共 73 条
[1]
Directed Evolution of Adeno-associated Virus for Enhanced Gene Delivery and Gene Targeting in Human Pluripotent Stem Cells
[J].
Asuri, Prashanth
;
Bartel, Melissa A.
;
Vazin, Tandis
;
Jang, Jae-Hyung
;
Wong, Tiffany B.
;
Schaffer, David V.
.
MOLECULAR THERAPY,
2012, 20 (02)
:329-338

Asuri, Prashanth
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Calif Berkeley, Dept Chem & Biomol Engn, Berkeley, CA 94720 USA
Univ Calif Berkeley, Dept Bioengn, Berkeley, CA 94720 USA
Univ Calif Berkeley, Helen Wills Neurosci Inst, Berkeley, CA 94720 USA Univ Calif Berkeley, Dept Chem & Biomol Engn, Berkeley, CA 94720 USA

Bartel, Melissa A.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Calif Berkeley, Dept Chem & Biomol Engn, Berkeley, CA 94720 USA
Univ Calif Berkeley, Dept Bioengn, Berkeley, CA 94720 USA
Univ Calif Berkeley, Helen Wills Neurosci Inst, Berkeley, CA 94720 USA Univ Calif Berkeley, Dept Chem & Biomol Engn, Berkeley, CA 94720 USA

Vazin, Tandis
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Calif Berkeley, Dept Chem & Biomol Engn, Berkeley, CA 94720 USA
Univ Calif Berkeley, Dept Bioengn, Berkeley, CA 94720 USA
Univ Calif Berkeley, Helen Wills Neurosci Inst, Berkeley, CA 94720 USA Univ Calif Berkeley, Dept Chem & Biomol Engn, Berkeley, CA 94720 USA

Jang, Jae-Hyung
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Calif Berkeley, Dept Chem & Biomol Engn, Berkeley, CA 94720 USA
Univ Calif Berkeley, Dept Bioengn, Berkeley, CA 94720 USA
Univ Calif Berkeley, Helen Wills Neurosci Inst, Berkeley, CA 94720 USA
Yonsei Univ, Dept Chem & Biomol Engn, Seoul 120749, South Korea Univ Calif Berkeley, Dept Chem & Biomol Engn, Berkeley, CA 94720 USA

Wong, Tiffany B.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Calif Berkeley, Dept Mol & Cell Biol, Berkeley, CA 94720 USA Univ Calif Berkeley, Dept Chem & Biomol Engn, Berkeley, CA 94720 USA

Schaffer, David V.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Calif Berkeley, Dept Chem & Biomol Engn, Berkeley, CA 94720 USA
Univ Calif Berkeley, Dept Bioengn, Berkeley, CA 94720 USA
Univ Calif Berkeley, Helen Wills Neurosci Inst, Berkeley, CA 94720 USA Univ Calif Berkeley, Dept Chem & Biomol Engn, Berkeley, CA 94720 USA
[2]
Effect of gene therapy on visual function in Leber's congenital amaurosis
[J].
Bainbridge, James W. B.
;
Smith, Alexander J.
;
Barker, Susie S.
;
Robbie, Scott
;
Henderson, Robert
;
Balaggan, Kamaljit
;
Viswanathan, Ananth
;
Holder, Graham E.
;
Stockman, Andrew
;
Tyler, Nick
;
Petersen-Jones, Simon
;
Bhattacharya, Shomi S.
;
Thrasher, Adrian J.
;
Fitzke, Fred W.
;
Carter, Barrie J.
;
Rubin, Gary S.
;
Moore, Anthony T.
;
Ali, Robin R.
.
NEW ENGLAND JOURNAL OF MEDICINE,
2008, 358 (21)
:2231-2239

Bainbridge, James W. B.
论文数: 0 引用数: 0
h-index: 0
机构:
UCL, Inst Ophthalmol, London EC1V 9EL, England
Moorfields Eye Hosp, London, England
UCL, Natl Inst Hlth Res, Biomed Res Ctr Ophthalmol, London, England UCL, Inst Ophthalmol, London EC1V 9EL, England

