FIREFISH Part 1: Survival, Ventilation and Swallowing Ability in Infants with Type 1 SMA Receiving Risdiplam (RG7916)

被引：0
|
作者：
Servais, Laurent [1 ,2 ]
Baranello, Giovanni [3 ]
Day, John W. [4 ]
Deconinck, Nicolas [5 ,6 ]
Mercuri, Eugenio [7 ,8 ]
Klein, Andrea [9 ,10 ]
Darras, Basil [11 ]
Masson, Riccardo [3 ]
Kletzl, Heidemarie [12 ]
Cleary, Yumi [12 ]
El-Khairi, Muna [13 ]
Seabrook, Timothy [12 ]
Czech, Christian [12 ]
Gerber, Marianne [12 ]
Nguyen, Coralie [12 ]
Gelblin, Kristina [12 ]
Gorni, Ksenija [12 ]
Khwaja, Omar [12 ]
机构：
[1] Inst Myol, Paris, France
[2] Ctr Hosp Reg Citadelle, Reference Ctr Neuromuscular Dis, Liege, Belgium
[3] Carlo Besta Neurol Res Inst Fdn, Dev Neurol Unit, Milan, Italy
[4] Stanford Univ, Dept Neurol, Palo Alto, CA 94304 USA
[5] Univ Libre Bruxelles, Queen Fabiola Childrens Univ Hosp, Brussels, Belgium
[6] UZ Ghent, Neuromuscular Reference Ctr, Ghent, Belgium
[7] Catholic Univ, Paediat Neurol & Nemo Ctr, Rome, Italy
[8] Policlin Gemelli, Rome, Italy
[9] