共 10 条
[1]
[Anonymous], 2012, CONC PAP EXTR EFF SA
[2]
Nusinersen in later-onset spinalmuscular atrophy Long-term results from the phase 1/2 studies
[J].
Darras, Basil T.
;
Chiriboga, Claudia A.
;
Iannaccone, Susan T.
;
Swoboda, Kathryn J.
;
Montes, Jacqueline
;
Mignon, Laurence
;
Xia, Shuting
;
Bennett, C. Frank
;
Bishop, Kathie M.
;
Shefner, Jeremy M.
;
Green, Allison M.
;
Sun, Peng
;
Bhan, Ishir
;
Gheuens, Sarah
;
Schneider, Eugene
;
Farwell, Wildon
;
De Vivo, Darryl C.
;
Castro, Diana
;
Cowie, Margaret
;
Gilbreath, Heather
;
Johnson, Shanda
;
Kauk, Melissa
;
Khan, Muna
;
McElroy, Ebra
;
Kneirbein, Erin Neil
;
Nelson, Leslie
;
Smith, Lauren
;
Trest, Stephanie
;
Aziz-Zaman, Sonya
;
Cappell, Joshua
;
Constantinescu, Andrei
;
Cruz, Rosangel
;
Dastgir, Jahannaz
;
Dunaway, Sally
;
Holuba, Nicole
;
Khandji, Alexander G.
;
Kramer, Samantha
;
Marra, Jonathan
;
Ortiz-Miller, Courtney
;
Popolizio, Molly
;
Salazar, Rachel
;
Sanabria, Luz
;
Sproule, Douglas M.
;
Weimer, Louis
;
Berde, Charles
;
Binalsheikh, Ibrahim
;
Graham, Robert
;
Kang, Peter
;
Koka, Anjali
;
Landrigan-, Mary
.
NEUROLOGY,
2019, 92 (21)
:E2492-E2506

Darras, Basil T.
论文数: 0 引用数: 0
h-index: 0
机构:
Boston Childrens Hosp, Dept Neurol, Boston, MA 02115 USA Boston Childrens Hosp, Dept Neurol, Boston, MA 02115 USA

Chiriboga, Claudia A.
论文数: 0 引用数: 0
h-index: 0
机构:
Columbia Univ, Irving Med Ctr, Dept Neurol, New York, NY USA
Columbia Univ, Irving Med Ctr, Dept Pediat, New York, NY USA Boston Childrens Hosp, Dept Neurol, Boston, MA 02115 USA

Iannaccone, Susan T.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Texas Southwestern Med Ctr Dallas, Dept Pediat, Dallas, TX USA Boston Childrens Hosp, Dept Neurol, Boston, MA 02115 USA

Swoboda, Kathryn J.
论文数: 0 引用数: 0
h-index: 0
机构:
Massachusetts Gen Hosp, Dept Neurol, Boston, MA 02114 USA Boston Childrens Hosp, Dept Neurol, Boston, MA 02115 USA

Montes, Jacqueline
论文数: 0 引用数: 0
h-index: 0
机构:
Columbia Univ, Irving Med Ctr, Dept Neurol, New York, NY USA
Columbia Univ, Irving Med Ctr, Dept Rehabil & Regenerat Med, New York, NY USA Boston Childrens Hosp, Dept Neurol, Boston, MA 02115 USA

Mignon, Laurence
论文数: 0 引用数: 0
h-index: 0
机构:
Ionis Pharmaceut Inc, Carlsbad, CA USA Boston Childrens Hosp, Dept Neurol, Boston, MA 02115 USA

Xia, Shuting
论文数: 0 引用数: 0
h-index: 0
机构:
Ionis Pharmaceut Inc, Carlsbad, CA USA Boston Childrens Hosp, Dept Neurol, Boston, MA 02115 USA

Bennett, C. Frank
论文数: 0 引用数: 0
h-index: 0
机构:
Ionis Pharmaceut Inc, Carlsbad, CA USA Boston Childrens Hosp, Dept Neurol, Boston, MA 02115 USA

Bishop, Kathie M.
论文数: 0 引用数: 0
h-index: 0
机构:
Employee Ionis Pharmaceut Inc, Carlsbad, CA USA Boston Childrens Hosp, Dept Neurol, Boston, MA 02115 USA

Shefner, Jeremy M.
论文数: 0 引用数: 0
h-index: 0
机构:
Barrow Neurol Inst, Dept Neurol, Phoenix, AZ 85013 USA Boston Childrens Hosp, Dept Neurol, Boston, MA 02115 USA

Green, Allison M.
论文数: 0 引用数: 0
h-index: 0
机构:
Excel Sci Solut, Southport, CT USA Boston Childrens Hosp, Dept Neurol, Boston, MA 02115 USA

Sun, Peng
论文数: 0 引用数: 0
h-index: 0
机构:
Biogen, Cambridge, MA USA Boston Childrens Hosp, Dept Neurol, Boston, MA 02115 USA

Bhan, Ishir
论文数: 0 引用数: 0
h-index: 0
机构:
Biogen, Cambridge, MA USA Boston Childrens Hosp, Dept Neurol, Boston, MA 02115 USA

Gheuens, Sarah
论文数: 0 引用数: 0
h-index: 0
机构:
Biogen, Cambridge, MA USA Boston Childrens Hosp, Dept Neurol, Boston, MA 02115 USA

Schneider, Eugene
论文数: 0 引用数: 0
h-index: 0
机构:
Ionis Pharmaceut Inc, Carlsbad, CA USA Boston Childrens Hosp, Dept Neurol, Boston, MA 02115 USA

Farwell, Wildon
论文数: 0 引用数: 0
h-index: 0
机构:
Biogen, Cambridge, MA USA Boston Childrens Hosp, Dept Neurol, Boston, MA 02115 USA

De Vivo, Darryl C.
论文数: 0 引用数: 0
h-index: 0
机构:
Columbia Univ, Irving Med Ctr, Dept Neurol, New York, NY USA
Columbia Univ, Irving Med Ctr, Dept Pediat, New York, NY USA Boston Childrens Hosp, Dept Neurol, Boston, MA 02115 USA

Castro, Diana
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Texas Southwestern Med Ctr Dallas, Dallas, TX 75390 USA Boston Childrens Hosp, Dept Neurol, Boston, MA 02115 USA

Cowie, Margaret
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Texas Southwestern Med Ctr Dallas, Dallas, TX 75390 USA Boston Childrens Hosp, Dept Neurol, Boston, MA 02115 USA

