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Cardiac phenotype determines survival in Duchenne muscular dystrophy
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Birnkrant, David J.
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Ararat, Erhan
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Mhanna, Maroun J.
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PEDIATRIC PULMONOLOGY,
2016, 51 (01)
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Birnkrant, David J.
论文数: 0 引用数: 0
h-index: 0
机构:
Case Western Reserve Univ, Sch Med, Dept Pediat, Metrohlth Med Ctr, Cleveland, OH 44106 USA Case Western Reserve Univ, Sch Med, Dept Pediat, Metrohlth Med Ctr, Cleveland, OH 44106 USA

Ararat, Erhan
论文数: 0 引用数: 0
h-index: 0
机构:
Case Western Reserve Univ, Sch Med, Dept Pediat, Metrohlth Med Ctr, Cleveland, OH 44106 USA Case Western Reserve Univ, Sch Med, Dept Pediat, Metrohlth Med Ctr, Cleveland, OH 44106 USA

Mhanna, Maroun J.
论文数: 0 引用数: 0
h-index: 0
机构:
Case Western Reserve Univ, Sch Med, Dept Pediat, Metrohlth Med Ctr, Cleveland, OH 44106 USA Case Western Reserve Univ, Sch Med, Dept Pediat, Metrohlth Med Ctr, Cleveland, OH 44106 USA
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Bushby, Katharine
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Finkel, Richard
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Wong, Brenda
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Barohn, Richard
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Campbell, Craig
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Comi, Giacomo P.
;
Connolly, Anne M.
;
Day, John W.
;
Flanigan, Kevin M.
;
Goemans, Nathalie
;
Jones, Kristi J.
;
Mercuri, Eugenio
;
Quinlivan, Ros
;
Renfroe, James B.
;
Russman, Barry
;
Ryan, Monique M.
;
Tulinius, Mar
;
Voit, Thomas
;
Moore, Steven A.
;
Sweeney, H. Lee
;
Abresch, Richard T.
;
Coleman, Kim L.
;
Eagle, Michelle
;
Florence, Julaine
;
Gappmaier, Eduard
;
Glanzman, Allan M.
;
Henricson, Erik
;
Barth, Jay
;
Elfring, Gary L.
;
Reha, Allen
;
Spiegel, Robert J.
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O'Donnell, Michael W.
;
Peltz, Stuart W.
;
McDonald, Craig M.
.
MUSCLE & NERVE,
2014, 50 (04)
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Bushby, Katharine
论文数: 0 引用数: 0
h-index: 0
机构:
Newcastle Univ, Inst Genet Med, Newcastle Upon Tyne NE1 7RU, Tyne & Wear, England Newcastle Univ, Inst Genet Med, Newcastle Upon Tyne NE1 7RU, Tyne & Wear, England

Finkel, Richard
论文数: 0 引用数: 0
h-index: 0
机构:
Childrens Hosp Philadelphia, Philadelphia, PA USA Newcastle Univ, Inst Genet Med, Newcastle Upon Tyne NE1 7RU, Tyne & Wear, England

Wong, Brenda
论文数: 0 引用数: 0
h-index: 0
机构:
Cincinnati Childrens Hosp Med Ctr, Cincinnati, OH 45229 USA Newcastle Univ, Inst Genet Med, Newcastle Upon Tyne NE1 7RU, Tyne & Wear, England

Barohn, Richard
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Kansas, Med Ctr, Lawrence, KS 66045 USA Newcastle Univ, Inst Genet Med, Newcastle Upon Tyne NE1 7RU, Tyne & Wear, England

Campbell, Craig
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Western Ontario, London, ON, Canada Newcastle Univ, Inst Genet Med, Newcastle Upon Tyne NE1 7RU, Tyne & Wear, England

Comi, Giacomo P.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Milan, Dino Ferrari Ctr, Dept Neurol Sci, IRCCS Fdn Ca Granda,Osped Maggiore Policlin, Milan, Italy Newcastle Univ, Inst Genet Med, Newcastle Upon Tyne NE1 7RU, Tyne & Wear, England

Connolly, Anne M.
论文数: 0 引用数: 0
h-index: 0
机构:
Washington Univ, Sch Med, St Louis, MO USA Newcastle Univ, Inst Genet Med, Newcastle Upon Tyne NE1 7RU, Tyne & Wear, England

Day, John W.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Minnesota, Minneapolis, MN USA Newcastle Univ, Inst Genet Med, Newcastle Upon Tyne NE1 7RU, Tyne & Wear, England

Flanigan, Kevin M.
论文数: 0 引用数: 0
h-index: 0
机构:
Nationwide Childrens Hosp, Columbus, OH USA
Ohio State Univ, Columbus, OH 43210 USA Newcastle Univ, Inst Genet Med, Newcastle Upon Tyne NE1 7RU, Tyne & Wear, England

Goemans, Nathalie
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Hosp Leuven, Leuven, Belgium Newcastle Univ, Inst Genet Med, Newcastle Upon Tyne NE1 7RU, Tyne & Wear, England