Smith, Alexander J.
论文数: 0 引用数: 0
h-index: 0
机构:
UCL, Inst Ophthalmol, London EC1V 9EL, England UCL, Inst Ophthalmol, London EC1V 9EL, England

Barker, Susie S.
论文数: 0 引用数: 0
h-index: 0
机构:
UCL, Inst Ophthalmol, London EC1V 9EL, England UCL, Inst Ophthalmol, London EC1V 9EL, England

Robbie, Scott
论文数: 0 引用数: 0
h-index: 0
机构:
UCL, Inst Ophthalmol, London EC1V 9EL, England UCL, Inst Ophthalmol, London EC1V 9EL, England

Henderson, Robert
论文数: 0 引用数: 0
h-index: 0
机构:
UCL, Inst Ophthalmol, London EC1V 9EL, England UCL, Inst Ophthalmol, London EC1V 9EL, England

Balaggan, Kamaljit
论文数: 0 引用数: 0
h-index: 0
机构:
UCL, Inst Ophthalmol, London EC1V 9EL, England UCL, Inst Ophthalmol, London EC1V 9EL, England

Viswanathan, Ananth
论文数: 0 引用数: 0
h-index: 0
机构:
UCL, Inst Ophthalmol, London EC1V 9EL, England
Moorfields Eye Hosp, London, England UCL, Inst Ophthalmol, London EC1V 9EL, England

Holder, Graham E.
论文数: 0 引用数: 0
h-index: 0
机构:
UCL, Inst Ophthalmol, London EC1V 9EL, England
Moorfields Eye Hosp, London, England UCL, Inst Ophthalmol, London EC1V 9EL, England

Stockman, Andrew
论文数: 0 引用数: 0
h-index: 0
机构:
UCL, Inst Ophthalmol, London EC1V 9EL, England UCL, Inst Ophthalmol, London EC1V 9EL, England

Tyler, Nick
论文数: 0 引用数: 0
h-index: 0
机构:
UCL, Dept Civil & Environm Engn, London, England UCL, Inst Ophthalmol, London EC1V 9EL, England

论文数: 引用数:
h-index:
机构:

Bhattacharya, Shomi S.
论文数: 0 引用数: 0
h-index: 0
机构:
UCL, Inst Ophthalmol, London EC1V 9EL, England UCL, Inst Ophthalmol, London EC1V 9EL, England

Thrasher, Adrian J.
论文数: 0 引用数: 0
h-index: 0
机构:
UCL, Inst Child Hlth, London, England UCL, Inst Ophthalmol, London EC1V 9EL, England

Fitzke, Fred W.
论文数: 0 引用数: 0
h-index: 0
机构:
UCL, Inst Ophthalmol, London EC1V 9EL, England UCL, Inst Ophthalmol, London EC1V 9EL, England

Carter, Barrie J.
论文数: 0 引用数: 0
h-index: 0
机构:
Targeted Genet Corp, Seattle, WA USA UCL, Inst Ophthalmol, London EC1V 9EL, England

Rubin, Gary S.
论文数: 0 引用数: 0
h-index: 0
机构:
UCL, Inst Ophthalmol, London EC1V 9EL, England
Moorfields Eye Hosp, London, England
UCL, Natl Inst Hlth Res, Biomed Res Ctr Ophthalmol, London, England UCL, Inst Ophthalmol, London EC1V 9EL, England

Moore, Anthony T.
论文数: 0 引用数: 0
h-index: 0
机构:
UCL, Inst Ophthalmol, London EC1V 9EL, England
Moorfields Eye Hosp, London, England
UCL, Natl Inst Hlth Res, Biomed Res Ctr Ophthalmol, London, England UCL, Inst Ophthalmol, London EC1V 9EL, England

