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Characterization of the rat spinocerebellar ataxia type 3 gene
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Neurogenetics,
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I. Schmitt
论文数: 0 引用数: 0
h-index: 0
机构: Molecular Human Genetics,

T. Brattig
论文数: 0 引用数: 0
h-index: 0
机构: Molecular Human Genetics,

M. Gossen
论文数: 0 引用数: 0
h-index: 0
机构: Molecular Human Genetics,

O. Riess
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Extracellular vesicles for therapy of spinocerebellar ataxia type 3
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HUMAN GENE THERAPY,
2019, 30 (11)
:A101-A101

论文数: 引用数:
h-index:
机构:

Carmona, V.
论文数: 0 引用数: 0
h-index: 0
机构:
Ctr Neurosci & Cell Biol, Coimbra, Portugal
Univ Coimbra, Inst Interdisciplinary Res, Coimbra, Portugal Ctr Neurosci & Cell Biol, Coimbra, Portugal

Martins, I. M.
论文数: 0 引用数: 0
h-index: 0
机构:
Ctr Neurosci & Cell Biol, Coimbra, Portugal
Univ Coimbra, Inst Interdisciplinary Res, Coimbra, Portugal Ctr Neurosci & Cell Biol, Coimbra, Portugal

Barreira, M.
论文数: 0 引用数: 0
h-index: 0
机构:
Ctr Neurosci & Cell Biol, Coimbra, Portugal Ctr Neurosci & Cell Biol, Coimbra, Portugal

Albuquerque, P. R.
论文数: 0 引用数: 0
h-index: 0
机构:
Ctr Neurosci & Cell Biol, Coimbra, Portugal
Univ Coimbra, CIBB Ctr Innovat Biomed & Biotechnol, Coimbra, Portugal
Univ Coimbra, Fac Pharm, Coimbra, Portugal Ctr Neurosci & Cell Biol, Coimbra, Portugal

Faro, R.
论文数: 0 引用数: 0
h-index: 0
机构:
Ctr Neurosci & Cell Biol, Coimbra, Portugal Ctr Neurosci & Cell Biol, Coimbra, Portugal

Perfeito, R.
论文数: 0 引用数: 0
h-index: 0
机构:
Ctr Neurosci & Cell Biol, Coimbra, Portugal
Univ Coimbra, CIBB Ctr Innovat Biomed & Biotechnol, Coimbra, Portugal
Univ Coimbra, Inst Interdisciplinary Res, Coimbra, Portugal Ctr Neurosci & Cell Biol, Coimbra, Portugal

Nobre, R. J.
论文数: 0 引用数: 0
h-index: 0
机构:
Ctr Neurosci & Cell Biol, Coimbra, Portugal
Univ Coimbra, CIBB Ctr Innovat Biomed & Biotechnol, Coimbra, Portugal
Univ Coimbra, Inst Interdisciplinary Res, Coimbra, Portugal Ctr Neurosci & Cell Biol, Coimbra, Portugal

de Almeida, L. P.
论文数: 0 引用数: 0
h-index: 0
机构:
Ctr Neurosci & Cell Biol, Coimbra, Portugal
Univ Coimbra, CIBB Ctr Innovat Biomed & Biotechnol, Coimbra, Portugal
Univ Coimbra, Fac Pharm, Coimbra, Portugal Ctr Neurosci & Cell Biol, Coimbra, Portugal
[33]
AAV-based gene therapy prevents neuropathology and results in normal cognitive development in the hyperargininemic mouse
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Lee, E. K.
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Hu, C.
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Novicoff, S.
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Rozengurt, N.
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Marescau, B.
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De Deyn, P.
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Stout, D.
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GENE THERAPY,
2013, 20 (08)
:785-796

Lee, E. K.
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h-index: 0
机构:
Univ Calif Los Angeles, David Geffen Sch Med, Dept Surg, Los Angeles, CA 90095 USA Univ Calif Los Angeles, David Geffen Sch Med, Dept Surg, Los Angeles, CA 90095 USA

Hu, C.
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h-index: 0
机构:
Univ Calif Los Angeles, David Geffen Sch Med, Dept Surg, Los Angeles, CA 90095 USA Univ Calif Los Angeles, David Geffen Sch Med, Dept Surg, Los Angeles, CA 90095 USA

Bhargava, R.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Calif Los Angeles, David Geffen Sch Med, Dept Surg, Los Angeles, CA 90095 USA Univ Calif Los Angeles, David Geffen Sch Med, Dept Surg, Los Angeles, CA 90095 USA

Ponnusamy, R.
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h-index: 0
机构:
Univ Calif Los Angeles, David Geffen Sch Med, Dept Psychol, Los Angeles, CA 90095 USA Univ Calif Los Angeles, David Geffen Sch Med, Dept Surg, Los Angeles, CA 90095 USA

Park, H.
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h-index: 0
机构:
Univ Calif Los Angeles, David Geffen Sch Med, Dept Surg, Los Angeles, CA 90095 USA Univ Calif Los Angeles, David Geffen Sch Med, Dept Surg, Los Angeles, CA 90095 USA

Novicoff, S.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Calif Los Angeles, David Geffen Sch Med, Dept Surg, Los Angeles, CA 90095 USA Univ Calif Los Angeles, David Geffen Sch Med, Dept Surg, Los Angeles, CA 90095 USA