Jones, Kristi J.
论文数: 0 引用数: 0
h-index: 0
机构:
Sydney Childrens Hosp Network, Dept Clin Genet, Sydney, NSW, Australia
Univ Sydney, Discipline Genet, Fac Med, Sydney, NSW 2006, Australia
Univ Sydney, Discipline Paediat & Child Hlth, Fac Med, Sydney, NSW 2006, Australia Newcastle Univ, Inst Genet Med, Newcastle Upon Tyne NE1 7RU, Tyne & Wear, England

Mercuri, Eugenio
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Cattolica Sacro Cuore, Polilcin Gemelli, Pediat Neurol Unit, Rome, Italy Newcastle Univ, Inst Genet Med, Newcastle Upon Tyne NE1 7RU, Tyne & Wear, England

Quinlivan, Ros
论文数: 0 引用数: 0
h-index: 0
机构:
Inst Neurol, London WC1N 3BG, England Newcastle Univ, Inst Genet Med, Newcastle Upon Tyne NE1 7RU, Tyne & Wear, England

Renfroe, James B.
论文数: 0 引用数: 0
h-index: 0
机构:
Northwest Florida Clin Res Grp, Gulf Breeze, FL USA Newcastle Univ, Inst Genet Med, Newcastle Upon Tyne NE1 7RU, Tyne & Wear, England

论文数: 引用数:
h-index:
机构:

Ryan, Monique M.
论文数: 0 引用数: 0
h-index: 0
机构:
Royal Childrens Hosp, Murdoch Childrens Res Inst, Parkville, Vic 3052, Australia
Univ Melbourne, Parkville, Vic 3052, Australia Newcastle Univ, Inst Genet Med, Newcastle Upon Tyne NE1 7RU, Tyne & Wear, England

Tulinius, Mar
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Gothenburg, Dept Pediat, Gothenburg, Sweden Newcastle Univ, Inst Genet Med, Newcastle Upon Tyne NE1 7RU, Tyne & Wear, England

Voit, Thomas
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Paris 06, CNRS, INSERM, UM76,U974,UMR 7215,Inst Myol, Paris, France Newcastle Univ, Inst Genet Med, Newcastle Upon Tyne NE1 7RU, Tyne & Wear, England

Moore, Steven A.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Iowa, Iowa City, IA 52242 USA Newcastle Univ, Inst Genet Med, Newcastle Upon Tyne NE1 7RU, Tyne & Wear, England

Sweeney, H. Lee
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Penn, Philadelphia, PA 19104 USA Newcastle Univ, Inst Genet Med, Newcastle Upon Tyne NE1 7RU, Tyne & Wear, England

Abresch, Richard T.
论文数: 0 引用数: 0
h-index: 0
机构:
UC Davis Childrens Hosp, Lawrence J Ellison Ambulatory Care Ctr, Sacramento, CA 95817 USA Newcastle Univ, Inst Genet Med, Newcastle Upon Tyne NE1 7RU, Tyne & Wear, England

Coleman, Kim L.
论文数: 0 引用数: 0
h-index: 0
机构:
OrthoCare Innovat, Mountlake Terrace, WA USA Newcastle Univ, Inst Genet Med, Newcastle Upon Tyne NE1 7RU, Tyne & Wear, England

Eagle, Michelle
论文数: 0 引用数: 0
h-index: 0
机构:
Newcastle Univ, Inst Genet Med, Newcastle Upon Tyne NE1 7RU, Tyne & Wear, England Newcastle Univ, Inst Genet Med, Newcastle Upon Tyne NE1 7RU, Tyne & Wear, England

Florence, Julaine
论文数: 0 引用数: 0
h-index: 0
机构:
Washington Univ, Sch Med, St Louis, MO USA Newcastle Univ, Inst Genet Med, Newcastle Upon Tyne NE1 7RU, Tyne & Wear, England

Gappmaier, Eduard
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Utah, Sch Med, Salt Lake City, UT USA Newcastle Univ, Inst Genet Med, Newcastle Upon Tyne NE1 7RU, Tyne & Wear, England

Glanzman, Allan M.
论文数: 0 引用数: 0
h-index: 0
机构:
Childrens Hosp Philadelphia, Philadelphia, PA USA Newcastle Univ, Inst Genet Med, Newcastle Upon Tyne NE1 7RU, Tyne & Wear, England

Henricson, Erik
论文数: 0 引用数: 0
h-index: 0
机构:
UC Davis Childrens Hosp, Lawrence J Ellison Ambulatory Care Ctr, Sacramento, CA 95817 USA Newcastle Univ, Inst Genet Med, Newcastle Upon Tyne NE1 7RU, Tyne & Wear, England

Barth, Jay
论文数: 0 引用数: 0
h-index: 0
机构:
PTC Therapeut, South Plainfield, NJ USA Newcastle Univ, Inst Genet Med, Newcastle Upon Tyne NE1 7RU, Tyne & Wear, England

Elfring, Gary L.
论文数: 0 引用数: 0
h-index: 0
机构:
PTC Therapeut, South Plainfield, NJ USA Newcastle Univ, Inst Genet Med, Newcastle Upon Tyne NE1 7RU, Tyne & Wear, England

Reha, Allen
论文数: 0 引用数: 0
h-index: 0
机构:
PTC Therapeut, South Plainfield, NJ USA Newcastle Univ, Inst Genet Med, Newcastle Upon Tyne NE1 7RU, Tyne & Wear, England