Gilbreath, Heather
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Texas Southwestern Med Ctr Dallas, Dallas, TX 75390 USA Boston Childrens Hosp, Dept Neurol, Boston, MA 02115 USA

Johnson, Shanda
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Texas Southwestern Med Ctr Dallas, Dallas, TX 75390 USA Boston Childrens Hosp, Dept Neurol, Boston, MA 02115 USA

Kauk, Melissa
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Texas Southwestern Med Ctr Dallas, Dallas, TX 75390 USA Boston Childrens Hosp, Dept Neurol, Boston, MA 02115 USA

Khan, Muna
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Texas Southwestern Med Ctr Dallas, Dallas, TX 75390 USA Boston Childrens Hosp, Dept Neurol, Boston, MA 02115 USA

McElroy, Ebra
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Texas Southwestern Med Ctr Dallas, Dallas, TX 75390 USA Boston Childrens Hosp, Dept Neurol, Boston, MA 02115 USA

Kneirbein, Erin Neil
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Texas Southwestern Med Ctr Dallas, Dallas, TX 75390 USA Boston Childrens Hosp, Dept Neurol, Boston, MA 02115 USA

Nelson, Leslie
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Texas Southwestern Med Ctr Dallas, Dallas, TX 75390 USA Boston Childrens Hosp, Dept Neurol, Boston, MA 02115 USA

Smith, Lauren
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Texas Southwestern Med Ctr Dallas, Dallas, TX 75390 USA Boston Childrens Hosp, Dept Neurol, Boston, MA 02115 USA

Trest, Stephanie
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Texas Southwestern Med Ctr Dallas, Dallas, TX 75390 USA Boston Childrens Hosp, Dept Neurol, Boston, MA 02115 USA

Aziz-Zaman, Sonya
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Texas Southwestern Med Ctr Dallas, Dallas, TX 75390 USA
Columbia Univ, Med Ctr, New York, NY USA Boston Childrens Hosp, Dept Neurol, Boston, MA 02115 USA

Cappell, Joshua
论文数: 0 引用数: 0
h-index: 0
机构:
Columbia Univ, Med Ctr, New York, NY USA Boston Childrens Hosp, Dept Neurol, Boston, MA 02115 USA

Constantinescu, Andrei
论文数: 0 引用数: 0
h-index: 0
机构:
Columbia Univ, Med Ctr, New York, NY USA Boston Childrens Hosp, Dept Neurol, Boston, MA 02115 USA

Cruz, Rosangel
论文数: 0 引用数: 0
h-index: 0
机构:
Columbia Univ, Med Ctr, New York, NY USA Boston Childrens Hosp, Dept Neurol, Boston, MA 02115 USA

Dastgir, Jahannaz
论文数: 0 引用数: 0
h-index: 0
机构:
Columbia Univ, Med Ctr, New York, NY USA Boston Childrens Hosp, Dept Neurol, Boston, MA 02115 USA

Dunaway, Sally
论文数: 0 引用数: 0
h-index: 0
机构:
Columbia Univ, Med Ctr, New York, NY USA Boston Childrens Hosp, Dept Neurol, Boston, MA 02115 USA

Holuba, Nicole
论文数: 0 引用数: 0
h-index: 0
机构:
Columbia Univ, Med Ctr, New York, NY USA Boston Childrens Hosp, Dept Neurol, Boston, MA 02115 USA

Khandji, Alexander G.
论文数: 0 引用数: 0
h-index: 0
机构:
Columbia Univ, Med Ctr, New York, NY USA Boston Childrens Hosp, Dept Neurol, Boston, MA 02115 USA

Kramer, Samantha
论文数: 0 引用数: 0
h-index: 0
机构:
Columbia Univ, Med Ctr, New York, NY USA Boston Childrens Hosp, Dept Neurol, Boston, MA 02115 USA

Marra, Jonathan
论文数: 0 引用数: 0
h-index: 0
机构:
Columbia Univ, Med Ctr, New York, NY USA Boston Childrens Hosp, Dept Neurol, Boston, MA 02115 USA

Ortiz-Miller, Courtney
论文数: 0 引用数: 0
h-index: 0
机构:
Columbia Univ, Med Ctr, New York, NY USA Boston Childrens Hosp, Dept Neurol, Boston, MA 02115 USA

Popolizio, Molly
论文数: 0 引用数: 0
h-index: 0
机构:
Columbia Univ, Med Ctr, New York, NY USA Boston Childrens Hosp, Dept Neurol, Boston, MA 02115 USA

Salazar, Rachel
论文数: 0 引用数: 0
h-index: 0
机构:
Columbia Univ, Med Ctr, New York, NY USA Boston Childrens Hosp, Dept Neurol, Boston, MA 02115 USA

Sanabria, Luz
论文数: 0 引用数: 0
h-index: 0
机构:
Columbia Univ, Med Ctr, New York, NY USA Boston Childrens Hosp, Dept Neurol, Boston, MA 02115 USA

Sproule, Douglas M.
论文数: 0 引用数: 0
h-index: 0
机构:
Columbia Univ, Med Ctr, New York, NY USA Boston Childrens Hosp, Dept Neurol, Boston, MA 02115 USA

Weimer, Louis
论文数: 0 引用数: 0
h-index: 0
机构:
Columbia Univ, Med Ctr, New York, NY USA Boston Childrens Hosp, Dept Neurol, Boston, MA 02115 USA

Berde, Charles
论文数: 0 引用数: 0
h-index: 0
机构:
Boston Childrens Hosp, Boston, MA USA Boston Childrens Hosp, Dept Neurol, Boston, MA 02115 USA

Binalsheikh, Ibrahim
论文数: 0 引用数: 0
h-index: 0
机构:
Boston Childrens Hosp, Boston, MA USA Boston Childrens Hosp, Dept Neurol, Boston, MA 02115 USA

Graham, Robert
论文数: 0 引用数: 0
h-index: 0
机构:
Boston Childrens Hosp, Boston, MA USA Boston Childrens Hosp, Dept Neurol, Boston, MA 02115 USA

Kang, Peter
论文数: 0 引用数: 0
h-index: 0
机构:
Boston Childrens Hosp, Boston, MA USA Boston Childrens Hosp, Dept Neurol, Boston, MA 02115 USA

Koka, Anjali
论文数: 0 引用数: 0
h-index: 0
机构:
Boston Childrens Hosp, Boston, MA USA Boston Childrens Hosp, Dept Neurol, Boston, MA 02115 USA

