Gene therapy approaches for prevention of retinal degeneration in Usher syndrome

被引：7

作者：

Williams, D. S. ^{[1
,2
,3
]}

Chadha, A. ^{[1
,2
,3
]}

Hazim, R. ^{[1
,2
,3
,4
]}

Gibbs, D. ^{[5
]}

机构：

[1] Univ Calif Los Angeles, Sch Med, Stein Eye Inst, Los Angeles, CA 90095 USA

[2] Univ Calif Los Angeles, Sch Med, Dept Opthalmol, Los Angeles, CA 90095 USA

[3] Univ Calif Los Angeles, Sch Med, Dept Neurobiol, Los Angeles, CA 90095 USA

[4] Univ Calif Los Angeles, Sch Med, Interdepartmental Program Neurosci, Los Angeles, CA 90095 USA

[5] Univ Calif San Diego, Sch Med, Translat Neurosci Inst, Dept Neurosci, La Jolla, CA 92093 USA

来源：

GENE THERAPY | 2017年 / 24卷 / 02期

关键词：

LEBERS CONGENITAL AMAUROSIS; SYNDROME-TYPE-II; MYOSIN VIIA; MOUSE MODEL; RETINITIS-PIGMENTOSA; ADENOASSOCIATED VIRUS; RPE65; MUTATIONS; 1B SYNDROME; DELIVERY; DEAFNESS;

D O I：

10.1038/gt.2016.81

中图分类号：

Q5 [生物化学]; Q7 [分子生物学];

学科分类号：

071010 ; 081704 ;

摘要：

引用

页码：68 / 71

页数：4

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