Rozengurt, N.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Calif Los Angeles, David Geffen Sch Med, Dept Pathol & Lab Med, Los Angeles, CA 90095 USA Univ Calif Los Angeles, David Geffen Sch Med, Dept Surg, Los Angeles, CA 90095 USA

Marescau, B.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Antwerp, Lab Neurochem & Behav, B-2020 Antwerp, Belgium
Inst Born Bunge, Antwerp, Belgium Univ Calif Los Angeles, David Geffen Sch Med, Dept Surg, Los Angeles, CA 90095 USA

De Deyn, P.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Antwerp, Lab Neurochem & Behav, B-2020 Antwerp, Belgium
Inst Born Bunge, Antwerp, Belgium Univ Calif Los Angeles, David Geffen Sch Med, Dept Surg, Los Angeles, CA 90095 USA

Stout, D.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Calif Los Angeles, David Geffen Sch Med, Dept Mol & Med Pharmacol, Los Angeles, CA 90095 USA Univ Calif Los Angeles, David Geffen Sch Med, Dept Surg, Los Angeles, CA 90095 USA

Schlichting, L.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Colorado, Biochem Genet Lab, Denver, CO 80202 USA Univ Calif Los Angeles, David Geffen Sch Med, Dept Surg, Los Angeles, CA 90095 USA

Grody, W. W.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Calif Los Angeles, David Geffen Sch Med, Dept Pathol & Lab Med, Los Angeles, CA 90095 USA
Univ Calif Los Angeles, David Geffen Sch Med, Dept Pediat, Los Angeles, CA 90095 USA
Univ Calif Los Angeles, David Geffen Sch Med, Dept Human Genet, Los Angeles, CA 90095 USA Univ Calif Los Angeles, David Geffen Sch Med, Dept Surg, Los Angeles, CA 90095 USA

Cederbaum, S. D.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Calif Los Angeles, David Geffen Sch Med, Dept Pediat, Los Angeles, CA 90095 USA
Univ Calif Los Angeles, David Geffen Sch Med, Dept Human Genet, Los Angeles, CA 90095 USA
Univ Calif Los Angeles, David Geffen Sch Med, Dept Psychiat, Intellectual & Dev Disabil Res Ctr, Los Angeles, CA 90095 USA
Univ Calif Los Angeles, David Geffen Sch Med, Semel Inst Neurosci, Los Angeles, CA 90095 USA Univ Calif Los Angeles, David Geffen Sch Med, Dept Surg, Los Angeles, CA 90095 USA

Lipshutz, G. S.
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h-index: 0
机构:
Univ Calif Los Angeles, David Geffen Sch Med, Dept Surg, Los Angeles, CA 90095 USA
Univ Calif Los Angeles, David Geffen Sch Med, Dept Psychiat, Intellectual & Dev Disabil Res Ctr, Los Angeles, CA 90095 USA
Univ Calif Los Angeles, David Geffen Sch Med, Semel Inst Neurosci, Los Angeles, CA 90095 USA Univ Calif Los Angeles, David Geffen Sch Med, Dept Surg, Los Angeles, CA 90095 USA
[34]
Development and validation of a recovery and purification process for recombinant AAV-based gene therapy vectors.
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Well, JR
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Eith, E
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Giugler, L
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Ta, Angeline
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Locanabio Inc, San Diego, CA USA Locanabio Inc, San Diego, CA USA

Narayan, Nandini
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Angelis, Dimitrios
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Berlin, Aaron
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Locanabio Inc, San Diego, CA USA Locanabio Inc, San Diego, CA USA

Gibbs, Dan
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Zisoulis, Dimitrios
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h-index: 0
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C Hu
论文数: 0 引用数: 0
h-index: 0
机构: David Geffen School of Medicine at University of California,Department of Surgery

R Bhargava
论文数: 0 引用数: 0
h-index: 0
机构: David Geffen School of Medicine at University of California,Department of Surgery

R Ponnusamy
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h-index: 0
机构: David Geffen School of Medicine at University of California,Department of Surgery

H Park
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h-index: 0
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S Novicoff
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N Rozengurt
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B Marescau
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h-index: 0
机构: David Geffen School of Medicine at University of California,Department of Surgery

P De Deyn
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D Stout
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机构: David Geffen School of Medicine at University of California,Department of Surgery

L Schlichting
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h-index: 0
机构: David Geffen School of Medicine at University of California,Department of Surgery

W W Grody
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S D Cederbaum
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G S Lipshutz
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Ma, C.
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Li, C.
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Lian, Q.
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Sechenov Univ, Martsinovsky Inst Med Parasitol Trop & Vector Born, Moscow, Russia Sechenov Univ, Martsinovsky Inst Med Parasitol Trop & Vector Born, Moscow, Russia

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Sechenov Univ, Martsinovsky Inst Med Parasitol Trop & Vector Born, Moscow, Russia Sechenov Univ, Martsinovsky Inst Med Parasitol Trop & Vector Born, Moscow, Russia

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Sechenov Univ, Martsinovsky Inst Med Parasitol Trop & Vector Born, Moscow, Russia
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Leiden Univ, Med Ctr, Human Genet, Leiden, Netherlands UniQure, Amsterdam, Netherlands

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