Spiegel, Robert J.
论文数: 0 引用数: 0
h-index: 0
机构:
PTC Therapeut, South Plainfield, NJ USA Newcastle Univ, Inst Genet Med, Newcastle Upon Tyne NE1 7RU, Tyne & Wear, England

O'Donnell, Michael W.
论文数: 0 引用数: 0
h-index: 0
机构:
PTC Therapeut, South Plainfield, NJ USA Newcastle Univ, Inst Genet Med, Newcastle Upon Tyne NE1 7RU, Tyne & Wear, England

Peltz, Stuart W.
论文数: 0 引用数: 0
h-index: 0
机构:
PTC Therapeut, South Plainfield, NJ USA Newcastle Univ, Inst Genet Med, Newcastle Upon Tyne NE1 7RU, Tyne & Wear, England

McDonald, Craig M.
论文数: 0 引用数: 0
h-index: 0
机构:
UC Davis Childrens Hosp, Lawrence J Ellison Ambulatory Care Ctr, Sacramento, CA 95817 USA Newcastle Univ, Inst Genet Med, Newcastle Upon Tyne NE1 7RU, Tyne & Wear, England
[5]
Diagnosis and management of Duchenne muscular dystrophy, part 2: implementation of multidisciplinary care
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Bushby, Katharine
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Finkel, Richard
;
Birnkrant, David J.
;
Case, Laura E.
;
Clemens, Paula R.
;
Cripe, Linda
;
Kaul, Ajay
;
Kinnett, Kathi
;
McDonald, Craig
;
Pandya, Shree
;
Poysky, James
;
Shapiro, Frederic
;
Tomezsko, Jean
;
Constantin, Carolyn
.
LANCET NEUROLOGY,
2010, 9 (02)
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Bushby, Katharine
论文数: 0 引用数: 0
h-index: 0
机构:
Newcastle Univ, Inst Human Genet, Int Ctr Life, Newcastle Upon Tyne NE1 3BZ, Tyne & Wear, England Newcastle Univ, Inst Human Genet, Int Ctr Life, Newcastle Upon Tyne NE1 3BZ, Tyne & Wear, England

Finkel, Richard
论文数: 0 引用数: 0
h-index: 0
机构:
Childrens Hosp Philadelphia, Div Neurol, Philadelphia, PA 19104 USA Newcastle Univ, Inst Human Genet, Int Ctr Life, Newcastle Upon Tyne NE1 3BZ, Tyne & Wear, England

Birnkrant, David J.
论文数: 0 引用数: 0
h-index: 0
机构:
Case Western Reserve Univ, Div Pediat Pulm Med, Metrohlth Med Ctr, Cleveland, OH 44106 USA Newcastle Univ, Inst Human Genet, Int Ctr Life, Newcastle Upon Tyne NE1 3BZ, Tyne & Wear, England

Case, Laura E.
论文数: 0 引用数: 0
h-index: 0
机构:
Duke Univ, Div Phys Therapy, Dept Community & Family Med, Durham, NC USA Newcastle Univ, Inst Human Genet, Int Ctr Life, Newcastle Upon Tyne NE1 3BZ, Tyne & Wear, England

Clemens, Paula R.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Pittsburgh, Dept Neurol Mol Genet & Biochem, Pittsburgh, PA USA
Dept Vet Affairs Med Ctr, Pittsburgh, PA USA Newcastle Univ, Inst Human Genet, Int Ctr Life, Newcastle Upon Tyne NE1 3BZ, Tyne & Wear, England

Cripe, Linda
论文数: 0 引用数: 0
h-index: 0
机构:
Cincinnati Childrens Hosp, Med Ctr, Div Cardiol, Cincinnati, OH USA Newcastle Univ, Inst Human Genet, Int Ctr Life, Newcastle Upon Tyne NE1 3BZ, Tyne & Wear, England

Kaul, Ajay
论文数: 0 引用数: 0
h-index: 0
机构:
Cincinnati Childrens Hosp, Med Ctr, Div Pediat Gastroenterol Hepatol & Nutr, Cincinnati, OH USA Newcastle Univ, Inst Human Genet, Int Ctr Life, Newcastle Upon Tyne NE1 3BZ, Tyne & Wear, England

Kinnett, Kathi
论文数: 0 引用数: 0
h-index: 0
机构:
Cincinnati Childrens Hosp, Med Ctr, Div Cardiol, Cincinnati, OH USA Newcastle Univ, Inst Human Genet, Int Ctr Life, Newcastle Upon Tyne NE1 3BZ, Tyne & Wear, England

McDonald, Craig
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Calif Davis, Dept Phys Med & Rehabil, Davis, CA 95616 USA Newcastle Univ, Inst Human Genet, Int Ctr Life, Newcastle Upon Tyne NE1 3BZ, Tyne & Wear, England

Pandya, Shree
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Rochester, Dept Neurol, Rochester, NY USA Newcastle Univ, Inst Human Genet, Int Ctr Life, Newcastle Upon Tyne NE1 3BZ, Tyne & Wear, England

Poysky, James
论文数: 0 引用数: 0
h-index: 0
机构:
Baylor Coll Med, Sch Allied Hlth Sci, Houston, TX 77030 USA Newcastle Univ, Inst Human Genet, Int Ctr Life, Newcastle Upon Tyne NE1 3BZ, Tyne & Wear, England

