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- [41] Autologous Ex Vivo Lentiviral Gene Therapy for Adenosine Deaminase DeficiencyNEW ENGLAND JOURNAL OF MEDICINE, 2021, 384 (21) : 2002 - 2013Kohn, D. B.论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Los Angeles, Dept Microbiol Immunol & Mol Genet, 3163 Terasaki Life Sci Bldg, Los Angeles, CA 90095 USA Univ Calif Los Angeles, Dept Pediat, Los Angeles, CA USA Univ Calif Los Angeles, Eli & Edythe Broad Ctr Regenerat Med & Stem Cell, Los Angeles, CA USA Univ Calif Los Angeles, Dept Microbiol Immunol & Mol Genet, 3163 Terasaki Life Sci Bldg, Los Angeles, CA 90095 USABooth, C.论文数: 0 引用数: 0 h-index: 0机构: UCL, Great Ormond St Inst Child Hlth, London, England Great Ormond St Hosp Children NHS Fdn Trust, London, England Univ Calif Los Angeles, Dept Microbiol Immunol & Mol Genet, 3163 Terasaki Life Sci Bldg, Los Angeles, CA 90095 USAShaw, K. L.论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Los Angeles, Dept Microbiol Immunol & Mol Genet, 3163 Terasaki Life Sci Bldg, Los Angeles, CA 90095 USA Univ Calif Los Angeles, Dept Microbiol Immunol & Mol Genet, 3163 Terasaki Life Sci Bldg, Los Angeles, CA 90095 USAXu-Bayford, J.论文数: 0 引用数: 0 h-index: 0机构: UCL, Great Ormond St Inst Child Hlth, London, England Great Ormond St Hosp Children NHS Fdn Trust, London, England Univ Calif Los Angeles, Dept Microbiol Immunol & Mol Genet, 3163 Terasaki Life Sci Bldg, Los Angeles, CA 90095 USAGarabedian, E.论文数: 0 引用数: 0 h-index: 0机构: NHGRI, NIH, Bethesda, MD 20892 USA Univ Calif Los Angeles, Dept Microbiol Immunol & Mol Genet, 3163 Terasaki Life Sci Bldg, Los Angeles, CA 90095 USATrevisan, V.论文数: 0 引用数: 0 h-index: 0机构: UCL, Great Ormond St Inst Child Hlth, London, England Great Ormond St Hosp Children NHS Fdn Trust, London, England Univ Calif Los Angeles, Dept Microbiol Immunol & Mol Genet, 3163 Terasaki Life Sci Bldg, Los Angeles, CA 90095 USACarbonaro-Sarracino, D. A.论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Los Angeles, Dept Microbiol Immunol & Mol Genet, 3163 Terasaki Life Sci Bldg, Los Angeles, CA 90095 USA Orchard Therapeut Europe, London, England Univ Calif Los Angeles, Dept Microbiol Immunol & Mol Genet, 3163 Terasaki Life Sci Bldg, Los Angeles, CA 90095 USASoni, K.论文数: 0 引用数: 0 h-index: 0机构: UCL, Great Ormond St Inst Child Hlth, London, England Great Ormond St Hosp Children NHS Fdn Trust, London, England Univ Calif Los Angeles, Dept Microbiol Immunol & Mol Genet, 3163 Terasaki Life Sci Bldg, Los Angeles, CA 90095 USATerrazas, D.论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Los Angeles, Dept Microbiol Immunol & Mol Genet, 3163 Terasaki Life Sci Bldg, Los Angeles, CA 90095 USA Univ Calif Los Angeles, Dept Microbiol Immunol & Mol Genet, 3163 Terasaki Life Sci Bldg, Los Angeles, CA 90095 USASnell, K.论文数: 0 引用数: 0 h-index: 0机构: UCL, Great Ormond St Inst Child Hlth, London, England Great Ormond St Hosp Children NHS Fdn Trust, London, England Univ Calif Los Angeles, Dept Microbiol Immunol & Mol Genet, 3163 Terasaki Life Sci Bldg, Los Angeles, CA 90095 USAIkeda, A.论文数: 0 引用数: 0 h-index: 0机构: Cure 4 Kids Fdn, Las Vegas, NV USA Univ Calif Los Angeles, Dept Microbiol Immunol & Mol Genet, 3163 Terasaki Life Sci Bldg, Los Angeles, CA 90095 USALeon-Rico, D.论文数: 0 引用数: 0 h-index: 0机构: UCL, Great Ormond St Inst Child Hlth, London, England Great Ormond St Hosp Children NHS Fdn Trust, London, England Univ Calif Los Angeles, Dept Microbiol Immunol & Mol Genet, 3163 Terasaki Life Sci Bldg, Los Angeles, CA 90095 USAMoore, T. B.论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Los Angeles, Dept Pediat, Los Angeles, CA USA Univ Calif Los Angeles, Dept Microbiol Immunol & Mol Genet, 3163 Terasaki Life Sci Bldg, Los Angeles, CA 90095 USABuckland, K. F.论文数: 0 引用数: 0 h-index: 0机构: UCL, Great Ormond St Inst Child Hlth, London, England Great Ormond St Hosp Children NHS Fdn Trust, London, England Univ Calif Los Angeles, Dept Microbiol Immunol & Mol Genet, 3163 Terasaki Life Sci Bldg, Los Angeles, CA 90095 USAShah, A. J.论文数: 0 引用数: 0 h-index: 0机构: Stanford Sch Med, Palo Alto, CA USA Univ Calif Los Angeles, Dept Microbiol Immunol & Mol Genet, 3163 Terasaki Life Sci Bldg, Los Angeles, CA 90095 USAGilmour, K. C.论文数: 0 引用数: 0 h-index: 0机构: UCL, Great Ormond St Inst Child Hlth, London, England Great Ormond St Hosp Children NHS Fdn Trust, London, England Univ Calif Los Angeles, Dept Microbiol Immunol & Mol Genet, 3163 Terasaki Life Sci Bldg, Los Angeles, CA 90095 USADe Oliveira, S.