Landrigan-, Mary
论文数: 0 引用数: 0
h-index: 0
机构:
Boston Childrens Hosp, Boston, MA USA Boston Childrens Hosp, Dept Neurol, Boston, MA 02115 USA
[3]
Day J, 2018, NEUROLOGY S, V90, pS46
[4]
Elsheikh B, 2018, NEUROLOGY S, V90, pS46
[5]
Nusinersen versus Sham Control in Infantile-Onset Spinal Muscular Atrophy
[J].
Finkel, R. S.
;
Mercuri, E.
;
Darras, B. T.
;
Connolly, A. M.
;
Kuntz, N. L.
;
Kirschner, J.
;
Chiriboga, C. A.
;
Saito, K.
;
Servais, L.
;
Tizzano, E.
;
Topaloglu, H.
;
Tulinius, M.
;
Montes, J.
;
Glanzman, A. M.
;
Bishop, K.
;
Zhong, Z. J.
;
Gheuens, S.
;
Bennett, C. F.
;
Schneider, E.
;
Farwell, W.
;
De Vivo, D. C.
.
NEW ENGLAND JOURNAL OF MEDICINE,
2017, 377 (18)
:1723-1732

Finkel, R. S.
论文数: 0 引用数: 0
h-index: 0
机构:
Nemours Childrens Hosp, Dept Pediat, Div Neurol, 13535 Nemours Pkwy,5th Fl, Orlando, FL 32827 USA Nemours Childrens Hosp, Dept Pediat, Div Neurol, 13535 Nemours Pkwy,5th Fl, Orlando, FL 32827 USA

Mercuri, E.
论文数: 0 引用数: 0
h-index: 0
机构:
Catholic Univ, Dept Pediat Neurol, Rome, Italy Nemours Childrens Hosp, Dept Pediat, Div Neurol, 13535 Nemours Pkwy,5th Fl, Orlando, FL 32827 USA

Darras, B. T.
论文数: 0 引用数: 0
h-index: 0
机构:
Boston Childrens Hosp, Dept Neurol, Boston, MA USA Nemours Childrens Hosp, Dept Pediat, Div Neurol, 13535 Nemours Pkwy,5th Fl, Orlando, FL 32827 USA

Connolly, A. M.
论文数: 0 引用数: 0
h-index: 0
机构:
St Louis Childrens Hosp, Dept Neurol, St Louis, MO 63178 USA Nemours Childrens Hosp, Dept Pediat, Div Neurol, 13535 Nemours Pkwy,5th Fl, Orlando, FL 32827 USA

Kuntz, N. L.
论文数: 0 引用数: 0
h-index: 0
机构:
Ann & Robert H Lurie Childrens Hosp Chicago, Dept Pediat, Chicago, IL 60611 USA Nemours Childrens Hosp, Dept Pediat, Div Neurol, 13535 Nemours Pkwy,5th Fl, Orlando, FL 32827 USA

Kirschner, J.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Freiburg, Fac Med, Med Ctr, Dept Neuropediat & Muscle Disorders, Freiburg, Germany Nemours Childrens Hosp, Dept Pediat, Div Neurol, 13535 Nemours Pkwy,5th Fl, Orlando, FL 32827 USA

Chiriboga, C. A.
论文数: 0 引用数: 0
h-index: 0
机构:
Columbia Univ, Dept Neurol, New York, NY USA Nemours Childrens Hosp, Dept Pediat, Div Neurol, 13535 Nemours Pkwy,5th Fl, Orlando, FL 32827 USA

Saito, K.
论文数: 0 引用数: 0
h-index: 0
机构:
Tokyo Womens Med Coll, Inst Med Genet, Tokyo, Japan
Tokyo Womens Med Coll, Dept Pediat, Tokyo, Japan Nemours Childrens Hosp, Dept Pediat, Div Neurol, 13535 Nemours Pkwy,5th Fl, Orlando, FL 32827 USA

Servais, L.
论文数: 0 引用数: 0
h-index: 0
机构:
Inst Mot, Paris, France Nemours Childrens Hosp, Dept Pediat, Div Neurol, 13535 Nemours Pkwy,5th Fl, Orlando, FL 32827 USA

Tizzano, E.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Hosp Vall dHebron, Dept Clin & Mol Genet, Barcelona, Spain
Univ Hosp Vall dHebron, Rare Dis Unit, Barcelona, Spain
Ctr Invest Biomed Enfermedades Raras CIBERER, Barcelona, Spain Nemours Childrens Hosp, Dept Pediat, Div Neurol, 13535 Nemours Pkwy,5th Fl, Orlando, FL 32827 USA

Topaloglu, H.
论文数: 0 引用数: 0
h-index: 0
机构:
Hacettepe Univ, Sch Med, Dept Pediat, Ankara, Turkey Nemours Childrens Hosp, Dept Pediat, Div Neurol, 13535 Nemours Pkwy,5th Fl, Orlando, FL 32827 USA

Tulinius, M.
论文数: 0 引用数: 0
h-index: 0
机构:
Gothenburg Univ, Queen Silvia Childrens Hosp, Dept Pediat, Gothenburg, Sweden Nemours Childrens Hosp, Dept Pediat, Div Neurol, 13535 Nemours Pkwy,5th Fl, Orlando, FL 32827 USA

Montes, J.
论文数: 0 引用数: 0
h-index: 0
机构:
Columbia Univ, Dept Neurol, New York, NY USA
Columbia Univ, Dept Rehabil & Regenerat Med, New York, NY USA Nemours Childrens Hosp, Dept Pediat, Div Neurol, 13535 Nemours Pkwy,5th Fl, Orlando, FL 32827 USA

Glanzman, A. M.
论文数: 0 引用数: 0
h-index: 0
机构:
Childrens Hosp Philadelphia, Dept Phys Therapy, Philadelphia, PA 19104 USA Nemours Childrens Hosp, Dept Pediat, Div Neurol, 13535 Nemours Pkwy,5th Fl, Orlando, FL 32827 USA

Bishop, K.
论文数: 0 引用数: 0
h-index: 0
机构:
lonis Pharmaceut, Carlsbad, CA USA Nemours Childrens Hosp, Dept Pediat, Div Neurol, 13535 Nemours Pkwy,5th Fl, Orlando, FL 32827 USA

Zhong, Z. J.
论文数: 0 引用数: 0
h-index: 0
机构:
Biogen, Cambridge, MA USA Nemours Childrens Hosp, Dept Pediat, Div Neurol, 13535 Nemours Pkwy,5th Fl, Orlando, FL 32827 USA

