共 73 条
[11]
Efficient gene delivery to the cone-enriched pig retina by dual AAV vectors
[J].
Colella, P.
;
Trapani, I.
;
Cesi, G.
;
Sommella, A.
;
Manfredi, A.
;
Puppo, A.
;
Iodice, C.
;
Rossi, S.
;
Simonelli, F.
;
Giunti, M.
;
Bacci, M. L.
;
Auricchio, A.
.
GENE THERAPY,
2014, 21 (04)
:450-456

Colella, P.
论文数: 0 引用数: 0
h-index: 0
机构:
Telethon Inst Genet & Med TIGEM, I-80131 Naples, Italy Telethon Inst Genet & Med TIGEM, I-80131 Naples, Italy

Trapani, I.
论文数: 0 引用数: 0
h-index: 0
机构:
Telethon Inst Genet & Med TIGEM, I-80131 Naples, Italy Telethon Inst Genet & Med TIGEM, I-80131 Naples, Italy

Cesi, G.
论文数: 0 引用数: 0
h-index: 0
机构:
Telethon Inst Genet & Med TIGEM, I-80131 Naples, Italy Telethon Inst Genet & Med TIGEM, I-80131 Naples, Italy

Sommella, A.
论文数: 0 引用数: 0
h-index: 0
机构:
Telethon Inst Genet & Med TIGEM, I-80131 Naples, Italy Telethon Inst Genet & Med TIGEM, I-80131 Naples, Italy

Manfredi, A.
论文数: 0 引用数: 0
h-index: 0
机构:
Telethon Inst Genet & Med TIGEM, I-80131 Naples, Italy Telethon Inst Genet & Med TIGEM, I-80131 Naples, Italy

Puppo, A.
论文数: 0 引用数: 0
h-index: 0
机构:
Telethon Inst Genet & Med TIGEM, I-80131 Naples, Italy Telethon Inst Genet & Med TIGEM, I-80131 Naples, Italy

Iodice, C.
论文数: 0 引用数: 0
h-index: 0
机构:
Telethon Inst Genet & Med TIGEM, I-80131 Naples, Italy Telethon Inst Genet & Med TIGEM, I-80131 Naples, Italy

Rossi, S.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Naples 2, Dept Ophthalmol, Naples, Italy Telethon Inst Genet & Med TIGEM, I-80131 Naples, Italy

Simonelli, F.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Naples 2, Dept Ophthalmol, Naples, Italy Telethon Inst Genet & Med TIGEM, I-80131 Naples, Italy

Giunti, M.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Bologna, Dept Vet Morphophysiol & Anim Prod, Bologna, Italy Telethon Inst Genet & Med TIGEM, I-80131 Naples, Italy

Bacci, M. L.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Bologna, Dept Vet Morphophysiol & Anim Prod, Bologna, Italy Telethon Inst Genet & Med TIGEM, I-80131 Naples, Italy

Auricchio, A.
论文数: 0 引用数: 0
h-index: 0
机构:
Telethon Inst Genet & Med TIGEM, I-80131 Naples, Italy
Univ Naples Federico II, Dept Translat Med, Naples, Italy Telethon Inst Genet & Med TIGEM, I-80131 Naples, Italy
[12]
In Vivo-Directed Evolution of a New Adeno-Associated Virus for Therapeutic Outer Retinal Gene Delivery from the Vitreous
[J].
Dalkara, Deniz
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Byrne, Leah C.
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Klimczak, Ryan R.
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Visel, Meike
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Yin, Lu
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Merigan, William H.
;
Flannery, John G.
;
Schaffer, David V.
.
SCIENCE TRANSLATIONAL MEDICINE,
2013, 5 (189)

Dalkara, Deniz
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Calif Berkeley, Helen Wills Neurosci Inst, Berkeley, CA 94720 USA Univ Calif Berkeley, Helen Wills Neurosci Inst, Berkeley, CA 94720 USA

Byrne, Leah C.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Calif Berkeley, Helen Wills Neurosci Inst, Berkeley, CA 94720 USA Univ Calif Berkeley, Helen Wills Neurosci Inst, Berkeley, CA 94720 USA

Klimczak, Ryan R.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Calif Berkeley, Dept Mol & Cellular Biol, Berkeley, CA 94720 USA Univ Calif Berkeley, Helen Wills Neurosci Inst, Berkeley, CA 94720 USA

