Emerging Gene Therapy Treatments for Inherited Retinal Diseases

被引：3

作者：

Bakall, Benjamin ^{[1
]}

Hariprasad, Seenu M. ^{[2
]}

Klein, Kendra A. ^{[1
]}

机构：

[1] Associated Retina Consultants, 1750 E Glendale Ave, Phoenix, AZ 85020 USA

[2] Univ Chicago, Dept Ophthalmol & Visual Sci, 5841 S Maryland Ave,MC2114, Chicago, IL 60637 USA

来源：

OPHTHALMIC SURGERY LASERS & IMAGING RETINA | 2018年 / 49卷 / 07期

关键词：

LEBER CONGENITAL AMAUROSIS; LINKED RETINITIS-PIGMENTOSA; MOUSE MODEL; ADENOASSOCIATED VIRUS; BLINDNESS; SAFETY; TRIAL; EFFICACY; CHOROIDEREMIA; RETINOSCHISIS;

D O I：

10.3928/23258160-20180628-02

中图分类号：

R77 [眼科学];

学科分类号：

100212 ;

摘要：

[No abstract available]

引用

页码：472 / 478

页数：7

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