Shapiro, Frederic
论文数: 0 引用数: 0
h-index: 0
机构:
Childrens Hosp, Dept Orthopaed Surg, Boston, MA 02115 USA Newcastle Univ, Inst Human Genet, Int Ctr Life, Newcastle Upon Tyne NE1 3BZ, Tyne & Wear, England

Tomezsko, Jean
论文数: 0 引用数: 0
h-index: 0
机构:
Childrens Hosp Philadelphia, Div Pulm Med, Philadelphia, PA 19104 USA
Childrens Hosp Philadelphia, Div Gastroenterol, Philadelphia, PA 19104 USA
Childrens Hosp Philadelphia, Div Hepatol, Philadelphia, PA 19104 USA
Childrens Hosp Philadelphia, Div Nutr, Philadelphia, PA 19104 USA Newcastle Univ, Inst Human Genet, Int Ctr Life, Newcastle Upon Tyne NE1 3BZ, Tyne & Wear, England

Constantin, Carolyn
论文数: 0 引用数: 0
h-index: 0
机构:
Ctr Dis Control & Prevent, Natl Ctr Birth Defects & Dev Disabil, Atlanta, GA USA Newcastle Univ, Inst Human Genet, Int Ctr Life, Newcastle Upon Tyne NE1 3BZ, Tyne & Wear, England
[6]
Diagnosis and management of Duchenne muscular dystrophy, part 1: diagnosis, and pharmacological and psychosocial management
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Bushby, Katharine
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Finkel, Richard
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Birnkrant, David J.
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Case, Laura E.
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Clemens, Paula R.
;
Cripe, Linda
;
Kaul, Ajay
;
Kinnett, Kathi
;
McDonald, Craig
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Pandya, Shree
;
Poysky, James
;
Shapiro, Frederic
;
Tomezsko, Jean
;
Constantin, Carolyn
.
LANCET NEUROLOGY,
2010, 9 (01)
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Bushby, Katharine
论文数: 0 引用数: 0
h-index: 0
机构:
Newcastle Univ, Inst Human Genet, Int Ctr Life, Newcastle Upon Tyne NE1 3BZ, Tyne & Wear, England Newcastle Univ, Inst Human Genet, Int Ctr Life, Newcastle Upon Tyne NE1 3BZ, Tyne & Wear, England

Finkel, Richard
论文数: 0 引用数: 0
h-index: 0
机构:
Childrens Hosp Philadelphia, Div Neurol, Philadelphia, PA 19104 USA Newcastle Univ, Inst Human Genet, Int Ctr Life, Newcastle Upon Tyne NE1 3BZ, Tyne & Wear, England

Birnkrant, David J.
论文数: 0 引用数: 0
h-index: 0
机构:
Case Western Reserve Univ, Metrohlth Med Ctr, Div Pediat Pulm Med, Cleveland, OH USA Newcastle Univ, Inst Human Genet, Int Ctr Life, Newcastle Upon Tyne NE1 3BZ, Tyne & Wear, England

Case, Laura E.
论文数: 0 引用数: 0
h-index: 0
机构:
Duke Univ, Dept Community & Family Med, Div Phys Therapy, Durham, NC USA Newcastle Univ, Inst Human Genet, Int Ctr Life, Newcastle Upon Tyne NE1 3BZ, Tyne & Wear, England

Clemens, Paula R.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Pittsburgh, Dept Neurol Mol Genet & Biochem, Pittsburgh, PA USA
Dept Vet Affairs Med Ctr, Pittsburgh, PA USA Newcastle Univ, Inst Human Genet, Int Ctr Life, Newcastle Upon Tyne NE1 3BZ, Tyne & Wear, England

Cripe, Linda
论文数: 0 引用数: 0
h-index: 0
机构:
Cincinnati Childrens Hosp, Med Ctr, Div Cardiol, Cincinnati, OH USA Newcastle Univ, Inst Human Genet, Int Ctr Life, Newcastle Upon Tyne NE1 3BZ, Tyne & Wear, England

Kaul, Ajay
论文数: 0 引用数: 0
h-index: 0
机构:
Cincinnati Childrens Hosp, Med Ctr, Div Pediat Gastroenterol Hepatol & Nutr, Cincinnati, OH USA Newcastle Univ, Inst Human Genet, Int Ctr Life, Newcastle Upon Tyne NE1 3BZ, Tyne & Wear, England

Kinnett, Kathi
论文数: 0 引用数: 0
h-index: 0
机构:
Cincinnati Childrens Hosp, Med Ctr, Div Cardiol, Cincinnati, OH USA Newcastle Univ, Inst Human Genet, Int Ctr Life, Newcastle Upon Tyne NE1 3BZ, Tyne & Wear, England

McDonald, Craig
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Calif Davis, Dept Phys Med & Rehabil, Davis, CA 95616 USA Newcastle Univ, Inst Human Genet, Int Ctr Life, Newcastle Upon Tyne NE1 3BZ, Tyne & Wear, England

Pandya, Shree
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Rochester, Dept Neurol, Rochester, NY USA Newcastle Univ, Inst Human Genet, Int Ctr Life, Newcastle Upon Tyne NE1 3BZ, Tyne & Wear, England

