[1] Shinshu Univ Hosp, Intractable Dis Care Ctr, Matsumoto, Nagano, Japan
[2] Shinshu Univ, Sch Med, Dept Med Neurol & Rheumatol, Matsumoto, Nagano, Japan
[3] Shinshu Univ, Inst Biomed Sci, Matsumoto, Nagano, Japan
[4] Univ Alberta, Dept Med Genet, Fac Med & Dent, Sch Human Dev, Edmonton, AB, Canada
[5] NCNP, Natl Inst Neurosci, Dept Mol Therapy, Kodaira, Tokyo, Japan