Visel, Meike
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Calif Berkeley, Dept Mol & Cellular Biol, Berkeley, CA 94720 USA Univ Calif Berkeley, Helen Wills Neurosci Inst, Berkeley, CA 94720 USA

Yin, Lu
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Rochester, Flaum Eye Inst, Rochester, NY 14642 USA
Univ Rochester, Ctr Visual Sci, Rochester, NY 14642 USA Univ Calif Berkeley, Helen Wills Neurosci Inst, Berkeley, CA 94720 USA

Merigan, William H.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Rochester, Flaum Eye Inst, Rochester, NY 14642 USA
Univ Rochester, Ctr Visual Sci, Rochester, NY 14642 USA Univ Calif Berkeley, Helen Wills Neurosci Inst, Berkeley, CA 94720 USA

Flannery, John G.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Calif Berkeley, Helen Wills Neurosci Inst, Berkeley, CA 94720 USA
Univ Calif Berkeley, Dept Mol & Cellular Biol, Berkeley, CA 94720 USA Univ Calif Berkeley, Helen Wills Neurosci Inst, Berkeley, CA 94720 USA

Schaffer, David V.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Calif Berkeley, Helen Wills Neurosci Inst, Berkeley, CA 94720 USA
Univ Calif Berkeley, Dept Mol & Cellular Biol, Berkeley, CA 94720 USA
Univ Calif Berkeley, Dept Chem & Biomol Engn, Berkeley, CA 94720 USA Univ Calif Berkeley, Helen Wills Neurosci Inst, Berkeley, CA 94720 USA
[13]
AAV Mediated GDNF Secretion From Retinal Glia Slows Down Retinal Degeneration in a Rat Model of Retinitis Pigmentosa
[J].
Dalkara, Deniz
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Kolstad, Kathleen D.
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Guerin, Karen I.
;
Hoffmann, Natalie V.
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Visel, Meike
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Klimczak, Ryan R.
;
Schaffer, David V.
;
Flannery, John G.
.
MOLECULAR THERAPY,
2011, 19 (09)
:1602-1608

Dalkara, Deniz
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Calif Berkeley, Dept Mol & Cell Biol, Berkeley, CA 94720 USA
Univ Calif Berkeley, Helen Wills Neurosci Inst, Berkeley, CA 94720 USA
Univ Calif Berkeley, Dept Chem Engn, Berkeley, CA 94720 USA
Univ Calif Berkeley, Dept Bioengn, Berkeley, CA 94720 USA Univ Calif Berkeley, Dept Mol & Cell Biol, Berkeley, CA 94720 USA

Kolstad, Kathleen D.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Calif Berkeley, Dept Mol & Cell Biol, Berkeley, CA 94720 USA
Univ Calif Berkeley, Helen Wills Neurosci Inst, Berkeley, CA 94720 USA Univ Calif Berkeley, Dept Mol & Cell Biol, Berkeley, CA 94720 USA

Guerin, Karen I.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Calif Berkeley, Dept Mol & Cell Biol, Berkeley, CA 94720 USA
Univ Calif Berkeley, Helen Wills Neurosci Inst, Berkeley, CA 94720 USA Univ Calif Berkeley, Dept Mol & Cell Biol, Berkeley, CA 94720 USA

Hoffmann, Natalie V.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Calif Berkeley, Dept Mol & Cell Biol, Berkeley, CA 94720 USA
Univ Calif Berkeley, Helen Wills Neurosci Inst, Berkeley, CA 94720 USA Univ Calif Berkeley, Dept Mol & Cell Biol, Berkeley, CA 94720 USA

Visel, Meike
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Calif Berkeley, Dept Mol & Cell Biol, Berkeley, CA 94720 USA
Univ Calif Berkeley, Helen Wills Neurosci Inst, Berkeley, CA 94720 USA Univ Calif Berkeley, Dept Mol & Cell Biol, Berkeley, CA 94720 USA

Klimczak, Ryan R.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Calif Berkeley, Dept Mol & Cell Biol, Berkeley, CA 94720 USA
Univ Calif Berkeley, Helen Wills Neurosci Inst, Berkeley, CA 94720 USA Univ Calif Berkeley, Dept Mol & Cell Biol, Berkeley, CA 94720 USA

Schaffer, David V.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Calif Berkeley, Dept Mol & Cell Biol, Berkeley, CA 94720 USA
Univ Calif Berkeley, Helen Wills Neurosci Inst, Berkeley, CA 94720 USA
Univ Calif Berkeley, Dept Chem Engn, Berkeley, CA 94720 USA
Univ Calif Berkeley, Dept Bioengn, Berkeley, CA 94720 USA Univ Calif Berkeley, Dept Mol & Cell Biol, Berkeley, CA 94720 USA

