AAV Therapy Attenuates Respiratory Dysfunction in a Novel Rat Model of Pompe Disease

被引：0

作者：

Mahajan, Bhuvna ^{[1
]}

Vaught, Lauren A. ^{[1
]}

Todd, A. Gary ^{[2
]}

Duncanson, Lauren A. ^{[1
]}

Doyle, Brendan ^{[3
]}

Fuller, David D. ^{[3
]}

Byrne, Barry J. ^{[1
]}

Falk, Darin J. ^{[1
]}

机构：

[1] Univ Florida, Pediat, Gainesville, FL USA

[2] Univ Florida, Pharmacol & Therapeut, Gainesville, FL USA

[3] Univ Florida, Phys Therapy, Gainesville, FL USA

来源：

MOLECULAR THERAPY | 2018年 / 26卷 / 05期

关键词：

D O I：

暂无

中图分类号：

Q81 [生物工程学（生物技术）]; Q93 [微生物学];

学科分类号：

071005 ; 0836 ; 090102 ; 100705 ;

摘要：

356

引用

页码：166 / 166

页数：1

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