment of Gaucher diseases - Commentary
    Cox, T
    JOURNAL OF INHERITED METABOLIC DISEASE, 2001, 24 : 87 - 88
  • [6] Lysosomal Storage Diseases: Heterogeneous Group of Disorders
    Wenger, David A.
    Luzi, Paola
    Rafi, Mohammad A.
    BIOIMPACTS, 2013, 3 (04) : 145 - 147
  • [7] Approaches for the treatment of lysosomal storage diseases
    Schuchman, E. H.
    Dhami, R.
    Muro, S.
    He, X.
    JOURNAL OF INHERITED METABOLIC DISEASE, 2006, 29 : 9 - 9
  • [8] Lysosomal storage diseases: treatment options
    Beck, Michael
    MEDIZINISCHE GENETIK, 2015, 27 (03): : 276 - 281
  • [9] Treatment perspectives for the lysosomal storage diseases
    Grabowski, Gregory A.
    EXPERT OPINION ON EMERGING DRUGS, 2008, 13 (01) : 197 - 211
  • [10] Treatment strategies for lysosomal storage disorders
    Beck, Michael
    DEVELOPMENTAL MEDICINE AND CHILD NEUROLOGY, 2018, 60 (01): : 13 - 18