论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Los Angeles, Dept Pediat, Los Angeles, CA USA Univ Calif Los Angeles, Dept Microbiol Immunol & Mol Genet, 3163 Terasaki Life Sci Bldg, Los Angeles, CA 90095 USARivat, C.论文数: 0 引用数: 0 h-index: 0机构: UCL, Great Ormond St Inst Child Hlth, London, England Great Ormond St Hosp Children NHS Fdn Trust, London, England Univ Calif Los Angeles, Dept Microbiol Immunol & Mol Genet, 3163 Terasaki Life Sci Bldg, Los Angeles, CA 90095 USACrooks, G. M.论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Los Angeles, Dept Pathol & Lab Med, Los Angeles, CA USA Univ Calif Los Angeles, Eli & Edythe Broad Ctr Regenerat Med & Stem Cell, Los Angeles, CA USA Univ Calif Los Angeles, Dept Microbiol Immunol & Mol Genet, 3163 Terasaki Life Sci Bldg, Los Angeles, CA 90095 USAIzotova, N.论文数: 0 引用数: 0 h-index: 0机构: UCL, Great Ormond St Inst Child Hlth, London, England Great Ormond St Hosp Children NHS Fdn Trust, London, England Univ Calif Los Angeles, Dept Microbiol Immunol & Mol Genet, 3163 Terasaki Life Sci Bldg, Los Angeles, CA 90095 USATse, J.论文数: 0 引用数: 0 h-index: 0机构: Ronald Reagan UCLA Med Ctr, Dept Pharmaceut Serv, Los Angeles, CA USA Univ Calif Los Angeles, Dept Microbiol Immunol & Mol Genet, 3163 Terasaki Life Sci Bldg, Los Angeles, CA 90095 USAAdams, S.论文数: 0 引用数: 0 h-index: 0机构: Great Ormond St Hosp Children NHS Fdn Trust, London, England Univ Calif Los Angeles, Dept Microbiol Immunol & Mol Genet, 3163 Terasaki Life Sci Bldg, Los Angeles, CA 90095 USAShupien, S.论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Los Angeles, Dept Pediat, Los Angeles, CA USA Univ Calif Los Angeles, Dept Microbiol Immunol & Mol Genet, 3163 Terasaki Life Sci Bldg, Los Angeles, CA 90095 USARicketts, H.论文数: 0 引用数: 0 h-index: 0机构: UCL, Great Ormond St Inst Child Hlth, London, England Great Ormond St Hosp Children NHS Fdn Trust, London, England Univ Calif Los Angeles, Dept Microbiol Immunol & Mol Genet, 3163 Terasaki Life Sci Bldg, Los Angeles, CA 90095 USADavila, A.论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Los Angeles, Dept Microbiol Immunol & Mol Genet, 3163 Terasaki Life Sci Bldg, Los Angeles, CA 90095 USA Univ Calif Los Angeles, Dept Microbiol Immunol & Mol Genet, 3163 Terasaki Life Sci Bldg, Los Angeles, CA 90095 USAUzowuru, C.论文数: 0 引用数: 0 h-index: 0机构: UCL, Great Ormond St Inst Child Hlth, London, England Great Ormond St Hosp Children NHS Fdn Trust, London, England Univ Calif Los Angeles, Dept Microbiol Immunol & Mol Genet, 3163 Terasaki Life Sci Bldg, Los Angeles, CA 90095 USAIcreverzi, A.论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Los Angeles, Dept Microbiol Immunol & Mol Genet, 3163 Terasaki Life Sci Bldg, Los Angeles, CA 90095 USA Univ Calif Los Angeles, Dept Microbiol Immunol & Mol Genet, 3163 Terasaki Life Sci Bldg, Los Angeles, CA 90095 USABarman, P.论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Los Angeles, Dept Microbiol Immunol & Mol Genet, 3163 Terasaki Life Sci Bldg, Los Angeles, CA 90095 USA Univ Calif Los Angeles, Dept Microbiol Immunol & Mol Genet, 3163 Terasaki Life Sci Bldg, Los Angeles, CA 90095 USAFernandez, B. Campo论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Los Angeles, Dept Microbiol Immunol & Mol Genet, 3163 Terasaki Life Sci Bldg, Los Angeles, CA 90095 USA Univ Calif Los Angeles, Dept Microbiol Immunol & Mol Genet, 3163 Terasaki Life Sci Bldg, Los Angeles, CA 90095 USAHollis, R. P.论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Los Angeles, Dept Microbiol Immunol & Mol Genet, 3163 Terasaki Life Sci Bldg, Los Angeles, CA 90095 USA Univ Calif Los Angeles, Dept Microbiol Immunol & Mol Genet, 3163 Terasaki Life Sci Bldg, Los Angeles, CA 90095 USACoronel, M.论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Los Angeles, Dept Microbiol Immunol & Mol Genet, 3163 Terasaki Life Sci Bldg, Los Angeles, CA 90095 USA Univ Calif Los Angeles, Dept Microbiol Immunol & Mol Genet, 3163 Terasaki Life Sci Bldg, Los Angeles, CA 90095 USAYu, A.论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Los Angeles, Dept Microbiol Immunol & Mol Genet, 3163 Terasaki Life Sci Bldg, Los Angeles, CA 90095 USA Univ Calif Los Angeles, Dept Microbiol Immunol & Mol Genet, 3163 Terasaki Life Sci Bldg, Los Angeles, CA 90095 USAChun, K. M.