Haemophilia gene therapy: experiences and lessons from treated patients

被引：5
作者：
Hermans, Cedric [1 ]
机构：
[1] Univ catholique Louvain UCLouvain, Clin Univ St Luc, Div Adult Hematol, Haemostasis & Thrombosis Unit, Ave Hippocrate 10, B-1200 Brussels, Belgium
来源：
ORPHANET JOURNAL OF RARE DISEASES | 2022年 / 17卷 / 01期
关键词：
Haemophilia; Gene therapy; Decision making; Informed consent; Clinical trial;
D O I：
10.1186/s13023-022-02313-w
中图分类号：
Q3 [遗传学];
学科分类号：
071007 ; 090102 ;
摘要：
引用
收藏
页数：3
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