Gheuens, S.
论文数: 0 引用数: 0
h-index: 0
机构:
Biogen, Cambridge, MA USA Nemours Childrens Hosp, Dept Pediat, Div Neurol, 13535 Nemours Pkwy,5th Fl, Orlando, FL 32827 USA

Bennett, C. F.
论文数: 0 引用数: 0
h-index: 0
机构:
lonis Pharmaceut, Carlsbad, CA USA Nemours Childrens Hosp, Dept Pediat, Div Neurol, 13535 Nemours Pkwy,5th Fl, Orlando, FL 32827 USA

Schneider, E.
论文数: 0 引用数: 0
h-index: 0
机构:
lonis Pharmaceut, Carlsbad, CA USA Nemours Childrens Hosp, Dept Pediat, Div Neurol, 13535 Nemours Pkwy,5th Fl, Orlando, FL 32827 USA

Farwell, W.
论文数: 0 引用数: 0
h-index: 0
机构:
Biogen, Cambridge, MA USA Nemours Childrens Hosp, Dept Pediat, Div Neurol, 13535 Nemours Pkwy,5th Fl, Orlando, FL 32827 USA

De Vivo, D. C.
论文数: 0 引用数: 0
h-index: 0
机构:
Columbia Univ, Dept Neurol, Med Ctr, New York, NY USA
Columbia Univ, Dept Pediat, Med Ctr, New York, NY 10027 USA Nemours Childrens Hosp, Dept Pediat, Div Neurol, 13535 Nemours Pkwy,5th Fl, Orlando, FL 32827 USA
[6]
Glascock Jacqueline, 2018, J Neuromuscul Dis, V5, P145, DOI 10.3233/JND-180304
[7]
Single-Dose Gene-Replacement Therapy for Spinal Muscular Atrophy
[J].
Mendell, J. R.
;
Al-Zaidy, S.
;
Shell, R.
;
Arnold, W. D.
;
Rodino-Klapac, L. R.
;
Prior, T. W.
;
Lowes, L.
;
Alfano, L.
;
Berry, K.
;
Church, K.
;
Kissel, J. T.
;
Nagendran, S.
;
L'Italien, J.
;
Sproule, D. M.
;
Wells, C.
;
Cardenas, J. A.
;
Heitzer, M. D.
;
Kaspar, A.
;
Corcoran, S.
;
Braun, L.
;
Likhite, S.
;
Miranda, C.
;
Meyer, K.
;
Foust, K. D.
;
Burghes, A. H. M.
;
Kaspar, B. K.
.
NEW ENGLAND JOURNAL OF MEDICINE,
2017, 377 (18)
:1713-1722

Mendell, J. R.
论文数: 0 引用数: 0
h-index: 0
机构:
Nationwide Childrens Hosp, Res Inst, Ctr Gene Therap, Columbus, OH 43205 USA
Ohio State Univ, Dept Pediat, Columbus, OH 43210 USA
Ohio State Univ, Dept Neurol, Columbus, OH 43210 USA Nationwide Childrens Hosp, Res Inst, Ctr Gene Therap, Columbus, OH 43205 USA

Al-Zaidy, S.
论文数: 0 引用数: 0
h-index: 0
机构:
Nationwide Childrens Hosp, Res Inst, Ctr Gene Therap, Columbus, OH 43205 USA
Ohio State Univ, Dept Pediat, Columbus, OH 43210 USA Nationwide Childrens Hosp, Res Inst, Ctr Gene Therap, Columbus, OH 43205 USA

论文数: 引用数:
h-index:
机构:

Arnold, W. D.
论文数: 0 引用数: 0
h-index: 0
机构:
Ohio State Univ, Dept Neurol, Columbus, OH 43210 USA Nationwide Childrens Hosp, Res Inst, Ctr Gene Therap, Columbus, OH 43205 USA

Rodino-Klapac, L. R.
论文数: 0 引用数: 0
h-index: 0
机构:
Nationwide Childrens Hosp, Res Inst, Ctr Gene Therap, Columbus, OH 43205 USA
Ohio State Univ, Dept Neurol, Columbus, OH 43210 USA Nationwide Childrens Hosp, Res Inst, Ctr Gene Therap, Columbus, OH 43205 USA

Prior, T. W.
论文数: 0 引用数: 0
h-index: 0
机构:
Ohio State Univ, Dept Pathol, Columbus, OH 43210 USA Nationwide Childrens Hosp, Res Inst, Ctr Gene Therap, Columbus, OH 43205 USA

Lowes, L.
论文数: 0 引用数: 0
h-index: 0
机构:
Nationwide Childrens Hosp, Res Inst, Ctr Gene Therap, Columbus, OH 43205 USA
Ohio State Univ, Dept Pediat, Columbus, OH 43210 USA Nationwide Childrens Hosp, Res Inst, Ctr Gene Therap, Columbus, OH 43205 USA

论文数: 引用数:
h-index:
机构:

Berry, K.
论文数: 0 引用数: 0
h-index: 0
机构:
Nationwide Childrens Hosp, Res Inst, Ctr Gene Therap, Columbus, OH 43205 USA
Ohio State Univ, Dept Pediat, Columbus, OH 43210 USA Nationwide Childrens Hosp, Res Inst, Ctr Gene Therap, Columbus, OH 43205 USA

Church, K.
论文数: 0 引用数: 0
h-index: 0
机构:
Nationwide Childrens Hosp, Res Inst, Ctr Gene Therap, Columbus, OH 43205 USA
Ohio State Univ, Dept Pediat, Columbus, OH 43210 USA Nationwide Childrens Hosp, Res Inst, Ctr Gene Therap, Columbus, OH 43205 USA

Kissel, J. T.
论文数: 0 引用数: 0
h-index: 0
机构:
Ohio State Univ, Dept Pediat, Columbus, OH 43210 USA Nationwide Childrens Hosp, Res Inst, Ctr Gene Therap, Columbus, OH 43205 USA

Nagendran, S.
论文数: 0 引用数: 0
h-index: 0
机构:
AveXis, Bannockburn, IL USA Nationwide Childrens Hosp, Res Inst, Ctr Gene Therap, Columbus, OH 43205 USA

L'Italien, J.
论文数: 0 引用数: 0
h-index: 0
机构:
AveXis, Bannockburn, IL USA Nationwide Childrens Hosp, Res Inst, Ctr Gene Therap, Columbus, OH 43205 USA