论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Los Angeles, Dept Microbiol Immunol & Mol Genet, 3163 Terasaki Life Sci Bldg, Los Angeles, CA 90095 USA Univ Calif Los Angeles, Dept Microbiol Immunol & Mol Genet, 3163 Terasaki Life Sci Bldg, Los Angeles, CA 90095 USACasas, C. E.论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Los Angeles, Dept Microbiol Immunol & Mol Genet, 3163 Terasaki Life Sci Bldg, Los Angeles, CA 90095 USA Univ Calif Los Angeles, Dept Microbiol Immunol & Mol Genet, 3163 Terasaki Life Sci Bldg, Los Angeles, CA 90095 USAZhang, R.论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Los Angeles, Dept Microbiol Immunol & Mol Genet, 3163 Terasaki Life Sci Bldg, Los Angeles, CA 90095 USA Univ Calif Los Angeles, Dept Microbiol Immunol & Mol Genet, 3163 Terasaki Life Sci Bldg, Los Angeles, CA 90095 USAArduini, S.论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Los Angeles, Dept Microbiol Immunol & Mol Genet, 3163 Terasaki Life Sci Bldg, Los Angeles, CA 90095 USALynn, F.论文数: 0 引用数: 0 h-index: 0机构: Orchard Therapeut Europe, London, England Univ Calif Los Angeles, Dept Microbiol Immunol & Mol Genet, 3163 Terasaki Life Sci Bldg, Los Angeles, CA 90095 USAKudari, M.论文数: 0 引用数: 0 h-index: 0机构: Orchard Therapeut Europe, London, England Univ Calif Los Angeles, Dept Microbiol Immunol & Mol Genet, 3163 Terasaki Life Sci Bldg, Los Angeles, CA 90095 USASpezzi, A.论文数: 0 引用数: 0 h-index: 0机构: Orchard Therapeut Europe, London, England Univ Calif Los Angeles, Dept Microbiol Immunol & Mol Genet, 3163 Terasaki Life Sci Bldg, Los Angeles, CA 90095 USAZahn, M.论文数: 0 引用数: 0 h-index: 0机构: GeneWerk, Heidelberg, Germany German Canc Res Ctr, Heidelberg, Germany Natl Ctr Tumor Dis, Heidelberg, Germany Univ Calif Los Angeles, Dept Microbiol Immunol & Mol Genet, 3163 Terasaki Life Sci Bldg, Los Angeles, CA 90095 USAHeimke, R.论文数: 0 引用数: 0 h-index: 0机构: GeneWerk, Heidelberg, Germany Univ Calif Los Angeles, Dept Microbiol Immunol & Mol Genet, 3163 Terasaki Life Sci Bldg, Los Angeles, CA 90095 USALabik, I.论文数: 0 引用数: 0 h-index: 0机构: GeneWerk, Heidelberg, Germany Univ Calif Los Angeles, Dept Microbiol Immunol & Mol Genet, 3163 Terasaki Life Sci Bldg, Los Angeles, CA 90095 USAParrott, R.论文数: 0 引用数: 0 h-index: 0机构: Duke Univ, Durham, NC USA Univ Calif Los Angeles, Dept Microbiol Immunol & Mol Genet, 3163 Terasaki Life Sci Bldg, Los Angeles, CA 90095 USABuckley, R. H.论文数: 0 引用数: 0 h-index: 0机构: Duke Univ, Durham, NC USA Univ Calif Los Angeles, Dept Microbiol Immunol & Mol Genet, 3163 Terasaki Life Sci Bldg, Los Angeles, CA 90095 USAReeves, L.论文数: 0 引用数: 0 h-index: 0机构: Cincinnati Childrens Hosp Med Ctr, Cincinnati, OH 45229 USA Univ Calif Los Angeles, Dept Microbiol Immunol & Mol Genet, 3163 Terasaki Life Sci Bldg, Los Angeles, CA 90095 USACornetta, K.论文数: 0 引用数: 0 h-index: 0机构: Indiana Univ Sch Med, Indianapolis, IN 46202 USA Univ Calif Los Angeles, Dept Microbiol Immunol & Mol Genet, 3163 Terasaki Life Sci Bldg, Los Angeles, CA 90095 USASokolic, R.论文数: 0 引用数: 0 h-index: 0机构: NHGRI, NIH, Bethesda, MD 20892 USA Univ Calif Los Angeles, Dept Microbiol Immunol & Mol Genet, 3163 Terasaki Life Sci Bldg, Los Angeles, CA 90095 USAHershfield, M.论文数: 0 引用数: 0 h-index: 0机构: Duke Univ, Durham, NC USA Univ Calif Los Angeles, Dept Microbiol Immunol & Mol Genet, 3163 Terasaki Life Sci Bldg, Los Angeles, CA 90095 USASchmidt, M.论文数: 0 引用数: 0 h-index: 0机构: GeneWerk, Heidelberg, Germany German Canc Res Ctr, Heidelberg, Germany Natl Ctr Tumor Dis, Heidelberg, Germany Univ Calif Los Angeles, Dept Microbiol Immunol & Mol Genet, 3163 Terasaki Life Sci Bldg, Los Angeles, CA 90095 USA论文数: 引用数: h-index:机构:
- [42] Gene therapy for adenosine deaminase-deficient severe combined immune deficiency: clinical comparison of retroviral vectors and treatment plansBLOOD, 2012, 120 (18) : 3635 - 3646Candotti, Fabio论文数: 0 引用数: 0 h-index: 0机构: NHGRI, Genet & Mol Biol Branch, NIH, Bethesda, MD 20892 USA NHGRI, Genet & Mol Biol Branch, NIH, Bethesda, MD 20892 USAShaw, Kit L.