Development of an AAV-based microRNA gene therapy for treating spinocerebellar ataxia type 3

被引：0
作者：
Evers, Melvin
Martier, Raygene
Stricker-Shaver, Janice
Hubener-Schmid, Jeannette
Keskin, Sonay
van Deventer, Sander
Huu Phuc Nguyen
Higgins, Joseph J.
Konstantinova, Pavlina
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来源：
NEUROLOGY | 2019年 / 93卷 / 05期
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R74 [神经病学与精神病学];
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页码：E531 / E531
页数：1
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