共 6 条
[1]
Recombinant Adeno-Associated Viral Integration and Genotoxicity: Insights from Animal Models
[J].
Chandler, Randy J.
;
Sands, Mark S.
;
Venditti, Charles P.
.
HUMAN GENE THERAPY,
2017, 28 (04)
:314-322

Chandler, Randy J.
论文数: 0 引用数: 0
h-index: 0
机构:
NHGRI, Med Genom & Metab Genet Branch, NIH, Dept Hlth & Human Serv, Bldg 49,Room 4A18, Bethesda, MD 20895 USA NHGRI, Med Genom & Metab Genet Branch, NIH, Dept Hlth & Human Serv, Bldg 49,Room 4A18, Bethesda, MD 20895 USA

Sands, Mark S.
论文数: 0 引用数: 0
h-index: 0
机构:
Washington Univ, Sch Med, Dept Internal Med, St Louis, MO 63110 USA
Washington Univ, Sch Med, Dept Genet, St Louis, MO 63110 USA NHGRI, Med Genom & Metab Genet Branch, NIH, Dept Hlth & Human Serv, Bldg 49,Room 4A18, Bethesda, MD 20895 USA

Venditti, Charles P.
论文数: 0 引用数: 0
h-index: 0
机构:
NHGRI, Med Genom & Metab Genet Branch, NIH, Dept Hlth & Human Serv, Bldg 49,Room 4A18, Bethesda, MD 20895 USA NHGRI, Med Genom & Metab Genet Branch, NIH, Dept Hlth & Human Serv, Bldg 49,Room 4A18, Bethesda, MD 20895 USA
[2]
Liver Injury Increases the Incidence of HCC following AAV Gene Therapy in Mice
[J].
Dalwadi, Dhwanil A.
;
Torrens, Laura
;
Abril-Fornaguera, Jordi
;
Pinyol, Roser
;
Willoughby, Catherine
;
Posey, Jeffrey
;
Llovet, Josep M.
;
Lanciault, Christian
;
Russell, David W.
;
Grompe, Markus
;
Naugler, Willscott E.
.
MOLECULAR THERAPY,
2021, 29 (02)
:680-690

Dalwadi, Dhwanil A.
论文数: 0 引用数: 0
h-index: 0
机构:
Oregon Hlth & Sci Univ, Dept Med, Div Gastroenterol & Hepatol, Portland, OR 97239 USA
Oregon Hlth & Sci Univ, Pediat Res Inst, Dept Pediat, Pape Family, Portland, OR 97239 USA Oregon Hlth & Sci Univ, Dept Med, Div Gastroenterol & Hepatol, Portland, OR 97239 USA

Torrens, Laura
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Barcelona, IDIBAPS Hosp Clin, Liver Unit, Translat Res Hepat Oncol, Catalonia, Spain Oregon Hlth & Sci Univ, Dept Med, Div Gastroenterol & Hepatol, Portland, OR 97239 USA

论文数: 引用数:
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Pinyol, Roser
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Barcelona, IDIBAPS Hosp Clin, Liver Unit, Translat Res Hepat Oncol, Catalonia, Spain Oregon Hlth & Sci Univ, Dept Med, Div Gastroenterol & Hepatol, Portland, OR 97239 USA

Willoughby, Catherine
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Barcelona, IDIBAPS Hosp Clin, Liver Unit, Translat Res Hepat Oncol, Catalonia, Spain Oregon Hlth & Sci Univ, Dept Med, Div Gastroenterol & Hepatol, Portland, OR 97239 USA

论文数: 引用数:
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Llovet, Josep M.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Barcelona, IDIBAPS Hosp Clin, Liver Unit, Translat Res Hepat Oncol, Catalonia, Spain
Icahn Sch Med Mt Sinai, Mt Sinai Liver Canc Program, Div Liver Dis, Tisch Canc Inst, New York, NY 10029 USA
Inst Catalana Recerca & Estudis Avancats ICREA, Barcelona, Catalonia, Spain Oregon Hlth & Sci Univ, Dept Med, Div Gastroenterol & Hepatol, Portland, OR 97239 USA

Lanciault, Christian
论文数: 0 引用数: 0
h-index: 0
机构:
Oregon Hlth & Sci Univ, Dept Pathol, Portland, OR 97239 USA Oregon Hlth & Sci Univ, Dept Med, Div Gastroenterol & Hepatol, Portland, OR 97239 USA