论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Los Angeles, David Geffen Sch Med, Dept Microbiol Immunol & Mol Genet, Los Angeles, CA 90095 USA NHGRI, Genet & Mol Biol Branch, NIH, Bethesda, MD 20892 USAMuul, Linda论文数: 0 引用数: 0 h-index: 0机构: NHGRI, Genet & Mol Biol Branch, NIH, Bethesda, MD 20892 USA NHGRI, Genet & Mol Biol Branch, NIH, Bethesda, MD 20892 USACarbonaro, Denise论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Los Angeles, David Geffen Sch Med, Dept Microbiol Immunol & Mol Genet, Los Angeles, CA 90095 USA NHGRI, Genet & Mol Biol Branch, NIH, Bethesda, MD 20892 USASokolic, Robert论文数: 0 引用数: 0 h-index: 0机构: NHGRI, Genet & Mol Biol Branch, NIH, Bethesda, MD 20892 USA NHGRI, Genet & Mol Biol Branch, NIH, Bethesda, MD 20892 USAChoi, Christopher论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Los Angeles, David Geffen Sch Med, Dept Microbiol Immunol & Mol Genet, Los Angeles, CA 90095 USA NHGRI, Genet & Mol Biol Branch, NIH, Bethesda, MD 20892 USASchurman, Shepherd H.论文数: 0 引用数: 0 h-index: 0机构: NHGRI, Genet & Mol Biol Branch, NIH, Bethesda, MD 20892 USA NHGRI, Genet & Mol Biol Branch, NIH, Bethesda, MD 20892 USAGarabedian, Elizabeth论文数: 0 引用数: 0 h-index: 0机构: NHGRI, Genet & Mol Biol Branch, NIH, Bethesda, MD 20892 USA NHGRI, Genet & Mol Biol Branch, NIH, Bethesda, MD 20892 USAKesserwan, Chimene论文数: 0 引用数: 0 h-index: 0机构: NHGRI, Genet & Mol Biol Branch, NIH, Bethesda, MD 20892 USA NHGRI, Genet & Mol Biol Branch, NIH, Bethesda, MD 20892 USAJagadeesh, G. Jayashree论文数: 0 引用数: 0 h-index: 0机构: NHGRI, Genet & Mol Biol Branch, NIH, Bethesda, MD 20892 USA NHGRI, Genet & Mol Biol Branch, NIH, Bethesda, MD 20892 USAFu, Pei-Yu论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Los Angeles, David Geffen Sch Med, Dept Microbiol Immunol & Mol Genet, Los Angeles, CA 90095 USA NHGRI, Genet & Mol Biol Branch, NIH, Bethesda, MD 20892 USAGschweng, Eric论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Los Angeles, David Geffen Sch Med, Dept Microbiol Immunol & Mol Genet, Los Angeles, CA 90095 USA NHGRI, Genet & Mol Biol Branch, NIH, Bethesda, MD 20892 USACooper, Aaron论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Los Angeles, David Geffen Sch Med, Mol Biol Interdept PhD Program, Los Angeles, CA 90095 USA NHGRI, Genet & Mol Biol Branch, NIH, Bethesda, MD 20892 USATisdale, John F.论文数: 0 引用数: 0 h-index: 0机构: NIDDKD, Mol & Clin Hematol Branch, NIH, Bethesda, MD 20892 USA NHGRI, Genet & Mol Biol Branch, NIH, Bethesda, MD 20892 USAWeinberg, Kenneth I.论文数: 0 引用数: 0 h-index: 0机构: Stanford Sch Med, Dept Pediat, Stanford, CA USA NHGRI, Genet & Mol Biol Branch, NIH, Bethesda, MD 20892 USACrooks, Gay M.论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Los Angeles, David Geffen Sch Med, Dept Pathol & Lab Med, Los Angeles, CA 90095 USA NHGRI, Genet & Mol Biol Branch, NIH, Bethesda, MD 20892 USAKapoor, Neena论文数: 0 引用数: 0 h-index: 0机构: Univ So Calif, Keck Sch Med, Childrens Hosp Los Angeles, Div Res Immunol Bone Marrow Transplant,Dept Pedia, Los Angeles, CA 90033 USA NHGRI, Genet & Mol Biol Branch, NIH, Bethesda, MD 20892 USAShah, Ami论文数: 0 引用数: 0 h-index: 0机构: Univ So Calif, Keck Sch Med, Childrens Hosp Los Angeles, Div Res Immunol Bone Marrow Transplant,Dept Pedia, Los Angeles, CA 90033 USA NHGRI, Genet & Mol Biol Branch, NIH, Bethesda, MD 20892 USAAbdel-Azim, Hisham论文数: 0 引用数: 0 h-index: 0机构: Univ So Calif, Keck Sch Med, Childrens Hosp Los Angeles, Div Res Immunol Bone Marrow Transplant,Dept Pedia, Los Angeles, CA 90033 USA NHGRI, Genet & Mol Biol Branch, NIH, Bethesda, MD 20892 USAYu, Xiao-Jin论文数: 0 引用数: 0 h-index: 0机构: Univ So Calif, Keck Sch Med, Childrens Hosp Los Angeles, Div Res Immunol Bone Marrow Transplant,Dept Pedia, Los Angeles, CA 90033 USA NHGRI, Genet & Mol Biol Branch, NIH, Bethesda, MD 20892 USASmogorzewska, Monika论文数: 0 引用数: 0 h-index: 0机构: Univ So Calif, Keck Sch Med, Childrens Hosp Los Angeles, Div Res Immunol Bone Marrow Transplant,Dept Pedia, Los Angeles, CA 90033 USA NHGRI, Genet & Mol Biol Branch, NIH, Bethesda, MD 20892 USAWayne, Alan S.论文数: 0 引用数: 0 h-index: 0机构: NCI, Hematol Dis Sect, Pediat Oncol Branch, NIH, Bethesda, MD 20892 USA NHGRI, Genet & Mol Biol Branch, NIH, Bethesda, MD 20892 USARosenblatt, Howard M.论文数: 0 引用数: 0 h-index: 0机构: Dell Childrens Med Ctr Cent Texas, Austin, TX USA NHGRI, Genet & Mol Biol Branch, NIH, Bethesda, MD 20892 USADavis, Carla M.论文数: 0 引用数: 0 h-index: 0机构: Texas Childrens Hosp, Dept Pediat, Sect Allergy & Immunol, Houston, TX 77030 USA NHGRI, Genet & Mol Biol Branch, NIH, Bethesda, MD 20892 USAHanson, Celine论文数: 0 引用数: 0 h-index: 0机构: Texas Childrens Hosp, Dept Pediat, Sect Allergy & Immunol, Houston, TX 77030 USA NHGRI, Genet & Mol Biol Branch, NIH, Bethesda, MD 20892 USARishi, Radha G.