Flannery, John G.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Calif Berkeley, Dept Mol & Cell Biol, Berkeley, CA 94720 USA
Univ Calif Berkeley, Helen Wills Neurosci Inst, Berkeley, CA 94720 USA Univ Calif Berkeley, Dept Mol & Cell Biol, Berkeley, CA 94720 USA
[14]
Inner Limiting Membrane Barriers to AAV-mediated Retinal Transduction From the Vitreous
[J].
Dalkara, Deniz
;
Kolstad, Kathleen D.
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Caporale, Natalia
;
Visel, Meike
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Klimczak, Ryan R.
;
Schaffer, David V.
;
Flannery, John G.
.
MOLECULAR THERAPY,
2009, 17 (12)
:2096-2102

Dalkara, Deniz
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Calif Berkeley, Dept Chem Engn, Berkeley, CA 94720 USA
Univ Calif Berkeley, Dept Bioengn, Berkeley, CA 94720 USA
Univ Calif Berkeley, Helen Wills Neurosci Inst, Berkeley, CA 94720 USA Univ Calif Berkeley, Dept Chem Engn, Berkeley, CA 94720 USA

Kolstad, Kathleen D.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Calif Berkeley, Helen Wills Neurosci Inst, Berkeley, CA 94720 USA
Univ Calif Berkeley, Dept Mol & Cellular Biol, Berkeley, CA 94720 USA Univ Calif Berkeley, Dept Chem Engn, Berkeley, CA 94720 USA

论文数: 引用数:
h-index:
机构:

Visel, Meike
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Calif Berkeley, Helen Wills Neurosci Inst, Berkeley, CA 94720 USA
Univ Calif Berkeley, Dept Mol & Cellular Biol, Berkeley, CA 94720 USA Univ Calif Berkeley, Dept Chem Engn, Berkeley, CA 94720 USA

Klimczak, Ryan R.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Calif Berkeley, Helen Wills Neurosci Inst, Berkeley, CA 94720 USA
Univ Calif Berkeley, Dept Mol & Cellular Biol, Berkeley, CA 94720 USA Univ Calif Berkeley, Dept Chem Engn, Berkeley, CA 94720 USA

Schaffer, David V.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Calif Berkeley, Dept Chem Engn, Berkeley, CA 94720 USA
Univ Calif Berkeley, Dept Bioengn, Berkeley, CA 94720 USA
Univ Calif Berkeley, Helen Wills Neurosci Inst, Berkeley, CA 94720 USA Univ Calif Berkeley, Dept Chem Engn, Berkeley, CA 94720 USA

Flannery, John G.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Calif Berkeley, Helen Wills Neurosci Inst, Berkeley, CA 94720 USA
Univ Calif Berkeley, Dept Mol & Cellular Biol, Berkeley, CA 94720 USA Univ Calif Berkeley, Dept Chem Engn, Berkeley, CA 94720 USA
[15]
Structural Insight into the Unique Properties of Adeno-Associated Virus Serotype 9
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DiMattia, Michael A.
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Nam, Hyun-Joo
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Van Vliet, Kim
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Mitchell, Matthew
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Bennett, Antonette
;
Gurda, Brittney L.
;
McKenna, Robert
;
Olson, Norman H.
;
Sinkovits, Robert S.
;
Potter, Mark
;
Byrne, Barry J.
;
Aslanidi, George
;
Zolotukhin, Sergei
;
Muzyczka, Nicholas
;
Baker, Timothy S.
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Agbandje-McKennaa, Mavis
.
JOURNAL OF VIROLOGY,
2012, 86 (12)
:6947-6958

DiMattia, Michael A.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Florida, Coll Med, Dept Biochem & Mol Biol, Ctr Struct Biol,McKnight Brain Inst, Gainesville, FL 32610 USA Univ Florida, Coll Med, Dept Biochem & Mol Biol, Ctr Struct Biol,McKnight Brain Inst, Gainesville, FL 32610 USA

Nam, Hyun-Joo
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Florida, Coll Med, Dept Biochem & Mol Biol, Ctr Struct Biol,McKnight Brain Inst, Gainesville, FL 32610 USA Univ Florida, Coll Med, Dept Biochem & Mol Biol, Ctr Struct Biol,McKnight Brain Inst, Gainesville, FL 32610 USA