Russell, David W.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Washington, Dept Med, Seattle, WA 98195 USA
Univ Washington, Dept Biochem, Seattle, WA 98195 USA Oregon Hlth & Sci Univ, Dept Med, Div Gastroenterol & Hepatol, Portland, OR 97239 USA

论文数: 引用数:
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Naugler, Willscott E.
论文数: 0 引用数: 0
h-index: 0
机构:
Oregon Hlth & Sci Univ, Dept Med, Div Gastroenterol & Hepatol, Portland, OR 97239 USA Oregon Hlth & Sci Univ, Dept Med, Div Gastroenterol & Hepatol, Portland, OR 97239 USA
[3]
Observed incidence of tumorigenesis in long-term rodent studies of rAAV vectors
[J].
Donsante, A
;
Vogler, C
;
Muzyczka, N
;
Crawford, JM
;
Barker, J
;
Flotte, T
;
Campbell-Thompson, M
;
Daly, T
;
Sands, MS
.
GENE THERAPY,
2001, 8 (17)
:1343-1346

Donsante, A
论文数: 0 引用数: 0
h-index: 0
机构: Washington Univ, Sch Med, St Louis, MO 63110 USA

Vogler, C
论文数: 0 引用数: 0
h-index: 0
机构: Washington Univ, Sch Med, St Louis, MO 63110 USA

Muzyczka, N
论文数: 0 引用数: 0
h-index: 0
机构: Washington Univ, Sch Med, St Louis, MO 63110 USA

Crawford, JM
论文数: 0 引用数: 0
h-index: 0
机构: Washington Univ, Sch Med, St Louis, MO 63110 USA

Barker, J
论文数: 0 引用数: 0
h-index: 0
机构: Washington Univ, Sch Med, St Louis, MO 63110 USA

Flotte, T
论文数: 0 引用数: 0
h-index: 0
机构: Washington Univ, Sch Med, St Louis, MO 63110 USA

Campbell-Thompson, M
论文数: 0 引用数: 0
h-index: 0
机构: Washington Univ, Sch Med, St Louis, MO 63110 USA

Daly, T
论文数: 0 引用数: 0
h-index: 0
机构: Washington Univ, Sch Med, St Louis, MO 63110 USA

Sands, MS
论文数: 0 引用数: 0
h-index: 0
机构: Washington Univ, Sch Med, St Louis, MO 63110 USA
[4]
Enhanced Efficacy and Increased Long-Term Toxicity of CNS-Directed, AAV-Based Combination Therapy for Krabbe Disease
[J].
Li, Yedda
;
Miller, Christopher A.
;
Shea, Lauren K.
;
Jiang, Xuntian
;
Guzman, Miguel A.
;
Chandler, Randy J.
;
Ramakrishnan, Sai M.
;
Smith, Stephanie N.
;
Venditti, Charles P.
;
Vogler, Carole A.
;
Ory, Daniel S.
;
Ley, Timothy J.
;
Sands, Mark S.
.
MOLECULAR THERAPY,
2021, 29 (02)
:691-701

论文数: 引用数:
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机构:

Miller, Christopher A.
论文数: 0 引用数: 0
h-index: 0
机构:
Washington Univ, Sch Med, Dept Med, St Louis, MO 63110 USA Washington Univ, Sch Med, Dept Med, St Louis, MO 63110 USA

Shea, Lauren K.
论文数: 0 引用数: 0
h-index: 0
机构:
Washington Univ, Sch Med, Dept Med, St Louis, MO 63110 USA Washington Univ, Sch Med, Dept Med, St Louis, MO 63110 USA

Jiang, Xuntian
论文数: 0 引用数: 0
h-index: 0
机构:
Washington Univ, Sch Med, Dept Med, St Louis, MO 63110 USA Washington Univ, Sch Med, Dept Med, St Louis, MO 63110 USA

Guzman, Miguel A.
论文数: 0 引用数: 0
h-index: 0
机构:
St Louis Univ, Sch Med, Dept Pathol, St Louis, MO 63104 USA Washington Univ, Sch Med, Dept Med, St Louis, MO 63110 USA

Chandler, Randy J.
论文数: 0 引用数: 0
h-index: 0
机构:
NHGRI, Med Genom & Metab Genet Branch, Bethesda, MD USA Washington Univ, Sch Med, Dept Med, St Louis, MO 63110 USA