Sproule, D. M.
论文数: 0 引用数: 0
h-index: 0
机构:
AveXis, Bannockburn, IL USA Nationwide Childrens Hosp, Res Inst, Ctr Gene Therap, Columbus, OH 43205 USA

Wells, C.
论文数: 0 引用数: 0
h-index: 0
机构:
AveXis, Bannockburn, IL USA Nationwide Childrens Hosp, Res Inst, Ctr Gene Therap, Columbus, OH 43205 USA

Cardenas, J. A.
论文数: 0 引用数: 0
h-index: 0
机构:
AveXis, Bannockburn, IL USA Nationwide Childrens Hosp, Res Inst, Ctr Gene Therap, Columbus, OH 43205 USA

Heitzer, M. D.
论文数: 0 引用数: 0
h-index: 0
机构:
AveXis, Bannockburn, IL USA Nationwide Childrens Hosp, Res Inst, Ctr Gene Therap, Columbus, OH 43205 USA

Kaspar, A.
论文数: 0 引用数: 0
h-index: 0
机构:
AveXis, Bannockburn, IL USA Nationwide Childrens Hosp, Res Inst, Ctr Gene Therap, Columbus, OH 43205 USA

Corcoran, S.
论文数: 0 引用数: 0
h-index: 0
机构:
AveXis, Bannockburn, IL USA Nationwide Childrens Hosp, Res Inst, Ctr Gene Therap, Columbus, OH 43205 USA

Braun, L.
论文数: 0 引用数: 0
h-index: 0
机构:
AveXis, Bannockburn, IL USA Nationwide Childrens Hosp, Res Inst, Ctr Gene Therap, Columbus, OH 43205 USA

Likhite, S.
论文数: 0 引用数: 0
h-index: 0
机构:
Nationwide Childrens Hosp, Res Inst, Ctr Gene Therap, Columbus, OH 43205 USA Nationwide Childrens Hosp, Res Inst, Ctr Gene Therap, Columbus, OH 43205 USA

Miranda, C.
论文数: 0 引用数: 0
h-index: 0
机构:
Nationwide Childrens Hosp, Res Inst, Ctr Gene Therap, Columbus, OH 43205 USA Nationwide Childrens Hosp, Res Inst, Ctr Gene Therap, Columbus, OH 43205 USA

Meyer, K.
论文数: 0 引用数: 0
h-index: 0
机构:
Nationwide Childrens Hosp, Res Inst, Ctr Gene Therap, Columbus, OH 43205 USA Nationwide Childrens Hosp, Res Inst, Ctr Gene Therap, Columbus, OH 43205 USA

Foust, K. D.
论文数: 0 引用数: 0
h-index: 0
机构:
AveXis, Bannockburn, IL USA Nationwide Childrens Hosp, Res Inst, Ctr Gene Therap, Columbus, OH 43205 USA

Burghes, A. H. M.
论文数: 0 引用数: 0
h-index: 0
机构:
Ohio State Univ, Dept Neurol, Columbus, OH 43210 USA
Ohio State Univ, Dept Mol & Cellular Biochem, Columbus, OH 43210 USA Nationwide Childrens Hosp, Res Inst, Ctr Gene Therap, Columbus, OH 43205 USA

Kaspar, B. K.
论文数: 0 引用数: 0
h-index: 0
机构:
Nationwide Childrens Hosp, Res Inst, Ctr Gene Therap, Columbus, OH 43205 USA
Ohio State Univ, Dept Pediat, Columbus, OH 43210 USA
Ohio State Univ, Dept Neurol, Columbus, OH 43210 USA
AveXis, Bannockburn, IL USA Nationwide Childrens Hosp, Res Inst, Ctr Gene Therap, Columbus, OH 43205 USA
[8]
Nusinersen versus Sham Control in Later-Onset Spinal Muscular Atrophy
[J].
Mercuri, E.
;
Darras, B. T.
;
Chiriboga, C. A.
;
Day, J. W.
;
Campbell, C.
;
Connolly, A. M.
;
Iannaccone, S. T.
;
Kirschner, J.
;
Kuntz, N. L.
;
Saito, K.
;
Shieh, P. B.
;
Tulinius, M.
;
Mazzone, E. S.
;
Montes, J.
;
Bishop, K. M.
;
Yang, Q.
;
Foster, R.
;
Gheuens, S.
;
Bennett, C. F.
;
Farwell, W.
;
Schneider, E.
;
De Vivo, D. C.
;
Finkel, R. S.
;
Bradley, Walter G.
;
Kaufmann, Petra
;
Dickson, Patricia I.
;
Reingold, Stephen C.
;
Davis, Charles S.
;
Arredondo, Kristen
;
Castro, Diana
;
Cowie, Margaret
;
Farrow-Gillespie, Alan
;
Hebert, Andrew
;
Kauk, Melissa
;
Miller, Nancy
;
Nelson, Leslie
;
Spain, Thomas, Jr.
;
Cappell, Joshua
;
Constantinescu, Andrei
;
Cruz, Rosangel
;
Dastgir, Jahannaz
;
De Vivo, Darryl
;
Dunaway, Sally
;
Engelstad, Kristin
;
Khandji, Alexander G.
;
Kramer, Samantha
;
Marra, Jonathan
;
Popolizio, Molly
;
Salazar, Rachel
;
Weimer, Louis H.
.
NEW ENGLAND JOURNAL OF MEDICINE,
2018, 378 (07)
:625-635

Mercuri, E.
论文数: 0 引用数: 0
h-index: 0
机构:
Catholic Univ, Dept Pediat Neurol, Rome, Italy Catholic Univ, Dept Pediat Neurol, Rome, Italy

Darras, B. T.
论文数: 0 引用数: 0
h-index: 0
机构:
Boston Childrens Hosp, Dept Neurol, Boston, MA USA Catholic Univ, Dept Pediat Neurol, Rome, Italy

Chiriboga, C. A.
论文数: 0 引用数: 0
h-index: 0
机构:
Columbia Univ Med Ctr, Dept Neurol, New York, NY USA
Columbia Univ Med Ctr, Dept Pediat, New York, NY USA Catholic Univ, Dept Pediat Neurol, Rome, Italy

Day, J. W.
论文数: 0 引用数: 0
h-index: 0
机构:
Stanford Sch Med, Dept Neurol, Stanford, CA USA Catholic Univ, Dept Pediat Neurol, Rome, Italy

Campbell, C.
论文数: 0 引用数: 0
h-index: 0
机构:
Childrens Hosp, London Hlth Sci Ctr, London, ON, Canada Catholic Univ, Dept Pediat Neurol, Rome, Italy