Poysky, James
论文数: 0 引用数: 0
h-index: 0
机构:
Baylor Coll Med, Sch Allied Hlth Sci, Houston, TX 77030 USA Newcastle Univ, Inst Human Genet, Int Ctr Life, Newcastle Upon Tyne NE1 3BZ, Tyne & Wear, England

Shapiro, Frederic
论文数: 0 引用数: 0
h-index: 0
机构:
Childrens Hosp, Dept Orthopaed Surg, Boston, MA 02115 USA Newcastle Univ, Inst Human Genet, Int Ctr Life, Newcastle Upon Tyne NE1 3BZ, Tyne & Wear, England

Tomezsko, Jean
论文数: 0 引用数: 0
h-index: 0
机构:
Childrens Hosp Philadelphia, Div Pulm Med, Philadelphia, PA 19104 USA
Childrens Hosp Philadelphia, Div Gastroenterol Hepatol & Nutr, Philadelphia, PA 19104 USA Newcastle Univ, Inst Human Genet, Int Ctr Life, Newcastle Upon Tyne NE1 3BZ, Tyne & Wear, England

Constantin, Carolyn
论文数: 0 引用数: 0
h-index: 0
机构:
Ctr Dis Control & Prevent, Natl Ctr Birth Defects & Dev Disabil, Atlanta, GA USA Newcastle Univ, Inst Human Genet, Int Ctr Life, Newcastle Upon Tyne NE1 3BZ, Tyne & Wear, England
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Eteplirsen treatment for Duchenne muscular dystrophy Exon skipping and dystrophin production
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Charleston, Jay S.
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Schnell, Frederick J.
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Dworzak, Johannes
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Donoghue, Cas
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Lewis, Sarah
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Chen, Lei
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Young, G. David
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Milici, Anthony J.
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Voss, Jon
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DeAlwis, Uditha
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Wentworth, Bruce
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Rodino-Klapac, Louise R.
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Sahenk, Zarife
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Frank, Diane
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Mendell, Jerry R.
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NEUROLOGY,
2018, 90 (24)
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Charleston, Jay S.
论文数: 0 引用数: 0
h-index: 0
机构:
Sarepta Therapeut Inc, Cambridge, MA 02142 USA Sarepta Therapeut Inc, Cambridge, MA 02142 USA

Schnell, Frederick J.
论文数: 0 引用数: 0
h-index: 0
机构:
Sarepta Therapeut Inc, Cambridge, MA 02142 USA Sarepta Therapeut Inc, Cambridge, MA 02142 USA

Dworzak, Johannes
论文数: 0 引用数: 0
h-index: 0
机构:
Sarepta Therapeut Inc, Cambridge, MA 02142 USA Sarepta Therapeut Inc, Cambridge, MA 02142 USA

Donoghue, Cas
论文数: 0 引用数: 0
h-index: 0
机构:
Sarepta Therapeut Inc, Cambridge, MA 02142 USA Sarepta Therapeut Inc, Cambridge, MA 02142 USA

Lewis, Sarah
论文数: 0 引用数: 0
h-index: 0
机构:
Nationwide Childrens Hosp, Columbus, OH USA Sarepta Therapeut Inc, Cambridge, MA 02142 USA

Chen, Lei
论文数: 0 引用数: 0
h-index: 0
机构:
Nationwide Childrens Hosp, Columbus, OH USA Sarepta Therapeut Inc, Cambridge, MA 02142 USA

Young, G. David
论文数: 0 引用数: 0
h-index: 0
机构:
Flagship Biosci, Westminster, CO USA Sarepta Therapeut Inc, Cambridge, MA 02142 USA

Milici, Anthony J.
论文数: 0 引用数: 0
h-index: 0
机构:
Flagship Biosci, Westminster, CO USA Sarepta Therapeut Inc, Cambridge, MA 02142 USA

Voss, Jon
论文数: 0 引用数: 0
h-index: 0
机构:
Sarepta Therapeut Inc, Cambridge, MA 02142 USA Sarepta Therapeut Inc, Cambridge, MA 02142 USA

DeAlwis, Uditha
论文数: 0 引用数: 0
h-index: 0
机构:
Sarepta Therapeut Inc, Cambridge, MA 02142 USA Sarepta Therapeut Inc, Cambridge, MA 02142 USA

Wentworth, Bruce
论文数: 0 引用数: 0
h-index: 0
机构:
Sarepta Therapeut Inc, Cambridge, MA 02142 USA Sarepta Therapeut Inc, Cambridge, MA 02142 USA

Rodino-Klapac, Louise R.
论文数: 0 引用数: 0
h-index: 0
机构:
Nationwide Childrens Hosp, Columbus, OH USA Sarepta Therapeut Inc, Cambridge, MA 02142 USA

Sahenk, Zarife
论文数: 0 引用数: 0
h-index: 0
机构:
Nationwide Childrens Hosp, Columbus, OH USA Sarepta Therapeut Inc, Cambridge, MA 02142 USA

Frank, Diane
论文数: 0 引用数: 0
h-index: 0
机构:
Sarepta Therapeut Inc, Cambridge, MA 02142 USA Sarepta Therapeut Inc, Cambridge, MA 02142 USA