Ali, Robin R.
论文数: 0 引用数: 0
h-index: 0
机构:
UCL, Inst Ophthalmol, London EC1V 9EL, England
Moorfields Eye Hosp, London, England
UCL, Natl Inst Hlth Res, Biomed Res Ctr Ophthalmol, London, England
UCL, Inst Child Hlth, London, England UCL, Inst Ophthalmol, London EC1V 9EL, England
[3]
Directed evolution of novel adeno-associated viruses for therapeutic gene delivery
[J].
Bartel, M. A.
;
Weinstein, J. R.
;
Schaffer, D. V.
.
GENE THERAPY,
2012, 19 (06)
:694-700

Bartel, M. A.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Calif Berkeley, Dept Chem & Biomol Engn, Berkeley, CA 94720 USA Univ Calif Berkeley, Dept Chem & Biomol Engn, Berkeley, CA 94720 USA

Weinstein, J. R.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Calif Berkeley, Dept Chem, Berkeley, CA 94720 USA Univ Calif Berkeley, Dept Chem & Biomol Engn, Berkeley, CA 94720 USA

Schaffer, D. V.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Calif Berkeley, Dept Chem & Biomol Engn, Berkeley, CA 94720 USA
Univ Calif Berkeley, Dept Bioengn, Berkeley, CA 94720 USA
Univ Calif Berkeley, Helen Wills Neurosci Inst, Berkeley, CA 94720 USA Univ Calif Berkeley, Dept Chem & Biomol Engn, Berkeley, CA 94720 USA
[4]
Bartel MA, 2012, MOL THER, V20, pS140
[5]
Evaluation of Adeno-Associated Viral Vectors for Liver-Directed Gene Transfer in Dogs
[J].
Bell, Peter
;
Gao, Guangping
;
Haskins, Mark E.
;
Wang, Lili
;
Sleeper, Meg
;
Wang, Huan
;
Calcedo, Roberto
;
Vandenberghe, Luk H.
;
Chen, Shu-Jen
;
Weisse, Chick
;
Withnall, Elanor
;
Wilson, James M.
.
HUMAN GENE THERAPY,
2011, 22 (08)
:985-997

Bell, Peter
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Penn, Dept Pathol & Lab Med, Gene Therapy Program, Philadelphia, PA 19104 USA Univ Penn, Dept Pathol & Lab Med, Gene Therapy Program, Philadelphia, PA 19104 USA

Gao, Guangping
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Penn, Dept Pathol & Lab Med, Gene Therapy Program, Philadelphia, PA 19104 USA Univ Penn, Dept Pathol & Lab Med, Gene Therapy Program, Philadelphia, PA 19104 USA

Haskins, Mark E.
论文数: 0 引用数: 0
h-index: 0
机构: Univ Penn, Dept Pathol & Lab Med, Gene Therapy Program, Philadelphia, PA 19104 USA

Wang, Lili
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Penn, Dept Pathol & Lab Med, Gene Therapy Program, Philadelphia, PA 19104 USA Univ Penn, Dept Pathol & Lab Med, Gene Therapy Program, Philadelphia, PA 19104 USA

Sleeper, Meg
论文数: 0 引用数: 0
h-index: 0
机构: Univ Penn, Dept Pathol & Lab Med, Gene Therapy Program, Philadelphia, PA 19104 USA

Wang, Huan
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Penn, Dept Pathol & Lab Med, Gene Therapy Program, Philadelphia, PA 19104 USA Univ Penn, Dept Pathol & Lab Med, Gene Therapy Program, Philadelphia, PA 19104 USA

Calcedo, Roberto
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Penn, Dept Pathol & Lab Med, Gene Therapy Program, Philadelphia, PA 19104 USA Univ Penn, Dept Pathol & Lab Med, Gene Therapy Program, Philadelphia, PA 19104 USA

Vandenberghe, Luk H.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Penn, Dept Pathol & Lab Med, Gene Therapy Program, Philadelphia, PA 19104 USA Univ Penn, Dept Pathol & Lab Med, Gene Therapy Program, Philadelphia, PA 19104 USA

Chen, Shu-Jen
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Penn, Dept Pathol & Lab Med, Gene Therapy Program, Philadelphia, PA 19104 USA Univ Penn, Dept Pathol & Lab Med, Gene Therapy Program, Philadelphia, PA 19104 USA

