EFFECT OF VX-770, A CFTR POTENTIATOR, ON SPIROMETRY AND QOL ASSESSMENT IN SUBJECTS WITH CF AND THE G551D-CFTR MUTATION

被引:0
作者
Boyle, M.
Clancy, J. P.
Rowe, S. M.
Durie, P. [1 ]
Dunitz, J.
Konstan, M. W.
Hornick, D.
Sagel, S. D.
Ramsey, B.
Dong, Q. [2 ]
Ordonez, C. [2 ]
Campbell, P.
Ashlock, M. [3 ]
Accurso, F. J.
机构
[1] Hosp Sick Children, Toronto, ON M5G 1X8, Canada
[2] Vertex Pharmaceut Inc, Cambridge, MA USA
[3] Cyst Fibrosis Fdn Therapeut Inc, Bethesda, MD USA
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D O I
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中图分类号
R72 [儿科学];
学科分类号
100202 ;
摘要
217
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页码:287 / 287
页数:1
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