TCRαβ CD19 depletion in allogeneic haematopoietic stem cell transplantation performed for Hurler syndrome

被引：6

作者：

Mainardi, C. ^{[1
]}

Tumino, M. ^{[1
]}

Gazzola, M. V. ^{[1
]}

Rampazzo, A. ^{[2
]}

Scarpa, M. ^{[2
]}

Messina, C. ^{[1
]}

机构：

[1] Univ Padua, Azienda Osped, DAI Salute Donna & Bambino, Clin Oncoematol Pediat, Padua, Italy

[2] Univ Padua, Azienda Osped, DAI Salute Donna & Bambino, Dipartimento Pediat, Padua, Italy

来源：

BONE MARROW TRANSPLANTATION | 2016年 / 51卷 / 03期

关键词：

BONE-MARROW-TRANSPLANTATION; METABOLIC STORAGE DISEASES; CHILDREN; EUROPE;

D O I：

10.1038/bmt.2015.258

中图分类号：

Q6 [生物物理学];

学科分类号：

071011 ;

摘要：

引用

页码：438 / 439

页数：2

共 15 条

[1] The clinical outcome of Hurler syndrome after stem cell transplantation [J].

Aldenboven, Mieke ;

Boelens, FaapFan ;

de Koning, Tom F. .

BIOLOGY OF BLOOD AND MARROW TRANSPLANTATION, 2008, 14 (05) :485-498

[2] Outcomes of hematopoietic stem cell transplantation for Hurler's syndrome in Europe: a risk factor analysis for graft failure [J].

Boelens, J. J. ;

Wynn, R. F. ;

O'Meara, A. ;

Veys, P. ;

Bertrand, Y. ;

Souillet, G. ;

Wraith, J. E. ;

Fischer, A. ;

Cavazzana-Calvo, M. ;

Sykora, K. W. ;

Sedlacek, P. ;

Rovelli, A. ;

Uiterwaal, C. S. P. M. ;

Wulffraat, N. .

BONE MARROW TRANSPLANTATION, 2007, 40 (03) :225-233

[3] Mucopolysaccharidosis type I: current knowledge on its pathophysiological mechanisms [J].

Campos, Derbis ;

Monaga, Madelyn .

METABOLIC BRAIN DISEASE, 2012, 27 (02) :121-129

[4] Reconstitution of lymphocyte subpopulations in children with inherited metabolic storage diseases after haematopoietic cell transplantation [J].

Corti, P ;

Peters, C ;

Balduzzi, A ;

Bertagnolio, B ;

Biondi, A ;

Bugarin, C ;

Dassi, M ;

Furlan, F ;

Gaipa, G ;

Longoni, D ;

Maglia, O ;

Parini, R ;

Perseghin, P ;

Uderzo, C ;

Uziel, G ;

Masera, G ;

Rovelli, A .

BRITISH JOURNAL OF HAEMATOLOGY, 2005, 130 (02) :249-255

[5] Haematopoietic cell transplantation (HCT) in combination with enzyme replacement therapy (ERT) in patients with Hurler syndrome [J].

Cox-Brinkman, J. ;

Boelens, J. -J. ;

Wraith, J. E. ;

O'Meara, A. ;

Veys, P. ;

Wijburg, F. A. ;

Wulffraat, N. ;

Wynn, R. F. .

BONE MARROW TRANSPLANTATION, 2006, 38 (01) :17-21

[6] Allogeneic bone marrow stem cell transplantation following CD34+immunomagnetic enrichment in patients with inherited metabolic storage diseases [J].

Gaipa, G ;

Dassi, M ;

Perseghin, P ;

Venturi, N ;

Corti, P ;

Bonanomi, S ;

Balduzzi, A ;

Longoni, D ;

Uderzo, C ;

Biondi, A ;

Masera, G ;

Parini, R ;

Bertagnolio, B ;

Uziel, G ;

Peters, C ;

Rovelli, A .

BONE MARROW TRANSPLANTATION, 2003, 31 (10) :857-860

[7] Transplantation of allogeneic CD34-selected stem cells after fludarabine-based conditioning regimen for children with mucopolysaccharidosis 1H (M. Hurler) [J].

Grigull, L ;

Beilken, A ;

Schrappe, M ;

Das, A ;

Luecke, T ;

Sander, A ;

Stanulla, M ;

Rehe, K ;

Sauer, M ;

Schmid, H ;

Welte, K ;

Lukacs, Z ;

Gal, A ;

Sykora, KW .

BONE MARROW TRANSPLANTATION, 2005, 35 (03) :265-269

[8]

Neufeld EF., 2001, The metabolic molecular basis of inherited disease, V8th ed., P3421, DOI DOI 10.1036/OMMBID.165

[9] Outcome of unrelated donor bone marrow transplantation in 40 children with Hurler syndrome [J].

Peters, C ;

Balthazor, M ;

Shapiro, EG ;

King, RJ ;

Kollman, C ;

Hegland, JD ;

HensleeDowney, J ;

Trigg, ME ;

Cowan, MJ ;

Sanders, J ;

Bunin, N ;

Weinstein, H ;

Lenarsky, C ;

Falk, P ;

Harris, R ;

Bowen, T ;

Williams, TE ;

Grayson, GH ;

Warkentin, P ;

Sender, L ;

Cool, VA ;

Crittenden, M ;

Packman, S ;

Kaplan, P ;

Lockman, LA ;

Anderson, J ;

Krivit, W ;

Dusenbery, K ;

Wagner, J .

BLOOD, 1996, 87 (11) :4894-4902

[10] Hurler syndrome: II. Outcome of HLA genotypically identical sibling and HLA-haploidentical related donor bone marrow transplantation in fifty-four children [J].

Peters, C ;

Shapiro, EG ;

Anderson, J ;

Henslee-Downey, PJ ;

Klemperer, MR ;

Cowan, MJ ;

Saunders, EF ;

deAlarcon, PA ;

Twist, C ;

Nachman, JB ;

Hale, GA ;

Harris, RE ;

Rozans, MK ;

Kurtzberg, J ;

Grayson, GH ;

Wiliams, TE ;

Lenarsky, C ;

Wagner, JE ;

Krivit, W .

BLOOD, 1998, 91 (07) :2601-2608

← 1 2 →