论文数: 引用数:
h-index:
机构:

Mitchell, Matthew
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Florida, Coll Med, Dept Biochem & Mol Biol, Ctr Struct Biol,McKnight Brain Inst, Gainesville, FL 32610 USA Univ Florida, Coll Med, Dept Biochem & Mol Biol, Ctr Struct Biol,McKnight Brain Inst, Gainesville, FL 32610 USA

Bennett, Antonette
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Florida, Coll Med, Dept Biochem & Mol Biol, Ctr Struct Biol,McKnight Brain Inst, Gainesville, FL 32610 USA Univ Florida, Coll Med, Dept Biochem & Mol Biol, Ctr Struct Biol,McKnight Brain Inst, Gainesville, FL 32610 USA

Gurda, Brittney L.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Florida, Coll Med, Dept Biochem & Mol Biol, Ctr Struct Biol,McKnight Brain Inst, Gainesville, FL 32610 USA Univ Florida, Coll Med, Dept Biochem & Mol Biol, Ctr Struct Biol,McKnight Brain Inst, Gainesville, FL 32610 USA

论文数: 引用数:
h-index:
机构:

Olson, Norman H.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Calif San Diego, Dept Chem & Biochem, La Jolla, CA 92093 USA
Univ Calif San Diego, Div Biol Sci, La Jolla, CA 92093 USA Univ Florida, Coll Med, Dept Biochem & Mol Biol, Ctr Struct Biol,McKnight Brain Inst, Gainesville, FL 32610 USA

Sinkovits, Robert S.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Calif San Diego, Dept Chem & Biochem, La Jolla, CA 92093 USA
Univ Calif San Diego, Div Biol Sci, La Jolla, CA 92093 USA Univ Florida, Coll Med, Dept Biochem & Mol Biol, Ctr Struct Biol,McKnight Brain Inst, Gainesville, FL 32610 USA

Potter, Mark
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Florida, Coll Med, Dept Pediat, Gainesville, FL USA
Univ Florida, Coll Med, Powell Gene Therapy Ctr, Div Cell & Mol Therapy, Gainesville, FL USA Univ Florida, Coll Med, Dept Biochem & Mol Biol, Ctr Struct Biol,McKnight Brain Inst, Gainesville, FL 32610 USA

Byrne, Barry J.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Florida, Coll Med, Dept Pediat, Gainesville, FL USA
Univ Florida, Coll Med, Powell Gene Therapy Ctr, Div Cell & Mol Therapy, Gainesville, FL USA Univ Florida, Coll Med, Dept Biochem & Mol Biol, Ctr Struct Biol,McKnight Brain Inst, Gainesville, FL 32610 USA

Aslanidi, George
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Florida, Coll Med, Dept Pediat, Gainesville, FL USA
Univ Florida, Coll Med, Powell Gene Therapy Ctr, Div Cell & Mol Therapy, Gainesville, FL USA Univ Florida, Coll Med, Dept Biochem & Mol Biol, Ctr Struct Biol,McKnight Brain Inst, Gainesville, FL 32610 USA

Zolotukhin, Sergei
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Florida, Coll Med, Dept Pediat, Gainesville, FL USA
Univ Florida, Coll Med, Powell Gene Therapy Ctr, Div Cell & Mol Therapy, Gainesville, FL USA Univ Florida, Coll Med, Dept Biochem & Mol Biol, Ctr Struct Biol,McKnight Brain Inst, Gainesville, FL 32610 USA

Muzyczka, Nicholas
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Florida, Coll Med, Dept Mol Genet & Microbiol, Gainesville, FL USA Univ Florida, Coll Med, Dept Biochem & Mol Biol, Ctr Struct Biol,McKnight Brain Inst, Gainesville, FL 32610 USA

Baker, Timothy S.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Calif San Diego, Dept Chem & Biochem, La Jolla, CA 92093 USA
Univ Calif San Diego, Div Biol Sci, La Jolla, CA 92093 USA Univ Florida, Coll Med, Dept Biochem & Mol Biol, Ctr Struct Biol,McKnight Brain Inst, Gainesville, FL 32610 USA