Weisse, Chick
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Penn, Sch Vet Med, Dept Clin Studies, Philadelphia, PA 19104 USA Univ Penn, Dept Pathol & Lab Med, Gene Therapy Program, Philadelphia, PA 19104 USA

Withnall, Elanor
论文数: 0 引用数: 0
h-index: 0
机构: Univ Penn, Dept Pathol & Lab Med, Gene Therapy Program, Philadelphia, PA 19104 USA

Wilson, James M.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Penn, Dept Pathol & Lab Med, Gene Therapy Program, Philadelphia, PA 19104 USA Univ Penn, Dept Pathol & Lab Med, Gene Therapy Program, Philadelphia, PA 19104 USA
[6]
AAV2 Gene Therapy Readministration in Three Adults with Congenital Blindness
[J].
Bennett, Jean
;
Ashtari, Manzar
;
Wellman, Jennifer
;
Marshall, Kathleen A.
;
Cyckowski, Laura L.
;
Chung, Daniel C.
;
McCague, Sarah
;
Pierce, Eric A.
;
Chen, Yifeng
;
Bennicelli, Jeannette L.
;
Zhu, Xiaosong
;
Ying, Gui-shuang
;
Sun, Junwei
;
Wright, J. Fraser
;
Auricchio, Alberto
;
Simonelli, Francesca
;
Shindler, Kenneth S.
;
Mingozzi, Federico
;
High, Katherine A.
;
Maguire, Albert M.
.
SCIENCE TRANSLATIONAL MEDICINE,
2012, 4 (120)

Bennett, Jean
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Penn, FM Kirby Ctr Mol Ophthalmol, Scheie Eye Inst, Philadelphia, PA 19104 USA
Childrens Hosp Philadelphia, Ctr Cellular & Mol Therapeut, Philadelphia, PA 19104 USA Univ Penn, FM Kirby Ctr Mol Ophthalmol, Scheie Eye Inst, Philadelphia, PA 19104 USA

Ashtari, Manzar
论文数: 0 引用数: 0
h-index: 0
机构:
Childrens Hosp Philadelphia, Dept Radiol, Philadelphia, PA 19104 USA Univ Penn, FM Kirby Ctr Mol Ophthalmol, Scheie Eye Inst, Philadelphia, PA 19104 USA

Wellman, Jennifer
论文数: 0 引用数: 0
h-index: 0
机构:
Childrens Hosp Philadelphia, Ctr Cellular & Mol Therapeut, Philadelphia, PA 19104 USA Univ Penn, FM Kirby Ctr Mol Ophthalmol, Scheie Eye Inst, Philadelphia, PA 19104 USA

Marshall, Kathleen A.
论文数: 0 引用数: 0
h-index: 0
机构:
Childrens Hosp Philadelphia, Ctr Cellular & Mol Therapeut, Philadelphia, PA 19104 USA Univ Penn, FM Kirby Ctr Mol Ophthalmol, Scheie Eye Inst, Philadelphia, PA 19104 USA

Cyckowski, Laura L.
论文数: 0 引用数: 0
h-index: 0
机构:
Childrens Hosp Philadelphia, Dept Radiol, Philadelphia, PA 19104 USA Univ Penn, FM Kirby Ctr Mol Ophthalmol, Scheie Eye Inst, Philadelphia, PA 19104 USA

Chung, Daniel C.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Penn, FM Kirby Ctr Mol Ophthalmol, Scheie Eye Inst, Philadelphia, PA 19104 USA
Childrens Hosp Philadelphia, Ctr Cellular & Mol Therapeut, Philadelphia, PA 19104 USA Univ Penn, FM Kirby Ctr Mol Ophthalmol, Scheie Eye Inst, Philadelphia, PA 19104 USA

McCague, Sarah
论文数: 0 引用数: 0
h-index: 0
机构:
Childrens Hosp Philadelphia, Ctr Cellular & Mol Therapeut, Philadelphia, PA 19104 USA Univ Penn, FM Kirby Ctr Mol Ophthalmol, Scheie Eye Inst, Philadelphia, PA 19104 USA