论文数: 0 引用数: 0 h-index: 0机构: Arizona Allergy Associates, Scottsdale, AZ USA NHGRI, Genet & Mol Biol Branch, NIH, Bethesda, MD 20892 USAWang, Xiaoyan论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Los Angeles, Sch Publ Hlth, Dept Biostat, Los Angeles, CA 90024 USA NHGRI, Genet & Mol Biol Branch, NIH, Bethesda, MD 20892 USAGjertson, David论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Los Angeles, David Geffen Sch Med, Dept Pathol & Lab Med, Los Angeles, CA 90095 USA Univ Calif Los Angeles, Sch Publ Hlth, Dept Biostat, Los Angeles, CA 90024 USA NHGRI, Genet & Mol Biol Branch, NIH, Bethesda, MD 20892 USAYang, Otto O.论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Los Angeles, David Geffen Sch Med, Dept Med, Div Infect Dis, Los Angeles, CA 90095 USA NHGRI, Genet & Mol Biol Branch, NIH, Bethesda, MD 20892 USABalamurugan, Arumugam论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Los Angeles, David Geffen Sch Med, Dept Med, Div Infect Dis, Los Angeles, CA 90095 USA NHGRI, Genet & Mol Biol Branch, NIH, Bethesda, MD 20892 USABauer, Gerhard论文数: 0 引用数: 0 h-index: 0机构: Calif State Univ Sacramento, Davis Sch Med, Dept Internal Med, Div Hematol Oncol, Sacramento, CA 95819 USA NHGRI, Genet & Mol Biol Branch, NIH, Bethesda, MD 20892 USAIreland, Joanna A.论文数: 0 引用数: 0 h-index: 0机构: Univ So Calif, Keck Sch Med, Childrens Hosp Los Angeles, Div Res Immunol Bone Marrow Transplant,Dept Pedia, Los Angeles, CA 90033 USA NHGRI, Genet & Mol Biol Branch, NIH, Bethesda, MD 20892 USAEngel, Barbara C.论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp, Philadelphia Res Inst, Philadelphia, PA 19104 USA NHGRI, Genet & Mol Biol Branch, NIH, Bethesda, MD 20892 USAPodsakoff, Gregory M.论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Philadelphia, Div Hematol, Philadelphia, PA USA Childrens Hosp Philadelphia, Ctr Cellular & Mol Therapeut, Philadelphia, PA USA NHGRI, Genet & Mol Biol Branch, NIH, Bethesda, MD 20892 USAHershfield, Michael S.论文数: 0 引用数: 0 h-index: 0机构: Duke Univ, Sch Med, Dept Biochem, Durham, NC USA NHGRI, Genet & Mol Biol Branch, NIH, Bethesda, MD 20892 USABlaese, R. Michael论文数: 0 引用数: 0 h-index: 0机构: Immune Deficiency Fdn, Towson, MD USA NHGRI, Genet & Mol Biol Branch, NIH, Bethesda, MD 20892 USAParkman, Robertson论文数: 0 引用数: 0 h-index: 0机构: Univ So Calif, Keck Sch Med, Childrens Hosp Los Angeles, Div Res Immunol Bone Marrow Transplant,Dept Pedia, Los Angeles, CA 90033 USA NHGRI, Genet & Mol Biol Branch, NIH, Bethesda, MD 20892 USAKohn, Donald B.论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Los Angeles, David Geffen Sch Med, Dept Microbiol Immunol & Mol Genet, Los Angeles, CA 90095 USA Univ Calif Los Angeles, Eli & Edythe Broad Ctr Regenerat Med & Stem Cell, Los Angeles, CA USA NHGRI, Genet & Mol Biol Branch, NIH, Bethesda, MD 20892 USA
- [43] Lentiviral Gene Therapy for Artemis-Deficient SCIDNEW ENGLAND JOURNAL OF MEDICINE, 2022, 387 (25) : 2344 - 2355Cowan, Morton J. J.论文数: 0 引用数: 0 h-index: 0机构: UCSF Benioff Childrens Hosp, Smith Cardiovasc Res Inst, Dept Pediat, Allergy Immunol & Blood & Marrow Transplant Div, 3118,555 Mission Bay Blvd South,Rm 252J, San Francisco, CA 94158 USA UCSF Benioff Childrens Hosp, Smith Cardiovasc Res Inst, Dept Pediat, Allergy Immunol & Blood & Marrow Transplant Div, 3118,555 Mission Bay Blvd South,Rm 252J, San Francisco, CA 94158 USAYu, Jason论文数: 0 引用数: 0 h-index: 0机构: UCSF Benioff Childrens Hosp, Smith Cardiovasc Res Inst, Dept Pediat, Allergy Immunol & Blood & Marrow Transplant Div, 3118,555 Mission Bay Blvd South,Rm 252J, San Francisco, CA 94158 USA UCSF Benioff Childrens Hosp, Smith Cardiovasc Res Inst, Dept Pediat, Allergy Immunol & Blood & Marrow Transplant Div, 3118,555 Mission Bay Blvd South,Rm 252J, San Francisco, CA 94158 USAFacchino, Janelle论文数: 0 引用数: 0 h-index: 0机构: UCSF Benioff Childrens Hosp, Smith Cardiovasc Res Inst, Dept Pediat, Allergy Immunol & Blood & Marrow Transplant Div, 3118,555 Mission Bay Blvd South,Rm 252J, San Francisco, CA 94158 USA UCSF Benioff Childrens Hosp, Smith Cardiovasc Res Inst, Dept Pediat, Allergy Immunol & Blood & Marrow Transplant Div, 3118,555 Mission Bay Blvd South,Rm 252J, San Francisco, CA 94158 USAFraser-Browne, Carol论文数: 0 引用数: 0 h-index: 0机构: UCSF Benioff Childrens Hosp, Smith Cardiovasc Res Inst, Dept Pediat, Allergy Immunol & Blood & Marrow Transplant Div, 3118,555 Mission Bay Blvd South,Rm 252J, San Francisco, CA 94158 USA UCSF Benioff Childrens Hosp, Smith Cardiovasc Res Inst, Dept Pediat, Allergy Immunol & Blood & Marrow