Ramakrishnan, Sai M.
论文数: 0 引用数: 0
h-index: 0
机构:
Washington Univ, Sch Med, Dept Med, St Louis, MO 63110 USA Washington Univ, Sch Med, Dept Med, St Louis, MO 63110 USA

Smith, Stephanie N.
论文数: 0 引用数: 0
h-index: 0
机构:
NHGRI, Med Genom & Metab Genet Branch, Bethesda, MD USA Washington Univ, Sch Med, Dept Med, St Louis, MO 63110 USA

Venditti, Charles P.
论文数: 0 引用数: 0
h-index: 0
机构:
NHGRI, Med Genom & Metab Genet Branch, Bethesda, MD USA Washington Univ, Sch Med, Dept Med, St Louis, MO 63110 USA

Vogler, Carole A.
论文数: 0 引用数: 0
h-index: 0
机构:
St Louis Univ, Sch Med, Dept Pathol, St Louis, MO 63104 USA Washington Univ, Sch Med, Dept Med, St Louis, MO 63110 USA

Ory, Daniel S.
论文数: 0 引用数: 0
h-index: 0
机构:
Washington Univ, Sch Med, Dept Med, St Louis, MO 63110 USA Washington Univ, Sch Med, Dept Med, St Louis, MO 63110 USA

Ley, Timothy J.
论文数: 0 引用数: 0
h-index: 0
机构:
Washington Univ, Sch Med, Dept Med, St Louis, MO 63110 USA
Washington Univ, Sch Med, Dept Genet, St Louis, MO 63110 USA Washington Univ, Sch Med, Dept Med, St Louis, MO 63110 USA

Sands, Mark S.
论文数: 0 引用数: 0
h-index: 0
机构:
Washington Univ, Sch Med, Dept Med, St Louis, MO 63110 USA
Washington Univ, Sch Med, Dept Genet, St Louis, MO 63110 USA Washington Univ, Sch Med, Dept Med, St Louis, MO 63110 USA
[5]
Identification of liver-specific enhancer-promoter activity in the 3′ untranslated region of the wild-type AAV2 genome
[J].
Logan, Grant J.
;
Dane, Allison P.
;
Hallwirth, Claus V.
;
Smyth, Christine M.
;
Wilkie, Emilie E.
;
Amaya, Anais K.
;
Zhu, Erhua
;
Khandekar, Neeta
;
Ginn, Samantha L.
;
Liao, Sophia H. Y.
;
Cunningham, Sharon C.
;
Sasaki, Natsuki
;
Cabanes-Creus, Marti
;
Tam, Patrick P. L.
;
Russell, David W.
;
Lisowski, Leszek
;
Alexander, Ian E.
.
NATURE GENETICS,
2017, 49 (08)
:1267-+

Logan, Grant J.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Sydney, Childrens Med Res Inst, Gene Therapy Res Unit, Sydney, NSW, Australia Univ Sydney, Childrens Med Res Inst, Gene Therapy Res Unit, Sydney, NSW, Australia

Dane, Allison P.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Sydney, Childrens Med Res Inst, Gene Therapy Res Unit, Sydney, NSW, Australia
UCL Royal Free Med Sch, Freeline Therapeut, London, England Univ Sydney, Childrens Med Res Inst, Gene Therapy Res Unit, Sydney, NSW, Australia

Hallwirth, Claus V.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Sydney, Childrens Med Res Inst, Gene Therapy Res Unit, Sydney, NSW, Australia Univ Sydney, Childrens Med Res Inst, Gene Therapy Res Unit, Sydney, NSW, Australia

Smyth, Christine M.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Sydney, Childrens Med Res Inst, Gene Therapy Res Unit, Sydney, NSW, Australia Univ Sydney, Childrens Med Res Inst, Gene Therapy Res Unit, Sydney, NSW, Australia

Wilkie, Emilie E.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Sydney, Sydney Childrens Hosp Network, Sydney, NSW, Australia
Univ Sydney, Childrens Med Res Inst, Bioinformat Unit, Sydney, NSW, Australia Univ Sydney, Childrens Med Res Inst, Gene Therapy Res Unit, Sydney, NSW, Australia

Amaya, Anais K.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Sydney, Childrens Med Res Inst, Gene Therapy Res Unit, Sydney, NSW, Australia Univ Sydney, Childrens Med Res Inst, Gene Therapy Res Unit, Sydney, NSW, Australia

