APL-2, a Complement C3 Inhibitor for the Potential Treatment of Paroxysmal Nocturnal Hemoglobinuria (PNH): Phase I Data from Two Completed Studies in Healthy Volunteers

被引:30
作者
Grossi, Federico V. [1 ]
Bedwell, Pauline [2 ]
Deschatelets, Pascal [1 ,3 ]
Edis, Lil
Francois, Cedric G. [1 ]
Johnson, Patrick J. [4 ]
Richardson, Helen J. [5 ]
Tan, Lisa [6 ]
Vega, Carolina A. [1 ]
Lickliter, Jason [7 ]
机构
[1] Apellis Pharmaceut Inc, Crestwood, KY USA
[2] PB Clin Serv Ltd, Minster, England
[3] Apellis Australia Pty Ltd, Brisbane, Qld, Australia
[4] JPharma Solut GmbH, Zurich, Switzerland
[5] Paramstat Ltd, Sandwich, Kent, England
[6] Lisa Tan Pharma Consulting, Cambridge, England
[7] Nucleus Network Ltd, Melbourne, Vic, Australia
关键词
D O I
10.1182/blood.V128.22.1251.1251
中图分类号
R5 [内科学];
学科分类号
1002 ; 100201 ;
摘要
1251
引用
收藏
页数:4
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