SIG-007: Novel encapsulated non-viral cell-based therapy for Fabry disease

被引：0

作者：

Fluharty, Brian ^{[1
]}

Tietz, Drew ^{[1
]}

Jansen, Lauren ^{[1
]}

Huang, Janet ^{[1
]}

Li, Jie ^{[1
]}

Schladenhauffen, Jacob ^{[1
]}

McAuliffe, Michele ^{[1
]}

Kelley, Elizabeth ^{[1
]}

Glyptis, Tina ^{[1
]}

Barrett, Verna Zhao Kathleen ^{[1
]}

Drapeau, Susan ^{[1
]}

Smith, Devyn ^{[1
]}

Makino, Elina ^{[1
]}

机构：

[1] Sigilon Therapeut, Cambridge, MA USA

来源：

MOLECULAR GENETICS AND METABOLISM | 2021年 / 132卷 / 02期

关键词：

D O I：

10.1016/j.ymgme.2020.12.079

中图分类号：

R5 [内科学];

学科分类号：

1002 ; 100201 ;

摘要：

引用

页码：S39 / S39

页数：1

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