AAV9 intracerebroventricular gene therapy improves lifespan and normalises long-term locomotor behaviour in a mouse model of Niemann-Pick type C1 disease

被引：0
|
作者：
Hughes, Michael [1 ]
Smith, Dave [2 ]
Morris, Lauren [2 ]
Fletcher, Claire [2 ]
Colaco, Allie [2 ]
Huebecker, Mylene [2 ]
Massaro, Giulia [1 ]
Tordo, Julie [3 ]
Palomar, Nuria [3 ]
Henckaerts, Els [3 ]
Waddington, Simon [4 ]
Platt, Fran [2 ]
Rahim, Ahad [1 ]
机构：
[1] UCL Sch Pharm, London, England
[2] Univ Oxford, Oxford, England
[3] Kings Coll London, London, England
[4] UCL Inst Womens Hlth, London, England
来源：
HUMAN GENE THERAPY | 2018年 / 29卷 / 07期
关键词：
D O I：
暂无
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
PO09
引用
收藏
页码：A8 / A8
页数：1
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