Connolly, A. M.
论文数: 0 引用数: 0
h-index: 0
机构:
Washington Univ, Sch Med, Dept Neurol, St Louis, MO 63110 USA Catholic Univ, Dept Pediat Neurol, Rome, Italy

Iannaccone, S. T.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Texas Southwestern Med Ctr Dallas, Dept Pediat, Dallas, TX USA Catholic Univ, Dept Pediat Neurol, Rome, Italy

Kirschner, J.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Freiburg, Med Ctr, Fac Med, Dept Neuropediat & Muscle Disorders, Freiburg, Germany Catholic Univ, Dept Pediat Neurol, Rome, Italy

Kuntz, N. L.
论文数: 0 引用数: 0
h-index: 0
机构:
Ann & Robert H Lurie Childrens Hosp Chicago, Dept Pediat, Chicago, IL 60611 USA Catholic Univ, Dept Pediat Neurol, Rome, Italy

Saito, K.
论文数: 0 引用数: 0
h-index: 0
机构:
Tokyo Womens Med Univ, Inst Med Genet, Tokyo, Japan
Tokyo Womens Med Univ, Dept Pediat, Tokyo, Japan Catholic Univ, Dept Pediat Neurol, Rome, Italy

Shieh, P. B.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Calif Los Angeles, David Geffen Sch Med, Los Angeles, CA 90095 USA Catholic Univ, Dept Pediat Neurol, Rome, Italy

Tulinius, M.
论文数: 0 引用数: 0
h-index: 0
机构:
Gothenburg Univ, Queen Silvia Childrens Hosp, Dept Pediat, Gothenburg, Sweden Catholic Univ, Dept Pediat Neurol, Rome, Italy

Mazzone, E. S.
论文数: 0 引用数: 0
h-index: 0
机构:
Catholic Univ, Dept Pediat Neurol, Rome, Italy Catholic Univ, Dept Pediat Neurol, Rome, Italy

Montes, J.
论文数: 0 引用数: 0
h-index: 0
机构:
Columbia Univ Med Ctr, Dept Neurol, New York, NY USA
Columbia Univ Med Ctr, Dept Rehabil & Regenerat Med, New York, NY USA Catholic Univ, Dept Pediat Neurol, Rome, Italy

Bishop, K. M.
论文数: 0 引用数: 0
h-index: 0
机构:
Ionis Pharmaceut, Carlsbad, CA USA Catholic Univ, Dept Pediat Neurol, Rome, Italy

Yang, Q.
论文数: 0 引用数: 0
h-index: 0
机构:
Ionis Pharmaceut, Carlsbad, CA USA Catholic Univ, Dept Pediat Neurol, Rome, Italy

Foster, R.
论文数: 0 引用数: 0
h-index: 0
机构:
Biogen, Cambridge, MA USA Catholic Univ, Dept Pediat Neurol, Rome, Italy

Gheuens, S.
论文数: 0 引用数: 0
h-index: 0
机构:
Biogen, Cambridge, MA USA Catholic Univ, Dept Pediat Neurol, Rome, Italy

Bennett, C. F.
论文数: 0 引用数: 0
h-index: 0
机构:
Ionis Pharmaceut, Carlsbad, CA USA Catholic Univ, Dept Pediat Neurol, Rome, Italy

Farwell, W.
论文数: 0 引用数: 0
h-index: 0
机构:
Biogen, Cambridge, MA USA Catholic Univ, Dept Pediat Neurol, Rome, Italy

Schneider, E.
论文数: 0 引用数: 0
h-index: 0
机构:
Ionis Pharmaceut, Carlsbad, CA USA Catholic Univ, Dept Pediat Neurol, Rome, Italy

De Vivo, D. C.
论文数: 0 引用数: 0
h-index: 0
机构:
Columbia Univ Med Ctr, Dept Neurol, New York, NY USA
Columbia Univ Med Ctr, Dept Pediat, New York, NY USA Catholic Univ, Dept Pediat Neurol, Rome, Italy

Finkel, R. S.
论文数: 0 引用数: 0
h-index: 0
机构:
Nemours Childrens Hosp, Dept Pediat, Div Neurol, Orlando, FL USA Catholic Univ, Dept Pediat Neurol, Rome, Italy

Bradley, Walter G.
论文数: 0 引用数: 0
h-index: 0
机构: Catholic Univ, Dept Pediat Neurol, Rome, Italy

Kaufmann, Petra
论文数: 0 引用数: 0
h-index: 0
机构: Catholic Univ, Dept Pediat Neurol, Rome, Italy

Dickson, Patricia I.
论文数: 0 引用数: 0
h-index: 0
机构: Catholic Univ, Dept Pediat Neurol, Rome, Italy

Reingold, Stephen C.
论文数: 0 引用数: 0
h-index: 0
机构: Catholic Univ, Dept Pediat Neurol, Rome, Italy

Davis, Charles S.
论文数: 0 引用数: 0
h-index: 0
机构: Catholic Univ, Dept Pediat Neurol, Rome, Italy

Arredondo, Kristen
论文数: 0 引用数: 0
h-index: 0
机构: Catholic Univ, Dept Pediat Neurol, Rome, Italy

Castro, Diana
论文数: 0 引用数: 0
h-index: 0
机构: Catholic Univ, Dept Pediat Neurol, Rome, Italy

Cowie, Margaret
论文数: 0 引用数: 0
h-index: 0
机构: Catholic Univ, Dept Pediat Neurol, Rome, Italy

Farrow-Gillespie, Alan
论文数: 0 引用数: 0
h-index: 0
机构: Catholic Univ, Dept Pediat Neurol, Rome, Italy

Hebert, Andrew
论文数: 0 引用数: 0
h-index: 0
机构: Catholic Univ, Dept Pediat Neurol, Rome, Italy

Kauk, Melissa
论文数: 0 引用数: 0
h-index: 0
机构: Catholic Univ, Dept Pediat Neurol, Rome, Italy

Miller, Nancy
论文数: 0 引用数: 0
h-index: 0
机构: Catholic Univ, Dept Pediat Neurol, Rome, Italy

Nelson, Leslie
论文数: 0 引用数: 0
h-index: 0
机构: Catholic Univ, Dept Pediat Neurol, Rome, Italy

Spain, Thomas, Jr.
论文数: 0 引用数: 0
h-index: 0
机构: Catholic Univ, Dept Pediat Neurol, Rome, Italy