Pierce, Eric A.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Penn, FM Kirby Ctr Mol Ophthalmol, Scheie Eye Inst, Philadelphia, PA 19104 USA
Childrens Hosp Philadelphia, Dept Ophthalmol, Philadelphia, PA 19104 USA Univ Penn, FM Kirby Ctr Mol Ophthalmol, Scheie Eye Inst, Philadelphia, PA 19104 USA

Chen, Yifeng
论文数: 0 引用数: 0
h-index: 0
机构:
Childrens Hosp Philadelphia, Ctr Cellular & Mol Therapeut, Philadelphia, PA 19104 USA Univ Penn, FM Kirby Ctr Mol Ophthalmol, Scheie Eye Inst, Philadelphia, PA 19104 USA

Bennicelli, Jeannette L.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Penn, FM Kirby Ctr Mol Ophthalmol, Scheie Eye Inst, Philadelphia, PA 19104 USA Univ Penn, FM Kirby Ctr Mol Ophthalmol, Scheie Eye Inst, Philadelphia, PA 19104 USA

Zhu, Xiaosong
论文数: 0 引用数: 0
h-index: 0
机构:
Childrens Hosp Philadelphia, Dept Ophthalmol, Philadelphia, PA 19104 USA Univ Penn, FM Kirby Ctr Mol Ophthalmol, Scheie Eye Inst, Philadelphia, PA 19104 USA

Ying, Gui-shuang
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Penn, Ctr Prevent Ophthalmol & Biostat, Scheie Eye Inst, Dept Ophthalmol, Philadelphia, PA 19104 USA Univ Penn, FM Kirby Ctr Mol Ophthalmol, Scheie Eye Inst, Philadelphia, PA 19104 USA

Sun, Junwei
论文数: 0 引用数: 0
h-index: 0
机构:
Childrens Hosp Philadelphia, Ctr Cellular & Mol Therapeut, Philadelphia, PA 19104 USA Univ Penn, FM Kirby Ctr Mol Ophthalmol, Scheie Eye Inst, Philadelphia, PA 19104 USA

Wright, J. Fraser
论文数: 0 引用数: 0
h-index: 0
机构:
Childrens Hosp Philadelphia, Ctr Cellular & Mol Therapeut, Philadelphia, PA 19104 USA Univ Penn, FM Kirby Ctr Mol Ophthalmol, Scheie Eye Inst, Philadelphia, PA 19104 USA

Auricchio, Alberto
论文数: 0 引用数: 0
h-index: 0
机构:
Telethon Inst Genet & Med, I-80131 Naples, Italy
Univ Naples Federico 2, Dept Pediat, I-80131 Naples, Italy Univ Penn, FM Kirby Ctr Mol Ophthalmol, Scheie Eye Inst, Philadelphia, PA 19104 USA

Simonelli, Francesca
论文数: 0 引用数: 0
h-index: 0
机构:
Telethon Inst Genet & Med, I-80131 Naples, Italy
Univ Naples 2, Dept Ophthalmol, I-80131 Naples, Italy Univ Penn, FM Kirby Ctr Mol Ophthalmol, Scheie Eye Inst, Philadelphia, PA 19104 USA

Shindler, Kenneth S.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Penn, FM Kirby Ctr Mol Ophthalmol, Scheie Eye Inst, Philadelphia, PA 19104 USA Univ Penn, FM Kirby Ctr Mol Ophthalmol, Scheie Eye Inst, Philadelphia, PA 19104 USA

Mingozzi, Federico
论文数: 0 引用数: 0
h-index: 0
机构:
Childrens Hosp Philadelphia, Ctr Cellular & Mol Therapeut, Philadelphia, PA 19104 USA Univ Penn, FM Kirby Ctr Mol Ophthalmol, Scheie Eye Inst, Philadelphia, PA 19104 USA

High, Katherine A.
论文数: 0 引用数: 0
h-index: 0
机构:
Childrens Hosp Philadelphia, Ctr Cellular & Mol Therapeut, Philadelphia, PA 19104 USA
Univ Penn, Howard Hughes Med Inst, Philadelphia, PA 19104 USA Univ Penn, FM Kirby Ctr Mol Ophthalmol, Scheie Eye Inst, Philadelphia, PA 19104 USA

