US HAEA Medical Advisory Board 2020 Guidelines for the Management of Hereditary Angioedema

被引：215

作者：

Busse, Paula J. ^{[1
]}

Christiansen, Sandra C. ^{[2
]}

Riedl, Marc A. ^{[2
]}

Banerji, Aleena ^{[3
]}

Bernstein, Jonathan A. ^{[4
]}

Castaldo, Anthony J. ^{[5
]}

Craig, Timothy ^{[6
]}

Davis-Lorton, Mark ^{[7
]}

Frank, Michael M. ^{[8
]}

Li, H. Henry ^{[9
]}

Lumry, William R. ^{[10
]}

Zuraw, Bruce L. ^{[2
,11
]}

机构：

[1] Mt Sinai Sch Med, Dept Med, Div Rheumatol Allergy & Immunol, New York, NY USA

[2] Univ Calif San Diego, Dept Med, Div Rheumatol Allergy & Immunol, La Jolla, CA 92093 USA

[3] Harvard Med Sch, Dept Med, Div Rheumatol Allergy & Immunol, Boston, MA 02115 USA

[4] Univ Cincinnati, Coll Med, Dept Med, Div Immunol Rheumatol & Allergy, Cincinnati, OH USA

[5] US Hereditary Angioedema Assoc, Fairfax, VA USA

[6] Penn State Univ, Dept Med Pediat & Grad Studies, Div Allergy Asthma & Immunol, Hershey, PA USA

[7] NYU Winthrop Hosp, Dept Med, Div Rheumatol Allergy & Clin Immunol, Mineola, NY USA

[8] Duke Univ, Med Ctr, Dept Pediat, Durham, NC 27710 USA

[9] Inst Asthma & Allergy, Med Serv, Chevy Chase, MD USA

[10] Allergy & Asthma Res Associates Res Ctr, Dallas, TX USA

[11] San Diego Vet Adm Healthcare, San Diego, CA USA

来源：

JOURNAL OF ALLERGY AND CLINICAL IMMUNOLOGY-IN PRACTICE | 2021年 / 9卷 / 01期

关键词：

Hereditary angioedema; C1; inhibitor; Bradykinin; Management; On-demand treatment; Prophylactic treatment; QUALITY-OF-LIFE; C1 INHIBITOR DEFICIENCY; SHORT-TERM PROPHYLAXIS; FACTOR-XII MUTATION; C1-INHIBITOR CONCENTRATE; ESTERASE INHIBITOR; ACUTE ATTACKS; C1-ESTERASE INHIBITOR; ANGIONEUROTIC-EDEMA; DOUBLE-BLIND;

D O I：

10.1016/j.jaip.2020.08.046

中图分类号：

R392 [医学免疫学];

学科分类号：

100102 ;

摘要：

Scientific and clinical progress together with the development of effective novel therapeutic options has engendered multiple important changes in the diagnosis and management of hereditary angioedema (HAE). We now update and extend the 2013 United States Hereditary Angioedema Association Medical Advisory Board guidelines for the treatment and management of HAE. The guidelines are based on a comprehensive literature review with recommendations indicating both the strength of our recommendation and the quality of the underlying evidence. Guidelines are provided regarding the classification, diagnosis, on-demand treatment, prophylactic treatment, special considerations for women and children, development of a comprehensive management and monitoring plan, and assessment of burden of illness for both HAE due to C1 inhibitor deficiency and HAE with normal C1 inhibitor. Advances in HAE treatment now allow the development of management plans that can help many patients with HAE lead a normal life. Achieving this goal requires that physicians be familiar with the diagnostic and therapeutic transformations that have occurred in recent years. Published by Elsevier Inc. on behalf of the American Academy of Allergy, Asthma & Immunology. This is an open access article under the CC BY-NC-ND license.

引用

页码：132 / 150.e3

页数：22

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