Antisense-Mediated Exon Skipping for Duchenne Muscular Dystrophy

被引：0

作者：

Aartsma-Rus, Annemieke ^{[1
]}

Heemskerk, Hans ^{[1
]}

de Winter, Christa ^{[1
]}

van Putten, Maaike ^{[1
]}

Janson, Anneke ^{[2
]}

Verschuuren, Jan ^{[3
]}

den Dunnen, Johan ^{[1
]}

van Deutekom, Judith ^{[2
]}

van Ommen, Gert-Jan ^{[1
]}

机构：

[1] Leiden Univ, Dept Human Genet, Med Ctr, NL-2300 RA Leiden, Netherlands

[2] Prosensa Therapeut BV, Leiden, Netherlands

[3] Leiden Univ, Med Ctr, Dept Neurol, Leiden, Netherlands

来源：

HUMAN GENE THERAPY | 2009年 / 20卷 / 06期

关键词：

D O I：

暂无

中图分类号：

Q81 [生物工程学（生物技术）]; Q93 [微生物学];

学科分类号：

071005 ; 0836 ; 090102 ; 100705 ;

摘要：

引用

页码：660 / 661

页数：2

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