Gene Therapy Overcomes the Need for Multiple Infusions of Enzyme Replacement Therapy in a Mouse Model of Lysosomal Storage Disease

被引：0

作者：

Ferla, Rita ^{[1
,2
]}

Claudiani, Pamela ^{[1
,2
]}

Cotugno, Gabriella ^{[1
,2
]}

Saccone, Paola ^{[3
]}

De Leonibus, Elvira ^{[3
]}

Auricchio, Alberto ^{[1
,2
]}

机构：

[1] Telethon Inst Genet & Med TIGEM, Naples, Italy

[2] Univ Naples Federico II, Dept Translat Med, Naples, Italy

[3] IGB, Naples, Italy

来源：

MOLECULAR THERAPY | 2014年 / 22卷

关键词：

D O I：

暂无

中图分类号：

Q81 [生物工程学（生物技术）]; Q93 [微生物学];

学科分类号：

071005 ; 0836 ; 090102 ; 100705 ;

摘要：

362

引用

页码：S138 / S138

页数：1

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