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- [6] Nutritional Therapy in Children With Spinal Muscular Atrophy in the Era of Nusinersen JOURNAL OF PEDIATRIC GASTROENTEROLOGY AND NUTRITION, 2021, 72 (06): : E154 - E160
- [8] Nusinersen for adults with spinal muscular atrophy Neurological Sciences, 2023, 44 : 2393 - 2400