共 50 条
- [1] Retinal gene therapy in RPE-65 gene mediated inherited retinal dystrophy Eye, 2023, 37 : 1874 - 1877
- [3] Thalassaemia: NICE recommends "life changing" gene editing therapy BMJ-BRITISH MEDICAL JOURNAL, 2024, 386
- [4] NICE recommends new gene therapy for adults with haemophilia B BMJ-BRITISH MEDICAL JOURNAL, 2024, 385