Agbandje-McKennaa, Mavis
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Florida, Coll Med, Dept Biochem & Mol Biol, Ctr Struct Biol,McKnight Brain Inst, Gainesville, FL 32610 USA Univ Florida, Coll Med, Dept Biochem & Mol Biol, Ctr Struct Biol,McKnight Brain Inst, Gainesville, FL 32610 USA
[16]
Directed evolution of adeno-associated virus to an infectious respiratory virus
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Excoffon, Katherine J. D. A.
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Koerber, James T.
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Dickey, David D.
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Murtha, Matthew
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Keshavjee, Shaf
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Kaspar, Brian K.
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Zabner, Joseph
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Schaffer, David V.
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PROCEEDINGS OF THE NATIONAL ACADEMY OF SCIENCES OF THE UNITED STATES OF AMERICA,
2009, 106 (10)
:3865-3870

Excoffon, Katherine J. D. A.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Iowa, Dept Internal Med, Iowa City, IA 52241 USA Univ Iowa, Dept Internal Med, Iowa City, IA 52241 USA

Koerber, James T.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Calif Berkeley, Dept Chem Engn, Berkeley, CA 94720 USA
Univ Calif Berkeley, Dept Bioengn, Berkeley, CA 94720 USA
Univ Calif Berkeley, Helen Willis Neurosci Inst, Berkeley, CA 94720 USA Univ Iowa, Dept Internal Med, Iowa City, IA 52241 USA

Dickey, David D.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Iowa, Dept Internal Med, Iowa City, IA 52241 USA Univ Iowa, Dept Internal Med, Iowa City, IA 52241 USA

Murtha, Matthew
论文数: 0 引用数: 0
h-index: 0
机构:
Nationwide Childrens Hosp, Res Inst, Dept Pediat, Columbus, OH 43205 USA
Nationwide Childrens Hosp, Res Inst, Childrens Res Inst, Columbus, OH 43205 USA
Ohio State Univ, Columbus, OH 43205 USA Univ Iowa, Dept Internal Med, Iowa City, IA 52241 USA

Keshavjee, Shaf
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Toronto, Toronto Gen Hosp, Div Thorac Surg, Dept Surg, Toronto, ON M5G 2C4, Canada Univ Iowa, Dept Internal Med, Iowa City, IA 52241 USA

Kaspar, Brian K.
论文数: 0 引用数: 0
h-index: 0
机构:
Nationwide Childrens Hosp, Res Inst, Dept Pediat, Columbus, OH 43205 USA
Nationwide Childrens Hosp, Res Inst, Childrens Res Inst, Columbus, OH 43205 USA
Ohio State Univ, Columbus, OH 43205 USA Univ Iowa, Dept Internal Med, Iowa City, IA 52241 USA

论文数: 引用数:
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机构:

Schaffer, David V.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Calif Berkeley, Dept Chem Engn, Berkeley, CA 94720 USA
Univ Calif Berkeley, Dept Bioengn, Berkeley, CA 94720 USA
Univ Calif Berkeley, Helen Willis Neurosci Inst, Berkeley, CA 94720 USA Univ Iowa, Dept Internal Med, Iowa City, IA 52241 USA
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CpG-depleted adeno-associated virus vectors evade immune detection
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Faust, Susan M.
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Bell, Peter
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Cutler, Benjamin J.
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Zhu, Yanqing
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Rabinowitz, Joseph E.
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Wilson, James M.
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JOURNAL OF CLINICAL INVESTIGATION,
2013, 123 (07)
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Faust, Susan M.
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h-index: 0
机构:
Univ Penn, Perelman Sch Med, Dept Pathol & Lab Med, Gene Therapy Program, Philadelphia, PA 19104 USA Univ Penn, Perelman Sch Med, Dept Pathol & Lab Med, Gene Therapy Program, Philadelphia, PA 19104 USA

Bell, Peter
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Penn, Perelman Sch Med, Dept Pathol & Lab Med, Gene Therapy Program, Philadelphia, PA 19104 USA Univ Penn, Perelman Sch Med, Dept Pathol & Lab Med, Gene Therapy Program, Philadelphia, PA 19104 USA

Cutler, Benjamin J.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Penn, Perelman Sch Med, Dept Pathol & Lab Med, Gene Therapy Program, Philadelphia, PA 19104 USA Univ Penn, Perelman Sch Med, Dept Pathol & Lab Med, Gene Therapy Program, Philadelphia, PA 19104 USA

Ashley, Scott N.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Penn, Perelman Sch Med, Dept Pathol & Lab Med, Gene Therapy Program, Philadelphia, PA 19104 USA Univ Penn, Perelman Sch Med, Dept Pathol & Lab Med, Gene Therapy Program, Philadelphia, PA 19104 USA