Zhu, Erhua
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Sydney, Childrens Med Res Inst, Gene Therapy Res Unit, Sydney, NSW, Australia Univ Sydney, Childrens Med Res Inst, Gene Therapy Res Unit, Sydney, NSW, Australia

Khandekar, Neeta
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Sydney, Childrens Med Res Inst, Gene Therapy Res Unit, Sydney, NSW, Australia Univ Sydney, Childrens Med Res Inst, Gene Therapy Res Unit, Sydney, NSW, Australia

Ginn, Samantha L.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Sydney, Childrens Med Res Inst, Gene Therapy Res Unit, Sydney, NSW, Australia Univ Sydney, Childrens Med Res Inst, Gene Therapy Res Unit, Sydney, NSW, Australia

Liao, Sophia H. Y.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Sydney, Childrens Med Res Inst, Gene Therapy Res Unit, Sydney, NSW, Australia Univ Sydney, Childrens Med Res Inst, Gene Therapy Res Unit, Sydney, NSW, Australia

Cunningham, Sharon C.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Sydney, Childrens Med Res Inst, Gene Therapy Res Unit, Sydney, NSW, Australia Univ Sydney, Childrens Med Res Inst, Gene Therapy Res Unit, Sydney, NSW, Australia

Sasaki, Natsuki
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Sydney, Childrens Med Res Inst, Gene Therapy Res Unit, Sydney, NSW, Australia Univ Sydney, Childrens Med Res Inst, Gene Therapy Res Unit, Sydney, NSW, Australia

Cabanes-Creus, Marti
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Sydney, Childrens Med Res Inst, Embryol Unit, Sydney, NSW, Australia
Univ Sydney, Childrens Med Res Inst, Translat Vectorol Grp, Sydney, NSW, Australia Univ Sydney, Childrens Med Res Inst, Gene Therapy Res Unit, Sydney, NSW, Australia

Tam, Patrick P. L.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Sydney, Childrens Med Res Inst, Bioinformat Unit, Sydney, NSW, Australia Univ Sydney, Childrens Med Res Inst, Gene Therapy Res Unit, Sydney, NSW, Australia

Russell, David W.
论文数: 0 引用数: 0
h-index: 0
机构:
UCL, Inst Child Hlth, Mol Immunol Unit, Ctr Immunodeficiency, London, England
Univ Washington, Dept Med, Seattle, WA USA Univ Sydney, Childrens Med Res Inst, Gene Therapy Res Unit, Sydney, NSW, Australia

Lisowski, Leszek
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Sydney, Childrens Med Res Inst, Embryol Unit, Sydney, NSW, Australia
Mil Inst Hyg & Epidemiol, Pulawy, Poland Univ Sydney, Childrens Med Res Inst, Gene Therapy Res Unit, Sydney, NSW, Australia

Alexander, Ian E.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Sydney, Childrens Med Res Inst, Gene Therapy Res Unit, Sydney, NSW, Australia
Univ Sydney, Discipline Child & Adolescent Hlth, Westmead, NSW, Australia Univ Sydney, Childrens Med Res Inst, Gene Therapy Res Unit, Sydney, NSW, Australia
[6]
A long-term study of AAV gene therapy in dogs with hemophilia A identifies clonal expansions of transduced liver cells
[J].
Nguyen, Giang N.
;
Everett, John K.
;
Kafle, Samita
;
Roche, Aoife M.
;
Raymond, Hayley E.
;
Leiby, Jacob
;
Wood, Christian
;
Assenmacher, Charles-Antoine
;
Merricks, Elizabeth P.
;
Long, C. Tyler
;
Kazazian, Haig H.
;
Nichols, Timothy C.
;
Bushman, Frederic D.
;
Sabatino, Denise E.
.
NATURE BIOTECHNOLOGY,
2021, 39 (01)
:47-55

Nguyen, Giang N.
论文数: 0 引用数: 0
h-index: 0
机构:
Childrens Hosp Philadelphia, Raymond G Perelman Ctr Cellular & Mol Therapeut, Philadelphia, PA 19104 USA Childrens Hosp Philadelphia, Raymond G Perelman Ctr Cellular & Mol Therapeut, Philadelphia, PA 19104 USA

