OUTCOMES IN SPINAL MUSCULAR ATROPHY INFANTS ON NUSINERSEN THERAPY

被引:0
|
作者
Kaltman, Joshua
Verma, Sumit
机构
关键词
D O I
暂无
中图分类号
R74 [神经病学与精神病学];
学科分类号
摘要
12
引用
收藏
页码:S7 / S7
页数:1
相关论文
共 50 条
  • [2] Nusinersen for spinal muscular atrophy
    Wurster, Claudia D.
    Ludolph, Albert C.
    THERAPEUTIC ADVANCES IN NEUROLOGICAL DISORDERS, 2018, 11
  • [3] Nusinersen: A Treatment for Spinal Muscular Atrophy
    Claborn, Melanie K.
    Stevens, Debra L.
    Walker, Cheri K.
    Gildon, Brooke L.
    ANNALS OF PHARMACOTHERAPY, 2019, 53 (01) : 61 - 69
  • [4] NUSINERSEN IN THE TREATMENT OF SPINAL MUSCULAR ATROPHY
    Sinko Gabriella
    Kiss Zsuzsanna
    Kalman Bernadette
    IDEGGYOGYASZATI SZEMLE-CLINICAL NEUROSCIENCE, 2018, 71 (3-4): : 90 - 94
  • [5] Nusinersen (Spinraza) for Spinal Muscular Atrophy
    不详
    MEDICAL LETTER ON DRUGS AND THERAPEUTICS, 2017, 59 (1517): : 50 - 52
  • [6] Nutritional Therapy in Children With Spinal Muscular Atrophy in the Era of Nusinersen
    Yerushalmy-Feler, Anat
    Levy, Dina
    Sagi, Liora
    Fattal-Valevski, Aviva
    Shiff, Yaffa Elbaum
    Brener, Avivit
    Cohen, Shlomi
    JOURNAL OF PEDIATRIC GASTROENTEROLOGY AND NUTRITION, 2021, 72 (06): : E154 - E160
  • [7] Nusinersen for adults with spinal muscular atrophy
    Arslan, Doruk
    Inan, Berin
    Kilinc, Muhammed
    Bekircan-Kurt, Can Ebru
    Erdem-Ozdamar, Sevim
    Tan, Ersin
    NEUROLOGICAL SCIENCES, 2023, 44 (07) : 2393 - 2400
  • [8] Nusinersen for adults with spinal muscular atrophy
    Doruk Arslan
    Berin Inan
    Muhammed Kilinc
    Can Ebru Bekircan-Kurt
    Sevim Erdem-Ozdamar
    Ersin Tan
    Neurological Sciences, 2023, 44 : 2393 - 2400
  • [9] Nusinersen for the treatment of spinal muscular atrophy
    Chiriboga, Claudia A.
    EXPERT REVIEW OF NEUROTHERAPEUTICS, 2017, 17 (10) : 955 - 962
  • [10] Treatment expectations and patient-reported outcomes of nusinersen therapy in adult spinal muscular atrophy
    Osmanovic, Alma
    Ranxha, Gresa
    Kumpe, Mareike
    Mueschen, Lars
    Binz, Camilla
    Wiehler, Flavia
    Paracka, Lejla
    Koerner, Sonja
    Kollewe, Katja
    Petri, Susanne
    Schreiber-Katz, Olivia
    JOURNAL OF NEUROLOGY, 2020, 267 (08) : 2398 - 2407