Gene Therapy Overcomes the Need for Multiple Infusions of Enzyme Replacement Therapy in a Mouse Model of Lysosomal Storage Disease

被引:0
作者
Ferla, Rita [1 ,2 ]
Claudiani, Pamela [1 ,2 ]
Cotugno, Gabriella [1 ,2 ]
Saccone, Paola [3 ]
De Leonibus, Elvira [3 ]
Auricchio, Alberto [1 ,2 ]
机构
[1] Telethon Inst Genet & Med TIGEM, Naples, Italy
[2] Univ Naples Federico II, Dept Translat Med, Naples, Italy
[3] IGB, Naples, Italy
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D O I
暂无
中图分类号
Q81 [生物工程学(生物技术)]; Q93 [微生物学];
学科分类号
071005 ; 0836 ; 090102 ; 100705 ;
摘要
362
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页码:S138 / S138
页数:1
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