[1] Univ Florida, Coll Med, Powell Gene Therapy Ctr, Gainesville, FL USA
[2] Univ Florida, Coll Med, Genet Inst, Gainesville, FL USA
[3] Univ Florida, Coll Med, Dept Mol Genet & Microbiol, Gainesville, FL USA
[4] Univ Florida, Coll Med, Dept Pediat, Gainesville, FL USA
[5] Univ Massachusetts, Sch Med, Off Dean, Worcester, MA USA
[6] Univ Massachusetts, Sch Med, Horae Gene Therapy Ctr, Worcester, MA USA
[7] Univ Massachusetts, Sch Med, Microbiol & Physiol Syst, Worcester, MA USA
[8] Univ Florida, Coll Med, Dept Ophthalmol, Gainesville, FL 32610 USA
[9] Free Univ Brussels, Dept Gene Therapy & Regenerat Med, Brussels, Belgium
[10] Univ N Carolina, Dept Mol Pharmaceut, Chapel Hill, NC USA
[11] Univ N Carolina, Gene Therapy Ctr, Chapel Hill, NC USA