Zhu, Yanqing
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Penn, Perelman Sch Med, Dept Pathol & Lab Med, Gene Therapy Program, Philadelphia, PA 19104 USA Univ Penn, Perelman Sch Med, Dept Pathol & Lab Med, Gene Therapy Program, Philadelphia, PA 19104 USA

Rabinowitz, Joseph E.
论文数: 0 引用数: 0
h-index: 0
机构:
Temple Univ, Dept Pharmacol, Philadelphia, PA 19122 USA Univ Penn, Perelman Sch Med, Dept Pathol & Lab Med, Gene Therapy Program, Philadelphia, PA 19104 USA

Wilson, James M.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Penn, Perelman Sch Med, Dept Pathol & Lab Med, Gene Therapy Program, Philadelphia, PA 19104 USA Univ Penn, Perelman Sch Med, Dept Pathol & Lab Med, Gene Therapy Program, Philadelphia, PA 19104 USA
[18]
STABLE IN-VIVO EXPRESSION OF THE CYSTIC-FIBROSIS TRANSMEMBRANE CONDUCTANCE REGULATOR WITH AN ADENOASSOCIATED VIRUS VECTOR
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FLOTTE, TR
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AFIONE, SA
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CONRAD, C
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OKA, H
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PROCEEDINGS OF THE NATIONAL ACADEMY OF SCIENCES OF THE UNITED STATES OF AMERICA,
1993, 90 (22)
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FLOTTE, TR
论文数: 0 引用数: 0
h-index: 0
机构: JOHNS HOPKINS UNIV,SCH MED,DEPT PHYSIOL,BALTIMORE,MD 21205

AFIONE, SA
论文数: 0 引用数: 0
h-index: 0
机构: JOHNS HOPKINS UNIV,SCH MED,DEPT PHYSIOL,BALTIMORE,MD 21205

CONRAD, C
论文数: 0 引用数: 0
h-index: 0
机构: JOHNS HOPKINS UNIV,SCH MED,DEPT PHYSIOL,BALTIMORE,MD 21205

MCGRATH, SA
论文数: 0 引用数: 0
h-index: 0
机构: JOHNS HOPKINS UNIV,SCH MED,DEPT PHYSIOL,BALTIMORE,MD 21205

SOLOW, R
论文数: 0 引用数: 0
h-index: 0
机构: JOHNS HOPKINS UNIV,SCH MED,DEPT PHYSIOL,BALTIMORE,MD 21205

OKA, H
论文数: 0 引用数: 0
h-index: 0
机构: JOHNS HOPKINS UNIV,SCH MED,DEPT PHYSIOL,BALTIMORE,MD 21205

ZEITLIN, PL
论文数: 0 引用数: 0
h-index: 0
机构: JOHNS HOPKINS UNIV,SCH MED,DEPT PHYSIOL,BALTIMORE,MD 21205

GUGGINO, WB
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h-index: 0
机构: JOHNS HOPKINS UNIV,SCH MED,DEPT PHYSIOL,BALTIMORE,MD 21205

CARTER, BJ
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h-index: 0
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Flotte, TR
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2004, 11 (10)
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Flotte, TR
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Univ Florida, Dept Pediat, Gainesville, FL 32610 USA Univ Florida, Dept Pediat, Gainesville, FL 32610 USA
[20]
ZFN, TALEN, and CRISPR/Cas-based methods for genome engineering
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Gaj, Thomas
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TRENDS IN BIOTECHNOLOGY,
2013, 31 (07)
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Gaj, Thomas
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Scripps Res Inst, Skaggs Inst Chem Biol, La Jolla, CA 92037 USA
Scripps Res Inst, Dept Mol Biol, La Jolla, CA 92037 USA
Scripps Res Inst, Dept Chem, La Jolla, CA 92037 USA Scripps Res Inst, Skaggs Inst Chem Biol, La Jolla, CA 92037 USA

Gersbach, Charles A.
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Duke Univ, Dept Biomed Engn, Durham, NC 27706 USA
Duke Univ, Inst Genome Sci & Policy, Durham, NC USA Scripps Res Inst, Skaggs Inst Chem Biol, La Jolla, CA 92037 USA

Barbas, Carlos F., III
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Scripps Res Inst, Skaggs Inst Chem Biol, La Jolla, CA 92037 USA
Scripps Res Inst, Dept Mol Biol, La Jolla, CA 92037 USA
Scripps Res Inst, Dept Chem, La Jolla, CA 92037 USA Scripps Res Inst, Skaggs Inst Chem Biol, La Jolla, CA 92037 USA