Transplant Div, 3118,555 Mission Bay Blvd South,Rm 252J, San Francisco, CA 94158 USASanford, Ukina论文数: 0 引用数: 0 h-index: 0机构: UCSF Benioff Childrens Hosp, Smith Cardiovasc Res Inst, Dept Pediat, Allergy Immunol & Blood & Marrow Transplant Div, 3118,555 Mission Bay Blvd South,Rm 252J, San Francisco, CA 94158 USA UCSF Benioff Childrens Hosp, Smith Cardiovasc Res Inst, Dept Pediat, Allergy Immunol & Blood & Marrow Transplant 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- [44] Fetal stem cell and gene therapySEMINARS IN FETAL & NEONATAL MEDICINE, 2017, 22 (06) : 410 - 414Witt, Russell论文数: 0 引用数: 0 h-index: 0机构: Univ Calif San Francisco, Div Pediat Surg, San Francisco, CA 94143 USA Univ Calif San Francisco, Div Pediat Surg, San Francisco, CA 94143 USAMacKenzie, Tippi C.论文数: 0 引用数: 0 h-index: 0机构: Univ Calif San Francisco, Div Pediat Surg, San Francisco, CA 94143 USA Univ Calif San Francisco, Div Pediat Surg, San Francisco, CA 94143 USAPeranteau, William H.论文数: 0 引用数: 0 h-index: 0机构: Univ Penn, Childrens Hosp Philadelphia, Div Pediat Gen Thorac & Fetal Surg, Perelman Sch Med, 3615 Civ Ctr Blvd,ARC 1116E, Philadelphia, PA 19104 USA Univ Calif San Francisco, Div Pediat Surg, San Francisco, CA 94143 USA
- [45] Enrichment of Human Hematopoietic Stem/Progenitor Cells Facilitates Transduction for Stem Cell Gene TherapySTEM CELLS, 2015, 33 (05) : 1532 - 1542Baldwin, Kismet论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Los Angeles, Dept Pediat, Childrens Discovery & Innovat Inst, Los Angeles, CA 90024 USA Univ Calif Los Angeles, Dept Pediat, Childrens Discovery & Innovat Inst, Los Angeles, CA 90024 USAUrbinati, Fabrizia论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Los Angeles, Dept Microbiol Immunol & Mol Genet, Los Angeles, CA USA Univ Calif Los Angeles, Dept Pediat, Childrens Discovery & Innovat Inst, Los Angeles, CA 90024 USARomero, Zulema论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Los Angeles, Dept Microbiol Immunol & Mol Genet, Los Angeles, CA USA Univ Calif Los Angeles, Dept Pediat, Childrens Discovery & Innovat Inst, Los Angeles, CA 90024 USACampo-Fernandez, Beatriz论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Los Angeles, Dept Microbiol Immunol & Mol Genet, Los Angeles, CA USA Univ Calif Los Angeles, Dept Pediat, Childrens Discovery & Innovat Inst, Los Angeles, CA 90024 USAKaufman, Michael L.论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Los Angeles, Dept Microbiol Immunol & Mol Genet, Los Angeles, CA USA Univ Calif Los Angeles, Dept Pediat, Childrens Discovery & Innovat Inst, Los Angeles, CA 90024 USACooper, Aaron R.论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Los Angeles, Inst Mol Biol, Los Angeles, CA 90024 USA Univ Calif Los Angeles, Dept Pediat, Childrens Discovery & Innovat Inst, Los Angeles, CA 90024 USAMasiuk, Katelyn论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Los Angeles, Dept Microbiol Immunol & Mol Genet, Los Angeles, CA USA Univ Calif Los Angeles, Dept Pediat, Childrens Discovery & Innovat Inst, Los Angeles, CA 90024 USAHollis, Roger P.论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Los Angeles, Dept Microbiol Immunol & Mol Genet, Los Angeles, CA USA Univ Calif Los Angeles, Dept Pediat, Childrens Discovery & Innovat Inst, Los Angeles, CA 90024 USAKohn, Donald B.论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Los Angeles, Dept Pediat, Childrens Discovery & Innovat Inst, Los Angeles, CA 90024 USA Univ Calif Los Angeles, Dept Microbiol Immunol & Mol Genet, Los Angeles, CA USA Univ Calif Los Angeles, Eli & Edythe Broad Ctr Regenerat Med & Stem Cell, Los Angeles, CA USA Univ Calif Los Angeles, Dept Pediat, Childrens Discovery & Innovat Inst, Los Angeles, CA 90024 USA
- [46] Busulfan Pharmacokinetics in Adenosine Deaminase-Deficient Severe Combined Immunodeficiency Gene TherapyBIOLOGY OF BLOOD AND MARROW TRANSPLANTATION, 2020, 26 (10) : 1819 - 1827Bradford, Kathryn L.