Maguire, Albert M.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Penn, FM Kirby Ctr Mol Ophthalmol, Scheie Eye Inst, Philadelphia, PA 19104 USA
Childrens Hosp Philadelphia, Ctr Cellular & Mol Therapeut, Philadelphia, PA 19104 USA
Childrens Hosp Philadelphia, Dept Ophthalmol, Philadelphia, PA 19104 USA Univ Penn, FM Kirby Ctr Mol Ophthalmol, Scheie Eye Inst, Philadelphia, PA 19104 USA
[7]
Prevalence of Serum IgG and Neutralizing Factors Against Adeno-Associated Virus (AAV) Types 1, 2, 5, 6, 8, and 9 in the Healthy Population: Implications for Gene Therapy Using AAV Vectors
[J].
Boutin, Sylvie
;
Monteilhet, Virginie
;
Veron, Philippe
;
Leborgne, Christian
;
Benveniste, Olivier
;
Montus, Marie Francoise
;
Masurier, Carole
.
HUMAN GENE THERAPY,
2010, 21 (06)
:704-712

Boutin, Sylvie
论文数: 0 引用数: 0
h-index: 0
机构: Genethon, Serv Immunol, R&D, Immunol Lab, F-91002 Evry, France

Monteilhet, Virginie
论文数: 0 引用数: 0
h-index: 0
机构: Genethon, Serv Immunol, R&D, Immunol Lab, F-91002 Evry, France

Veron, Philippe
论文数: 0 引用数: 0
h-index: 0
机构: Genethon, Serv Immunol, R&D, Immunol Lab, F-91002 Evry, France

Leborgne, Christian
论文数: 0 引用数: 0
h-index: 0
机构: Genethon, Serv Immunol, R&D, Immunol Lab, F-91002 Evry, France

Benveniste, Olivier
论文数: 0 引用数: 0
h-index: 0
机构:
Hop La Pitie Salpetriere, AP HP, Fac Med Pierre & Marie Curie, F-75013 Paris, France Genethon, Serv Immunol, R&D, Immunol Lab, F-91002 Evry, France

Montus, Marie Francoise
论文数: 0 引用数: 0
h-index: 0
机构: Genethon, Serv Immunol, R&D, Immunol Lab, F-91002 Evry, France

Masurier, Carole
论文数: 0 引用数: 0
h-index: 0
机构:
Genethon, Serv Immunol, R&D, Immunol Lab, F-91002 Evry, France Genethon, Serv Immunol, R&D, Immunol Lab, F-91002 Evry, France
[8]
Marker rescue of adeno-associated virus (AAV) capsid mutants: a novel approach for chimeric AAV production
[J].
Bowles, DE
;
Rabinowitz, JE
;
Samulski, RJ
.
JOURNAL OF VIROLOGY,
2003, 77 (01)
:423-432

Bowles, DE
论文数: 0 引用数: 0
h-index: 0
机构:
Univ N Carolina, Gene Therapy Ctr, Chapel Hill, NC 27599 USA Univ N Carolina, Gene Therapy Ctr, Chapel Hill, NC 27599 USA

Rabinowitz, JE
论文数: 0 引用数: 0
h-index: 0
机构:
Univ N Carolina, Gene Therapy Ctr, Chapel Hill, NC 27599 USA Univ N Carolina, Gene Therapy Ctr, Chapel Hill, NC 27599 USA

Samulski, RJ
论文数: 0 引用数: 0
h-index: 0
机构:
Univ N Carolina, Gene Therapy Ctr, Chapel Hill, NC 27599 USA Univ N Carolina, Gene Therapy Ctr, Chapel Hill, NC 27599 USA
[9]
Rare-disease genetics in the era of next-generation sequencing: discovery to translation
[J].
Boycott, Kym M.
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Vanstone, Megan R.
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Bulman, Dennis E.
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MacKenzie, Alex E.
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NATURE REVIEWS GENETICS,
2013, 14 (10)
:681-691