Mendell, Jerry R.
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h-index: 0
机构:
Nationwide Childrens Hosp, Columbus, OH USA Sarepta Therapeut Inc, Cambridge, MA 02142 USA
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CLINICAL TRIAL READINESS IN NON-AMBULATORY BOYS AND MEN WITH DUCHENNE MUSCULAR DYSTROPHY: MDA-DMD NETWORK FOLLOW-UP
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Connolly, Anne M.
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Mendell, Jerry R.
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Flanigan, Kevin M.
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Karachunski, Peter I.
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Day, John W.
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Mcdonald, Craig M.
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Darras, Basil T.
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Kang, Peter B.
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Siener, Catherine A.
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Gadeken, Rebecca K.
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Anand, Pallavi
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Schierbecker, Jeanine R.
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Malkus, Elizabeth C.
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Lowes, Linda P.
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2016, 54 (04)
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Connolly, Anne M.
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h-index: 0
机构:
Washington Univ, Sch Med, Dept Neurol, St Louis, MO 63110 USA
Washington Univ, Sch Med, Dept Pediat, St Louis, MO 63110 USA Washington Univ, Sch Med, Dept Neurol, St Louis, MO 63110 USA

Florence, Julaine M.
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h-index: 0
机构:
Washington Univ, Sch Med, Dept Neurol, St Louis, MO 63110 USA Washington Univ, Sch Med, Dept Neurol, St Louis, MO 63110 USA

Zaidman, Craig M.
论文数: 0 引用数: 0
h-index: 0
机构:
Washington Univ, Sch Med, Dept Neurol, St Louis, MO 63110 USA
Washington Univ, Sch Med, Dept Pediat, St Louis, MO 63110 USA Washington Univ, Sch Med, Dept Neurol, St Louis, MO 63110 USA

Golumbek, Paul T.
论文数: 0 引用数: 0
h-index: 0
机构:
Washington Univ, Sch Med, Dept Neurol, St Louis, MO 63110 USA
Washington Univ, Sch Med, Dept Pediat, St Louis, MO 63110 USA Washington Univ, Sch Med, Dept Neurol, St Louis, MO 63110 USA

Mendell, Jerry R.
论文数: 0 引用数: 0
h-index: 0
机构:
Ohio State Univ, Dept Pediat, Columbus, OH 43210 USA
Nationwide Childrens Hosp, Ctr Gene Therapy, Columbus, OH USA Washington Univ, Sch Med, Dept Neurol, St Louis, MO 63110 USA

Flanigan, Kevin M.
论文数: 0 引用数: 0
h-index: 0
机构:
Ohio State Univ, Dept Pediat, Columbus, OH 43210 USA
Nationwide Childrens Hosp, Ctr Gene Therapy, Columbus, OH USA Washington Univ, Sch Med, Dept Neurol, St Louis, MO 63110 USA

Karachunski, Peter I.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Minnesota, Dept Neurol, Minneapolis, MN 55455 USA Washington Univ, Sch Med, Dept Neurol, St Louis, MO 63110 USA

Day, John W.
论文数: 0 引用数: 0
h-index: 0
机构:
Stanford Univ, Dept Neurol, Stanford, CA 94305 USA Washington Univ, Sch Med, Dept Neurol, St Louis, MO 63110 USA

Mcdonald, Craig M.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Calif Davis, Med Ctr, Dept Phys Med & Rehabil, Sacramento, CA 95817 USA Washington Univ, Sch Med, Dept Neurol, St Louis, MO 63110 USA

Darras, Basil T.
论文数: 0 引用数: 0
h-index: 0
机构:
Harvard Univ, Boston Childrens Hosp, Dept Neurol, Boston, MA 02115 USA Washington Univ, Sch Med, Dept Neurol, St Louis, MO 63110 USA

Kang, Peter B.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Florida, Coll Med, Div Pediat Neurol, Gainesville, FL USA Washington Univ, Sch Med, Dept Neurol, St Louis, MO 63110 USA

Siener, Catherine A.
论文数: 0 引用数: 0
h-index: 0
机构:
Washington Univ, Sch Med, Dept Neurol, St Louis, MO 63110 USA Washington Univ, Sch Med, Dept Neurol, St Louis, MO 63110 USA

Gadeken, Rebecca K.
论文数: 0 引用数: 0
h-index: 0
机构:
Washington Univ, Sch Med, Dept Neurol, St Louis, MO 63110 USA Washington Univ, Sch Med, Dept Neurol, St Louis, MO 63110 USA

Anand, Pallavi
论文数: 0 引用数: 0
h-index: 0
机构:
Washington Univ, Sch Med, Dept Neurol, St Louis, MO 63110 USA Washington Univ, Sch Med, Dept Neurol, St Louis, MO 63110 USA

Schierbecker, Jeanine R.
论文数: 0 引用数: 0
h-index: 0
机构:
Washington Univ, Sch Med, Dept Neurol, St Louis, MO 63110 USA Washington Univ, Sch Med, Dept Neurol, St Louis, MO 63110 USA

Malkus, Elizabeth C.
论文数: 0 引用数: 0
h-index: 0
机构:
Washington Univ, Sch Med, Dept Neurol, St Louis, MO 63110 USA Washington Univ, Sch Med, Dept Neurol, St Louis, MO 63110 USA