论文数: 0 引用数: 0 h-index: 0机构: UCLA, David Geffen Sch Med, Dept Pediat Hematol Oncol, Los Angeles, CA 90095 USA UCLA, David Geffen Sch Med, Dept Pediat Hematol Oncol, Los Angeles, CA 90095 USALiu, Siyu论文数: 0 引用数: 0 h-index: 0机构: City Hope Beckman Res Inst, Dept Populat Sci, Duarte, CA USA City Hope Beckman Res Inst, Dept Hematol & Hematopoiet Cell Transplantat, Duarte, CA USA UCLA, David Geffen Sch Med, Dept Pediat Hematol Oncol, Los Angeles, CA 90095 USAKrajinovic, Maja论文数: 0 引用数: 0 h-index: 0机构: Univ Montreal, Dept Pediat, Montreal, PQ, Canada Univ Montreal, Dept Pharmacol & Physiol, Montreal, PQ, Canada UCLA, David Geffen Sch Med, Dept Pediat Hematol Oncol, Los Angeles, CA 90095 USAAnsari, Marc论文数: 0 引用数: 0 h-index: 0机构: Univ Geneva, Geneva Univ Hosp, Dept Pediat, Hematol Oncol Unit, Geneva, Switzerland Univ Geneva, CANSEARCH Res Lab, Geneva, Switzerland UCLA, David Geffen Sch Med, Dept Pediat Hematol Oncol, Los Angeles, CA 90095 USAGarabedian, Elizabeth论文数: 0 引用数: 0 h-index: 0机构: NHGRI, Genet & Mol Biol Branch, NIH, Bethesda, MD 20892 USA UCLA, David Geffen Sch Med, Dept Pediat Hematol Oncol, Los Angeles, CA 90095 USATse, John论文数: 0 引用数: 0 h-index: 0机构: UCLA, Dept Pharmaceut Serv, Ronald Reagan Med Ctr, Los Angeles, CA USA UCLA, David Geffen Sch Med, Dept Pediat Hematol Oncol, Los Angeles, CA 90095 USAWang, Xiaoyan论文数: 0 引用数: 0 h-index: 0机构: UCLA Hlth, Dept Gen Internal Med & Hlth Serv Res, Los Angeles, CA USA UCLA, David Geffen Sch Med, Dept Pediat Hematol Oncol, Los Angeles, CA 90095 USAShaw, Kit L.论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Los Angeles, Dept Microbiol Immunol & Mol Genet, Los Angeles, CA USA UCLA, David Geffen Sch Med, Dept Pediat Hematol Oncol, Los Angeles, CA 90095 USAGaspar, H. Bobby论文数: 0 引用数: 0 h-index: 0机构: UCL Great Ormond St Inst Child Hlth, London, England Orchard Therapeut, London, England UCLA, David Geffen Sch Med, Dept Pediat Hematol Oncol, Los Angeles, CA 90095 USACandotti, Fabio论文数: 0 引用数: 0 h-index: 0机构: NHGRI, Genet & Mol Biol Branch, NIH, Bethesda, MD 20892 USA Lausanne Univ Hosp, Div Immunol & Allergy, Lausanne, Switzerland UCLA, David Geffen Sch Med, Dept Pediat Hematol Oncol, Los Angeles, CA 90095 USAKohn, Donald B.论文数: 0 引用数: 0 h-index: 0机构: UCLA, David Geffen Sch Med, Dept Pediat Hematol Oncol, Los Angeles, CA 90095 USA Univ Calif Los Angeles, Dept Microbiol Immunol & Mol Genet, Los Angeles, CA USA UCLA, David Geffen Sch Med, Dept Mol & Med Pharmacol, Los Angeles, CA 90095 USA Univ Calif Los Angeles, Broad Stem Cell Res Ctr, Los Angeles, CA USA UCLA, David Geffen Sch Med, Dept Pediat Hematol Oncol, Los Angeles, CA 90095 USA
- [47] Cell and Gene Therapy for Anemia: Hematopoietic Stem Cells and Gene EditingINTERNATIONAL JOURNAL OF MOLECULAR SCIENCES, 2021, 22 (12)Anurogo, Dito论文数: 0 引用数: 0 h-index: 0机构: Taipei Med Univ, Coll Med, Int PhD Program Cell Therapy & Regenerat Med, Taipei 11031, Taiwan Taipei Med Univ, Coll Med, Sch Med, Dept Biochem & Mol Cell Biol, Taipei 11031, Taiwan Univ Muhammadiyah Makassar, Fac Med & Hlth Sci, Makassar 90221, Indonesia Taipei Med Univ, Coll Med, Int PhD Program Cell Therapy & Regenerat Med, Taipei 11031, TaiwanBudi, Nova Yuli Prasetyo论文数: 0 引用数: 0 h-index: 0机构: Taipei Med Univ, Coll Med, Int PhD Program Cell Therapy & Regenerat Med, Taipei 11031, Taiwan Taipei Med Univ, Coll Med, Sch Med, Dept Biochem & Mol Cell Biol, Taipei 11031, Taiwan Taipei Med Univ, Coll Med, Int PhD Program Cell Therapy & Regenerat Med, Taipei 11031, TaiwanMai-Huong Thi Ngo论文数: 0 引用数: 0 h-index: 0机构: Taipei Med Univ, Coll Med, Int PhD Program Cell Therapy & Regenerat Med, Taipei 11031, Taiwan Taipei Med Univ, Coll Med, Sch Med, Dept Biochem & Mol Cell Biol, Taipei 11031, Taiwan Taipei Med Univ, Coll Med, Int PhD Program Cell Therapy & Regenerat Med, Taipei 11031, TaiwanHuang, Yen-Hua论文数: 0 引用数: 0 h-index: 0机构: Taipei Med Univ, Coll Med, Int PhD Program Cell Therapy & Regenerat Med, Taipei 11031, Taiwan Taipei Med Univ, Coll Med, Sch Med, Dept Biochem & Mol Cell Biol, Taipei 11031, Taiwan Taipei Med Univ, Res Ctr Cell Therapy & Regenerat Med, Taipei 11031, Taiwan Taipei Med Univ, Coll Med, Grad Inst Med Sci, Taipei 11031, Taiwan Taipei Med Univ Hosp, Ctr Reprod Med, Taipei 11031, Taiwan Taipei Med Univ, Comprehens Canc Ctr, Taipei 11031, Taiwan Taipei Med Univ, Res Ctr Canc Translat Med, Taipei 11031, Taiwan Taipei Med Univ, Coll Med Sci & Technol, PhD Program Translat Med, Taipei 11031, Taiwan Taipei Med Univ, Coll Med, Int PhD Program Cell Therapy & Regenerat Med, Taipei 11031, TaiwanPawitan, Jeanne Adiwinata论文数: 0 引用数: 0 h-index: 0机构: Univ Indonesia, Fac Med, Dept Histol, Jakarta 10430, Indonesia Univ Indonesia, Cipto Mangunkusumo Cent Hosp, Fac Med, Stem Cell Med Technol Integrated Serv Unit, Jakarta 10430, Indonesia Univ Indonesia, Fac Med, Stem Cell & Tissue Engn Res Ctr, Indonesia Med Educ & Res Inst IMERI, Jakarta 10430, Indonesia Taipei Med Univ, Coll Med, Int PhD Program Cell Therapy & Regenerat Med, Taipei 11031, Taiwan