Boycott, Kym M.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Ottawa, Dept Pediat, Ottawa, ON K1H 8L1, Canada Univ Ottawa, Dept Pediat, Ottawa, ON K1H 8L1, Canada

Vanstone, Megan R.
论文数: 0 引用数: 0
h-index: 0
机构: Univ Ottawa, Dept Pediat, Ottawa, ON K1H 8L1, Canada

Bulman, Dennis E.
论文数: 0 引用数: 0
h-index: 0
机构: Univ Ottawa, Dept Pediat, Ottawa, ON K1H 8L1, Canada

MacKenzie, Alex E.
论文数: 0 引用数: 0
h-index: 0
机构: Univ Ottawa, Dept Pediat, Ottawa, ON K1H 8L1, Canada
[10]
Effect of Alipogene Tiparvovec (AAV1-LPLS447X) on Postprandial Chylomicron Metabolism in Lipoprotein Lipase-Deficient Patients
[J].
Carpentier, Andre C.
;
Frisch, Frederique
;
Labbe, Sebastien M.
;
Gagnon, Rene
;
de Wal, Janneke
;
Greentree, Stephen
;
Petry, Harald
;
Twisk, Jaap
;
Brisson, Diane
;
Gaudet, Daniel
.
JOURNAL OF CLINICAL ENDOCRINOLOGY & METABOLISM,
2012, 97 (05)
:1635-1644

Carpentier, Andre C.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Sherbrooke, Dept Med, Div Endocrinol, Sherbrooke, PQ J1H 5N4, Canada Univ Sherbrooke, Dept Med, Div Endocrinol, Sherbrooke, PQ J1H 5N4, Canada

Frisch, Frederique
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Sherbrooke, Dept Med, Div Endocrinol, Sherbrooke, PQ J1H 5N4, Canada Univ Sherbrooke, Dept Med, Div Endocrinol, Sherbrooke, PQ J1H 5N4, Canada

Labbe, Sebastien M.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Sherbrooke, Dept Med, Div Endocrinol, Sherbrooke, PQ J1H 5N4, Canada Univ Sherbrooke, Dept Med, Div Endocrinol, Sherbrooke, PQ J1H 5N4, Canada

Gagnon, Rene
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Sherbrooke, Dept Pediat, Div Genet, Sherbrooke, PQ J1H 5N4, Canada Univ Sherbrooke, Dept Med, Div Endocrinol, Sherbrooke, PQ J1H 5N4, Canada

de Wal, Janneke
论文数: 0 引用数: 0
h-index: 0
机构:
Amsterdam Mol Therapeut BV, NL-1105 BA Amsterdam, Netherlands Univ Sherbrooke, Dept Med, Div Endocrinol, Sherbrooke, PQ J1H 5N4, Canada

Greentree, Stephen
论文数: 0 引用数: 0
h-index: 0
机构:
Amsterdam Mol Therapeut BV, NL-1105 BA Amsterdam, Netherlands Univ Sherbrooke, Dept Med, Div Endocrinol, Sherbrooke, PQ J1H 5N4, Canada

Petry, Harald
论文数: 0 引用数: 0
h-index: 0
机构:
Amsterdam Mol Therapeut BV, NL-1105 BA Amsterdam, Netherlands Univ Sherbrooke, Dept Med, Div Endocrinol, Sherbrooke, PQ J1H 5N4, Canada

Twisk, Jaap
论文数: 0 引用数: 0
h-index: 0
机构:
Amsterdam Mol Therapeut BV, NL-1105 BA Amsterdam, Netherlands Univ Sherbrooke, Dept Med, Div Endocrinol, Sherbrooke, PQ J1H 5N4, Canada

Brisson, Diane
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Univ Montreal, Dept Med, ECOGENE Clin Res Ctr 21, Chicoutimi, PQ H3G 1M8, Canada Univ Sherbrooke, Dept Med, Div Endocrinol, Sherbrooke, PQ J1H 5N4, Canada

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