Optimization of Antisense Oligonucleotide for Skipping Human Dystrophin exon 45, 51 and 53 in Duchenne Muscular Dystrophy Patient-Derived Fibroblasts

被引：0
|
作者：
Wu, Bo [1 ]
Shah, Sapana N. [1 ]
Lu, Peijuan [1 ]
Lavigne, Jenifer L. [1 ]
Sparks, Susan [1 ]
Harper, Amy D. [1 ]
Lu, Qi Long [1 ]
机构：
[1] Carolinas Med Ctr, Charlotte, NC 28203 USA
来源：
MOLECULAR THERAPY | 2017年 / 25卷 / 05期
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暂无
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
257
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页码：121 / 121
页数：1
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