Exon Skipping for the Second Calponin Homology Domain of Dystrophin Using AAV. U7snRNA-In Vitro Intramuscular Studies Using a Novel Murine Model of Duchenne Muscular Dystrophy

被引：0
|
作者：
Lesman, Daniel [1 ]
Rajakumar, Dhanarajan [1 ]
Li, Ding [1 ]
Rodriguez, Yacidzohara [1 ]
Atre, Chaitrali [1 ]
Wein, Nicolas [1 ,2 ]
机构：
[1] Nationwide Childrens Hosp, Columbus, OH USA
[2] Ohio State Univ, Dept Pediat, Columbus, OH 43210 USA
来源：
MOLECULAR THERAPY | 2022年 / 30卷 / 04期
关键词：
D O I：
暂无
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
156
引用
收藏
页码：79 / 79
页数：1
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