- [48] Clinical Impact of Suicide Gene Therapy in Allogeneic Hematopoietic Stem Cell TransplantationHUMAN GENE THERAPY, 2010, 21 (03) : 241 - 250Lupo-Stanghellini, Maria Teresa论文数: 0 引用数: 0 h-index: 0机构: Ist Sci San Raffaele, Div Regenerat Med Gene Therapy & Stem Cells, Program Immunol Gene Therapy & Bioimmunotherapy C, Hematol & Bone Marrow Transplantat Unit, I-20132 Milan, Italy Ist Sci San Raffaele, Div Regenerat Med Gene Therapy & Stem Cells, Program Immunol Gene Therapy & Bioimmunotherapy C, Hematol & Bone Marrow Transplantat Unit, I-20132 Milan, ItalyProvasi, Elena论文数: 0 引用数: 0 h-index: 0机构: Ist Sci San Raffaele, Div Regenerat Med Gene Therapy & Stem Cells, Expt Hematol Unit, Program Immunol Gene Therapy & Bioimmunotherapy C, Via Olgettina 60, I-20132 Milan, Italy Univ Vita Salute, I-20132 Milan, Italy Ist Sci San Raffaele, Div Regenerat Med Gene Therapy & Stem Cells, Program Immunol Gene Therapy & Bioimmunotherapy C, Hematol & Bone Marrow Transplantat Unit, I-20132 Milan, ItalyBondanza, Attilio论文数: 0 引用数: 0 h-index: 0机构: Ist Sci San Raffaele, Div Regenerat Med Gene Therapy & Stem Cells, Program Immunol Gene Therapy & Bioimmunotherapy C, Hematol & Bone Marrow Transplantat Unit, I-20132 Milan, Italy Ist Sci San Raffaele, Div Regenerat Med Gene Therapy & Stem Cells, Expt Hematol Unit, Program Immunol Gene Therapy & Bioimmunotherapy C, Via Olgettina 60, I-20132 Milan, Italy Ist Sci San Raffaele, Div Regenerat Med Gene Therapy & Stem Cells, Program Immunol Gene Therapy & Bioimmunotherapy C, Hematol & Bone Marrow Transplantat Unit, I-20132 Milan, ItalyCiceri, Fabio论文数: 0 引用数: 0 h-index: 0机构: Ist Sci San Raffaele, Div Regenerat Med Gene Therapy & Stem Cells, Program Immunol Gene Therapy & Bioimmunotherapy C, Hematol & Bone Marrow Transplantat Unit, I-20132 Milan, Italy Ist Sci San Raffaele, Div Regenerat Med Gene Therapy & Stem Cells, Expt Hematol Unit, Program Immunol Gene Therapy & Bioimmunotherapy C, Via Olgettina 60, I-20132 Milan, Italy Univ Vita Salute, I-20132 Milan, Italy Ist Sci San Raffaele, Div Regenerat Med Gene Therapy & Stem Cells, Program Immunol Gene Therapy & Bioimmunotherapy C, Hematol & Bone Marrow Transplantat Unit, I-20132 Milan, ItalyBordignon, Claudio论文数: 0 引用数: 0 h-index: 0机构: Univ Vita Salute, I-20132 Milan, Italy MolMed, I-20132 Milan, Italy Ist Sci San Raffaele, Div Regenerat Med Gene Therapy & Stem Cells, Program Immunol Gene Therapy & Bioimmunotherapy C, Hematol & Bone Marrow Transplantat Unit, I-20132 Milan, ItalyBonini, Chiara论文数: 0 引用数: 0 h-index: 0机构: Ist Sci San Raffaele, Div Regenerat Med Gene Therapy & Stem Cells, Program Immunol Gene Therapy & Bioimmunotherapy C, Hematol & Bone Marrow Transplantat Unit, I-20132 Milan, Italy Ist Sci San Raffaele, Div Regenerat Med Gene Therapy & Stem Cells, Expt Hematol Unit, Program Immunol Gene Therapy & Bioimmunotherapy C, Via Olgettina 60, I-20132 Milan, Italy Univ Vita Salute, I-20132 Milan, Italy Ist Sci San Raffaele, Div Regenerat Med Gene Therapy & Stem Cells, Program Immunol Gene Therapy & Bioimmunotherapy C, Hematol & Bone Marrow Transplantat Unit, I-20132 Milan, Italy
- [49] A Possible Approach for Stem Cell Gene Therapy of Fanconi AnemiaCURRENT GENE THERAPY, 2009, 9 (01) : 26 - 32Song, Liting论文数: 0 引用数: 0 h-index: 0机构: Univ Waterloo, Dept Chem, Waterloo, ON N2L 3G1, Canada Univ Waterloo, Dept Chem, Waterloo, ON N2L 3G1, Canada
- [50] Morbidity in an adenosine deaminase-deficient patient during 27 years of enzyme replacement therapyCLINICAL IMMUNOLOGY, 2020, 211论文数: 引用数: h-index:机构:论文数: 引用数: h-index:机构:论文数: 引用数: h-index:机构:论文数: 引用数: h-index:机构:论文数: 引用数: h-index:机构:论文数: 引用数: h-index:机构:论文数: 引用数: h-index:机构:Lee, Erika论文数: 0 引用数: 0 h-index: 0机构: Univ Toronto, Toronto, ON, Canada St Michaels Hosp, Div Allergy & Immunol, Toronto, ON, Canada Hosp Sick Children, Dept Pediat, Div Immunol & Allergy, Toronto, ON, CanadaBetschel, Stephen论文数: 0 引用数: 0 h-index: 0机构: Univ Toronto, Toronto, ON, Canada St Michaels Hosp, Div Allergy & Immunol, Toronto, ON, Canada Hosp Sick Children, Dept Pediat, Div Immunol & Allergy, Toronto, ON, CanadaRoifman, Chaim M.论文数: 0 引用数: 0 h-index: 0机构: Hosp Sick Children, Dept Pediat, Div Immunol & Allergy, Toronto, ON, Canada Univ Toronto, Toronto, ON, Canada Hosp Sick Children, Dept Pediat, Div Immunol & Allergy, Toronto, ON, Canada