AAV Therapy Attenuates Respiratory Dysfunction in a Novel Rat Model of Pompe Disease

被引：0
作者：
Mahajan, Bhuvna [1 ]
Vaught, Lauren A. [1 ]
Todd, A. Gary [2 ]
Duncanson, Lauren A. [1 ]
Doyle, Brendan [3 ]
Fuller, David D. [3 ]
Byrne, Barry J. [1 ]
Falk, Darin J. [1 ]
机构：
[1] Univ Florida, Pediat, Gainesville, FL USA
[2] Univ Florida, Pharmacol & Therapeut, Gainesville, FL USA
[3] Univ Florida, Phys Therapy, Gainesville, FL USA
来源：
MOLECULAR THERAPY | 2018年 / 26卷 / 05期
关键词：
D O I：
暂无
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
356
引用
收藏
页码：166 / 166
页数：1
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