Lowes, Linda P.
论文数: 0 引用数: 0
h-index: 0
机构:
Ohio State Univ, Dept Pediat, Columbus, OH 43210 USA
Nationwide Childrens Hosp, Ctr Gene Therapy, Columbus, OH USA Washington Univ, Sch Med, Dept Neurol, St Louis, MO 63110 USA

Alfano, Lindsay N.
论文数: 0 引用数: 0
h-index: 0
机构:
Ohio State Univ, Dept Pediat, Columbus, OH 43210 USA
Nationwide Childrens Hosp, Ctr Gene Therapy, Columbus, OH USA Washington Univ, Sch Med, Dept Neurol, St Louis, MO 63110 USA

Johnson, Linda
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Calif Davis, Med Ctr, Dept Phys Med & Rehabil, Sacramento, CA 95817 USA Washington Univ, Sch Med, Dept Neurol, St Louis, MO 63110 USA

Nicorici, Alina
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Calif Davis, Med Ctr, Dept Phys Med & Rehabil, Sacramento, CA 95817 USA Washington Univ, Sch Med, Dept Neurol, St Louis, MO 63110 USA

Kelecic, Jason M.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Minnesota, Dept Neurol, Minneapolis, MN 55455 USA Washington Univ, Sch Med, Dept Neurol, St Louis, MO 63110 USA

Quigley, Janet
论文数: 0 引用数: 0
h-index: 0
机构:
Harvard Univ, Boston Childrens Hosp, Dept Neurol, Boston, MA 02115 USA Washington Univ, Sch Med, Dept Neurol, St Louis, MO 63110 USA

Pasternak, Amy E.
论文数: 0 引用数: 0
h-index: 0
机构:
Harvard Univ, Boston Childrens Hosp, Dept Neurol, Boston, MA 02115 USA Washington Univ, Sch Med, Dept Neurol, St Louis, MO 63110 USA

Miller, J. Philip
论文数: 0 引用数: 0
h-index: 0
机构:
Washington Univ, Sch Med, Div Biostat, St Louis, MO 63110 USA Washington Univ, Sch Med, Dept Neurol, St Louis, MO 63110 USA
[9]
OUTCOME RELIABILITY IN NON-AMBULATORY BOYS/MEN WITH DUCHENNE MUSCULAR DYSTROPHY
[J].
Connolly, Anne M.
;
Malkus, Elizabeth C.
;
Mendell, Jerry R.
;
Flanigan, Kevin M.
;
Miller, J. Philip
;
Schierbecker, Jeanine R.
;
Siener, Catherine A.
;
Golumbek, Paul T.
;
Zaidman, Craig M.
;
McDonald, Craig M.
;
Johnson, Linda
;
Nicorici, Alina
;
Karachunski, Peter I.
;
Day, John W.
;
Kelecic, Jason M.
;
Lowes, Linda P.
;
Alfano, Lindsay N.
;
Darras, Basil T.
;
Kang, Peter B.
;
Quigley, Janet
;
Pasternak, Amy E.
;
Florence, Julaine M.
.
MUSCLE & NERVE,
2015, 51 (04)
:522-532

Connolly, Anne M.
论文数: 0 引用数: 0
h-index: 0
机构:
Washington Univ, Sch Med, Dept Neurol, St Louis, MO 63110 USA
Washington Univ, Sch Med, Dept Pediat, St Louis, MO 63110 USA Washington Univ, Sch Med, Dept Neurol, St Louis, MO 63110 USA

Malkus, Elizabeth C.
论文数: 0 引用数: 0
h-index: 0
机构:
Washington Univ, Sch Med, Dept Neurol, St Louis, MO 63110 USA Washington Univ, Sch Med, Dept Neurol, St Louis, MO 63110 USA

Mendell, Jerry R.
论文数: 0 引用数: 0
h-index: 0
机构:
Ohio State Univ, Dept Pediat, Columbus, OH 43210 USA
Nationwide Childrens Hosp, Ctr Gene Therapy, Columbus, OH USA Washington Univ, Sch Med, Dept Neurol, St Louis, MO 63110 USA

Flanigan, Kevin M.
论文数: 0 引用数: 0
h-index: 0
机构:
Ohio State Univ, Dept Pediat, Columbus, OH 43210 USA
Nationwide Childrens Hosp, Ctr Gene Therapy, Columbus, OH USA Washington Univ, Sch Med, Dept Neurol, St Louis, MO 63110 USA

Miller, J. Philip
论文数: 0 引用数: 0
h-index: 0
机构:
Washington Univ, Sch Med, Dept Biostat, St Louis, MO 63110 USA Washington Univ, Sch Med, Dept Neurol, St Louis, MO 63110 USA

Schierbecker, Jeanine R.
论文数: 0 引用数: 0
h-index: 0
机构:
Washington Univ, Sch Med, Dept Neurol, St Louis, MO 63110 USA Washington Univ, Sch Med, Dept Neurol, St Louis, MO 63110 USA

Siener, Catherine A.
论文数: 0 引用数: 0
h-index: 0
机构:
Washington Univ, Sch Med, Dept Neurol, St Louis, MO 63110 USA Washington Univ, Sch Med, Dept Neurol, St Louis, MO 63110 USA

