Gene Therapy With the DWORF Micropeptide Attenuates Cardiomyopathy in Mice

被引:30
作者
Makarewich, Catherine A. [1 ,2 ]
Bezprozvannaya, Svetlana [3 ,4 ]
Gibson, Aaron M. [1 ]
Bassel-Duby, Rhonda [3 ,4 ]
Olson, Eric N. [3 ,4 ]
机构
[1] Cincinnati Childrens Hosp Med Ctr, Div Mol Cardiovasc Biol, Heart Inst, Cincinnati, OH 45229 USA
[2] Univ Cincinnati, Coll Med, Pediat, Cincinnati, OH 45221 USA
[3] Univ Texas Southwestern Med Ctr, Mol Biol, Dallas, TX USA
[4] Univ Texas Southwestern Med Ctr, Hamon Ctr Regenerat Sci & Med, Dallas, TX USA
基金
美国国家卫生研究院;
关键词
cardiomyopathy; calcium; heart failure; gene deletion; mice;
D O I
10.1161/CIRCRESAHA.120.317156
中图分类号
R5 [内科学];
学科分类号
1002 ; 100201 ;
摘要
引用
收藏
页码:1340 / 1342
页数:3
相关论文
共 5 条
[1]   Modulation of Cardiac Contractility by the Phopholamban/SERCA2a Regulatome [J].
Kranias, Evangelia G. ;
Hajjar, Roger J. .
CIRCULATION RESEARCH, 2012, 110 (12) :1646-1660
[2]   Cardiac-Specific YAP Activation Improves Cardiac Function and Survival in an Experimental Murine MI Model [J].
Lin, Zhiqiang ;
von Gise, Alexander ;
Zhou, Pingzhu ;
Gu, Fei ;
Ma, Qing ;
Jiang, Jianming ;
Yau, Allan L. ;
Buck, Jessica N. ;
Gouin, Katryna A. ;
van Gorp, Pim R. R. ;
Zhou, Bin ;
Chen, Jinghai ;
Seidman, Jonathan G. ;
Wang, Da-Zhi ;
Pu, William T. .
CIRCULATION RESEARCH, 2014, 115 (03) :354-+
[3]   The DWORF micropeptide enhances contractility and prevents heart failure in a mouse model of dilated cardiomyopathy [J].
Makarewich, Catherine A. ;
Munir, Amir Z. ;
Schiattarella, Gabriele G. ;
Bezprozvannaya, Svetlana ;
Raguimova, Olga N. ;
Cho, Ellen E. ;
Vidal, Alexander H. ;
Robia, Seth L. ;
Bassel-Duby, Rhonda ;
Olson, Eric N. .
ELIFE, 2018, 7
[4]   A peptide encoded by a transcript annotated as long noncoding RNA enhances SERCA activity in muscle [J].
Nelson, Benjamin R. ;
Makarewich, Catherine A. ;
Anderson, Douglas M. ;
Winders, Benjamin R. ;
Troupes, Constantine D. ;
Wu, Fenfen ;
Reese, Austin L. ;
McAnally, John R. ;
Chen, Xiongwen ;
Kavalali, Ege T. ;
Cannon, Stephen C. ;
Houser, Steven R. ;
Bassel-Duby, Rhonda ;
Olson, Eric N. .
SCIENCE, 2016, 351 (6270) :271-275
[5]   Randomized Clinical Trials of Gene Transfer for Heart Failure with Reduced Ejection Fraction [J].
Penny, William F. ;
Hammond, H. Kirk .
HUMAN GENE THERAPY, 2017, 28 (05) :378-384