Rate of disease progression and response to enzyme replacement therapy in children and adults with Pompe disease

被引：0
作者：
Van der Beek, N. A. M. [1 ]
De Vries, J. M. [1 ]
Van Capelle, C. I. [2 ]
Reuser, A. J. J. [1 ]
van Doorn, P. A. [1 ]
van der Ploeg, A. T. [2 ]
机构：
[1] Univ Med Ctr, Erasmus MC, Rotterdam, Netherlands
[2] Sophia Childrenss Hosp, Erasmus MC, Div Metab Dis, Rotterdam, Netherlands
来源：
NEUROMUSCULAR DISORDERS | 2009年 / 19卷 / 8-9期
关键词：
D O I：
10.1016/j.nmd.2009.06.157
中图分类号：
R74 [神经病学与精神病学];
学科分类号：
摘要：
引用
收藏
页码：593 / 593
页数：1
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