Cappell, Joshua
论文数: 0 引用数: 0
h-index: 0
机构: Catholic Univ, Dept Pediat Neurol, Rome, Italy

Constantinescu, Andrei
论文数: 0 引用数: 0
h-index: 0
机构: Catholic Univ, Dept Pediat Neurol, Rome, Italy

Cruz, Rosangel
论文数: 0 引用数: 0
h-index: 0
机构: Catholic Univ, Dept Pediat Neurol, Rome, Italy

Dastgir, Jahannaz
论文数: 0 引用数: 0
h-index: 0
机构: Catholic Univ, Dept Pediat Neurol, Rome, Italy

De Vivo, Darryl
论文数: 0 引用数: 0
h-index: 0
机构: Catholic Univ, Dept Pediat Neurol, Rome, Italy

Dunaway, Sally
论文数: 0 引用数: 0
h-index: 0
机构: Catholic Univ, Dept Pediat Neurol, Rome, Italy

Engelstad, Kristin
论文数: 0 引用数: 0
h-index: 0
机构: Catholic Univ, Dept Pediat Neurol, Rome, Italy

Khandji, Alexander G.
论文数: 0 引用数: 0
h-index: 0
机构: Catholic Univ, Dept Pediat Neurol, Rome, Italy

Kramer, Samantha
论文数: 0 引用数: 0
h-index: 0
机构: Catholic Univ, Dept Pediat Neurol, Rome, Italy

Marra, Jonathan
论文数: 0 引用数: 0
h-index: 0
机构: Catholic Univ, Dept Pediat Neurol, Rome, Italy

Popolizio, Molly
论文数: 0 引用数: 0
h-index: 0
机构: Catholic Univ, Dept Pediat Neurol, Rome, Italy

Salazar, Rachel
论文数: 0 引用数: 0
h-index: 0
机构: Catholic Univ, Dept Pediat Neurol, Rome, Italy

Weimer, Louis H.
论文数: 0 引用数: 0
h-index: 0
机构: Catholic Univ, Dept Pediat Neurol, Rome, Italy
[9]
Patterns of disease progression in type 2 and 3 SMA: Implications for clinical trials
[J].
Mercuri, Eugenio
;
Finkel, Richard
;
Montes, Jacqueline
;
Mazzone, Elena S.
;
Sormani, Maria Pia
;
Main, Marion
;
Ramsey, Danielle
;
Mayhew, Anna
;
Glanzman, Allan M.
;
Dunaway, Sally
;
Salazar, Rachel
;
Pasternak, Amy
;
Quigley, Janet
;
Pane, Marika
;
Pera, Maria Carmela
;
Scoto, Mariacristina
;
Messina, Sonia
;
Sframeli, Maria
;
Vita, Gian Luca
;
D'Amico, Adele
;
van den Hauwe, Marleen
;
Sivo, Serena
;
Goemans, Nathalie
;
Kaufmann, Petra
;
Darras, Basil T.
;
Bertini, Enrico
;
Muntoni, Francesco
;
De Vivo, Darryl C.
.
NEUROMUSCULAR DISORDERS,
2016, 26 (02)
:126-131

Mercuri, Eugenio
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Cattolica Sacro Cuore, Dept Paediat Neurol, I-00168 Rome, Italy Univ Cattolica Sacro Cuore, Dept Paediat Neurol, I-00168 Rome, Italy

Finkel, Richard
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Cent Florida, Coll Med, Nemours Childrens Hosp, Orlando, FL 32816 USA Univ Cattolica Sacro Cuore, Dept Paediat Neurol, I-00168 Rome, Italy

Montes, Jacqueline
论文数: 0 引用数: 0
h-index: 0
机构:
Columbia Univ, Med Ctr, Dept Neurol, New York, NY USA Univ Cattolica Sacro Cuore, Dept Paediat Neurol, I-00168 Rome, Italy

Mazzone, Elena S.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Cattolica Sacro Cuore, Dept Paediat Neurol, I-00168 Rome, Italy Univ Cattolica Sacro Cuore, Dept Paediat Neurol, I-00168 Rome, Italy

Sormani, Maria Pia
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Genoa, Dept Hlth Sci, Biostat Unit, Genoa, Italy Univ Cattolica Sacro Cuore, Dept Paediat Neurol, I-00168 Rome, Italy

Main, Marion
论文数: 0 引用数: 0
h-index: 0
机构:
UCL Inst Child Hlth, Dubowitz Neuromuscular Ctr, London, England
Great Ormond St Hosp Sick Children, London, England Univ Cattolica Sacro Cuore, Dept Paediat Neurol, I-00168 Rome, Italy

Ramsey, Danielle
论文数: 0 引用数: 0
h-index: 0
机构:
UCL Inst Child Hlth, Dubowitz Neuromuscular Ctr, London, England
Great Ormond St Hosp Sick Children, London, England Univ Cattolica Sacro Cuore, Dept Paediat Neurol, I-00168 Rome, Italy

Mayhew, Anna
论文数: 0 引用数: 0
h-index: 0
机构:
Newcastle Univ, Inst Med Genet, Newcastle Upon Tyne, Tyne & Wear, England Univ Cattolica Sacro Cuore, Dept Paediat Neurol, I-00168 Rome, Italy

Glanzman, Allan M.
论文数: 0 引用数: 0
h-index: 0
机构:
Childrens Hosp Philadelphia, Dept Phys Therapy, Philadelphia, PA 19104 USA Univ Cattolica Sacro Cuore, Dept Paediat Neurol, I-00168 Rome, Italy

Dunaway, Sally
论文数: 0 引用数: 0
h-index: 0
机构:
Columbia Univ, Med Ctr, Dept Neurol, New York, NY USA Univ Cattolica Sacro Cuore, Dept Paediat Neurol, I-00168 Rome, Italy

Salazar, Rachel
论文数: 0 引用数: 0
h-index: 0
机构:
Columbia Univ, Med Ctr, Dept Neurol, New York, NY USA Univ Cattolica Sacro Cuore, Dept Paediat Neurol, I-00168 Rome, Italy

Pasternak, Amy
论文数: 0 引用数: 0
h-index: 0
机构:
Harvard Univ, Sch Med, Dept Neurol, Boston Childrens Hosp, Boston, MA 02115 USA Univ Cattolica Sacro Cuore, Dept Paediat Neurol, I-00168 Rome, Italy