Golumbek, Paul T.
论文数: 0 引用数: 0
h-index: 0
机构:
Washington Univ, Sch Med, Dept Neurol, St Louis, MO 63110 USA
Washington Univ, Sch Med, Dept Pediat, St Louis, MO 63110 USA Washington Univ, Sch Med, Dept Neurol, St Louis, MO 63110 USA

Zaidman, Craig M.
论文数: 0 引用数: 0
h-index: 0
机构:
Washington Univ, Sch Med, Dept Neurol, St Louis, MO 63110 USA
Washington Univ, Sch Med, Dept Pediat, St Louis, MO 63110 USA Washington Univ, Sch Med, Dept Neurol, St Louis, MO 63110 USA

McDonald, Craig M.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Calif Davis, Med Ctr, Dept Phys Med & Rehabil, Sacramento, CA 95817 USA Washington Univ, Sch Med, Dept Neurol, St Louis, MO 63110 USA

Johnson, Linda
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Calif Davis, Med Ctr, Dept Phys Med & Rehabil, Sacramento, CA 95817 USA Washington Univ, Sch Med, Dept Neurol, St Louis, MO 63110 USA

Nicorici, Alina
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Calif Davis, Med Ctr, Dept Phys Med & Rehabil, Sacramento, CA 95817 USA Washington Univ, Sch Med, Dept Neurol, St Louis, MO 63110 USA

Karachunski, Peter I.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Minnesota, Dept Neurol, Minneapolis, MN 55455 USA Washington Univ, Sch Med, Dept Neurol, St Louis, MO 63110 USA

Day, John W.
论文数: 0 引用数: 0
h-index: 0
机构:
Stanford Univ, Dept Neurol, Stanford, CA 94305 USA Washington Univ, Sch Med, Dept Neurol, St Louis, MO 63110 USA

Kelecic, Jason M.
论文数: 0 引用数: 0
h-index: 0
机构:
Stanford Univ, Dept Neurol, Stanford, CA 94305 USA Washington Univ, Sch Med, Dept Neurol, St Louis, MO 63110 USA

Lowes, Linda P.
论文数: 0 引用数: 0
h-index: 0
机构:
Ohio State Univ, Dept Pediat, Columbus, OH 43210 USA
Nationwide Childrens Hosp, Ctr Gene Therapy, Columbus, OH USA Washington Univ, Sch Med, Dept Neurol, St Louis, MO 63110 USA

Alfano, Lindsay N.
论文数: 0 引用数: 0
h-index: 0
机构:
Ohio State Univ, Dept Pediat, Columbus, OH 43210 USA
Nationwide Childrens Hosp, Ctr Gene Therapy, Columbus, OH USA Washington Univ, Sch Med, Dept Neurol, St Louis, MO 63110 USA

Darras, Basil T.
论文数: 0 引用数: 0
h-index: 0
机构:
Harvard Univ, Dept Neurol, Boston Childrens Hosp, Boston, MA 02115 USA Washington Univ, Sch Med, Dept Neurol, St Louis, MO 63110 USA

Kang, Peter B.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Florida, Coll Med, Dept Neurol, Gainesville, FL 32611 USA Washington Univ, Sch Med, Dept Neurol, St Louis, MO 63110 USA

Quigley, Janet
论文数: 0 引用数: 0
h-index: 0
机构:
Harvard Univ, Dept Neurol, Boston Childrens Hosp, Boston, MA 02115 USA Washington Univ, Sch Med, Dept Neurol, St Louis, MO 63110 USA

Pasternak, Amy E.
论文数: 0 引用数: 0
h-index: 0
机构:
Harvard Univ, Dept Neurol, Boston Childrens Hosp, Boston, MA 02115 USA Washington Univ, Sch Med, Dept Neurol, St Louis, MO 63110 USA

Florence, Julaine M.
论文数: 0 引用数: 0
h-index: 0
机构:
Washington Univ, Sch Med, Dept Neurol, St Louis, MO 63110 USA Washington Univ, Sch Med, Dept Neurol, St Louis, MO 63110 USA
[10]
Effect of perindopril on the onset and progression of left ventricular dysfunction in Duchenne muscular dystrophy
[J].
Duboc, D
;
Meune, C
;
Lerebours, G
;
Devaux, JY
;
Vaksmann, G
;
Bécane, HM
.
JOURNAL OF THE AMERICAN COLLEGE OF CARDIOLOGY,
2005, 45 (06)
:855-857

Duboc, D
论文数: 0 引用数: 0
h-index: 0
机构: French Working Grp Heart Involvement Myopethies I, Paris, France

Meune, C
论文数: 0 引用数: 0
h-index: 0
机构: French Working Grp Heart Involvement Myopethies I, Paris, France

Lerebours, G
论文数: 0 引用数: 0
h-index: 0
机构: French Working Grp Heart Involvement Myopethies I, Paris, France

Devaux, JY
论文数: 0 引用数: 0
h-index: 0
机构: French Working Grp Heart Involvement Myopethies I, Paris, France

Vaksmann, G
论文数: 0 引用数: 0
h-index: 0
机构: French Working Grp Heart Involvement Myopethies I, Paris, France

Bécane, HM
论文数: 0 引用数: 0
h-index: 0
机构: French Working Grp Heart Involvement Myopethies I, Paris, France