Everett, John K.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Penn, Dept Microbiol, Perelman Sch Med, Philadelphia, PA 19104 USA Childrens Hosp Philadelphia, Raymond G Perelman Ctr Cellular & Mol Therapeut, Philadelphia, PA 19104 USA

Kafle, Samita
论文数: 0 引用数: 0
h-index: 0
机构:
Childrens Hosp Philadelphia, Raymond G Perelman Ctr Cellular & Mol Therapeut, Philadelphia, PA 19104 USA Childrens Hosp Philadelphia, Raymond G Perelman Ctr Cellular & Mol Therapeut, Philadelphia, PA 19104 USA

Roche, Aoife M.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Penn, Dept Microbiol, Perelman Sch Med, Philadelphia, PA 19104 USA Childrens Hosp Philadelphia, Raymond G Perelman Ctr Cellular & Mol Therapeut, Philadelphia, PA 19104 USA

Raymond, Hayley E.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Penn, Dept Microbiol, Perelman Sch Med, Philadelphia, PA 19104 USA Childrens Hosp Philadelphia, Raymond G Perelman Ctr Cellular & Mol Therapeut, Philadelphia, PA 19104 USA

Leiby, Jacob
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Penn, Dept Microbiol, Perelman Sch Med, Philadelphia, PA 19104 USA Childrens Hosp Philadelphia, Raymond G Perelman Ctr Cellular & Mol Therapeut, Philadelphia, PA 19104 USA

Wood, Christian
论文数: 0 引用数: 0
h-index: 0
机构:
Childrens Hosp Philadelphia, Raymond G Perelman Ctr Cellular & Mol Therapeut, Philadelphia, PA 19104 USA Childrens Hosp Philadelphia, Raymond G Perelman Ctr Cellular & Mol Therapeut, Philadelphia, PA 19104 USA

Assenmacher, Charles-Antoine
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Penn, Sch Vet Med, Dept Pathobiol, Philadelphia, PA 19104 USA Childrens Hosp Philadelphia, Raymond G Perelman Ctr Cellular & Mol Therapeut, Philadelphia, PA 19104 USA

Merricks, Elizabeth P.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ N Carolina, Dept Pathol & Lab Med, Chapel Hill, NC 27515 USA
Univ N Carolina, Sch Med, UNC Blood Res Ctr, Chapel Hill, NC 27515 USA Childrens Hosp Philadelphia, Raymond G Perelman Ctr Cellular & Mol Therapeut, Philadelphia, PA 19104 USA

Long, C. Tyler
论文数: 0 引用数: 0
h-index: 0
机构:
Univ N Carolina, Dept Pathol & Lab Med, Chapel Hill, NC 27515 USA
Univ N Carolina, Sch Med, UNC Blood Res Ctr, Chapel Hill, NC 27515 USA Childrens Hosp Philadelphia, Raymond G Perelman Ctr Cellular & Mol Therapeut, Philadelphia, PA 19104 USA

Kazazian, Haig H.
论文数: 0 引用数: 0
h-index: 0
机构:
Johns Hopkins Sch Med, Dept Genet Med, Baltimore, MD USA Childrens Hosp Philadelphia, Raymond G Perelman Ctr Cellular & Mol Therapeut, Philadelphia, PA 19104 USA

Nichols, Timothy C.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ N Carolina, Dept Pathol & Lab Med, Chapel Hill, NC 27515 USA
Univ N Carolina, Sch Med, UNC Blood Res Ctr, Chapel Hill, NC 27515 USA Childrens Hosp Philadelphia, Raymond G Perelman Ctr Cellular & Mol Therapeut, Philadelphia, PA 19104 USA

Bushman, Frederic D.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Penn, Dept Microbiol, Perelman Sch Med, Philadelphia, PA 19104 USA Childrens Hosp Philadelphia, Raymond G Perelman Ctr Cellular & Mol Therapeut, Philadelphia, PA 19104 USA

Sabatino, Denise E.
论文数: 0 引用数: 0
h-index: 0
机构:
Childrens Hosp Philadelphia, Raymond G Perelman Ctr Cellular & Mol Therapeut, Philadelphia, PA 19104 USA
Univ Penn, Dept Pediat, Div Hematol, Perelman Sch Med, Philadelphia, PA 19104 USA Childrens Hosp Philadelphia, Raymond G Perelman Ctr Cellular & Mol Therapeut, Philadelphia, PA 19104 USA