Quigley, Janet
论文数: 0 引用数: 0
h-index: 0
机构:
Harvard Univ, Sch Med, Dept Neurol, Boston Childrens Hosp, Boston, MA 02115 USA Univ Cattolica Sacro Cuore, Dept Paediat Neurol, I-00168 Rome, Italy

Pane, Marika
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Cattolica Sacro Cuore, Dept Paediat Neurol, I-00168 Rome, Italy Univ Cattolica Sacro Cuore, Dept Paediat Neurol, I-00168 Rome, Italy

Pera, Maria Carmela
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Cattolica Sacro Cuore, Dept Paediat Neurol, I-00168 Rome, Italy Univ Cattolica Sacro Cuore, Dept Paediat Neurol, I-00168 Rome, Italy

Scoto, Mariacristina
论文数: 0 引用数: 0
h-index: 0
机构:
UCL Inst Child Hlth, Dubowitz Neuromuscular Ctr, London, England
Great Ormond St Hosp Sick Children, London, England Univ Cattolica Sacro Cuore, Dept Paediat Neurol, I-00168 Rome, Italy

论文数: 引用数:
h-index:
机构:

Sframeli, Maria
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Messina, Dept Neurosci, Messina, Italy
Univ Messina, Nemo Sud Clin Ctr, Messina, Italy Univ Cattolica Sacro Cuore, Dept Paediat Neurol, I-00168 Rome, Italy

Vita, Gian Luca
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Messina, Dept Neurosci, Messina, Italy
Univ Messina, Nemo Sud Clin Ctr, Messina, Italy Univ Cattolica Sacro Cuore, Dept Paediat Neurol, I-00168 Rome, Italy

D'Amico, Adele
论文数: 0 引用数: 0
h-index: 0
机构:
IRCCS, Bambino Gesu Childrens Hosp, Dept Neurosci, Unit Neuromuscular & Neurodegenerat Disorders, Rome, Italy Univ Cattolica Sacro Cuore, Dept Paediat Neurol, I-00168 Rome, Italy

van den Hauwe, Marleen
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Hosp Leuven, Dept Child Neurol, Leuven, Belgium Univ Cattolica Sacro Cuore, Dept Paediat Neurol, I-00168 Rome, Italy

Sivo, Serena
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Cattolica Sacro Cuore, Dept Paediat Neurol, I-00168 Rome, Italy Univ Cattolica Sacro Cuore, Dept Paediat Neurol, I-00168 Rome, Italy

Goemans, Nathalie
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Hosp Leuven, Dept Child Neurol, Leuven, Belgium Univ Cattolica Sacro Cuore, Dept Paediat Neurol, I-00168 Rome, Italy

Kaufmann, Petra
论文数: 0 引用数: 0
h-index: 0
机构:
Columbia Univ, Med Ctr, Dept Neurol, New York, NY USA Univ Cattolica Sacro Cuore, Dept Paediat Neurol, I-00168 Rome, Italy

Darras, Basil T.
论文数: 0 引用数: 0
h-index: 0
机构:
Harvard Univ, Sch Med, Dept Neurol, Boston Childrens Hosp, Boston, MA 02115 USA Univ Cattolica Sacro Cuore, Dept Paediat Neurol, I-00168 Rome, Italy

Bertini, Enrico
论文数: 0 引用数: 0
h-index: 0
机构:
IRCCS, Bambino Gesu Childrens Hosp, Dept Neurosci, Unit Neuromuscular & Neurodegenerat Disorders, Rome, Italy Univ Cattolica Sacro Cuore, Dept Paediat Neurol, I-00168 Rome, Italy

Muntoni, Francesco
论文数: 0 引用数: 0
h-index: 0
机构:
UCL Inst Child Hlth, Dubowitz Neuromuscular Ctr, London, England
Great Ormond St Hosp Sick Children, London, England Univ Cattolica Sacro Cuore, Dept Paediat Neurol, I-00168 Rome, Italy

De Vivo, Darryl C.
论文数: 0 引用数: 0
h-index: 0
机构:
Columbia Univ, Med Ctr, Dept Neurol, New York, NY USA Univ Cattolica Sacro Cuore, Dept Paediat Neurol, I-00168 Rome, Italy
[10]
Evidence in focus: Nusinersen use in spinal muscular atrophy Report of the Guideline Development, Dissemination, and Implementation Subcommittee of the American Academy of Neurology
[J].
Michelson, David
;
Ciafaloni, Emma
;
Ashwal, Stephen
;
Lewis, Elliot
;
Narayanaswami, Pushpa
;
Oskoui, Maryam
;
Armstrong, Melissa J.
.
NEUROLOGY,
2018, 91 (20)
:923-933

Michelson, David
论文数: 0 引用数: 0
h-index: 0
机构:
Loma Linda Univ, Sch Med, Div Child Neurol, Dept Pediat, Loma Linda, CA 92350 USA Loma Linda Univ, Sch Med, Div Child Neurol, Dept Pediat, Loma Linda, CA 92350 USA

Ciafaloni, Emma
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Rochester, Med Ctr, Dept Neurol, Rochester, NY 14627 USA Loma Linda Univ, Sch Med, Div Child Neurol, Dept Pediat, Loma Linda, CA 92350 USA

Ashwal, Stephen
论文数: 0 引用数: 0
h-index: 0
机构:
Loma Linda Univ, Sch Med, Div Child Neurol, Dept Pediat, Loma Linda, CA 92350 USA Loma Linda Univ, Sch Med, Div Child Neurol, Dept Pediat, Loma Linda, CA 92350 USA

Lewis, Elliot
论文数: 0 引用数: 0
h-index: 0
机构: Loma Linda Univ, Sch Med, Div Child Neurol, Dept Pediat, Loma Linda, CA 92350 USA

Narayanaswami, Pushpa
论文数: 0 引用数: 0
h-index: 0
机构:
Harvard Med Sch, Beth Israel Deaconess Med Ctr, Boston, MA USA Loma Linda Univ, Sch Med, Div Child Neurol, Dept Pediat, Loma Linda, CA 92350 USA

Oskoui, Maryam
论文数: 0 引用数: 0
h-index: 0
机构:
McGill Univ, Dept Pediat & Neurol & Neurosurg, Montreal, PQ, Canada Loma Linda Univ, Sch Med, Div Child Neurol, Dept Pediat, Loma Linda, CA 92350 USA

Armstrong, Melissa J.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Florida, Coll Med, Dept Neurol, Gainesville, FL 32611 USA Loma Linda Univ, Sch Med, Div Child Neurol, Dept Pediat, Loma Linda, CA 92350 USA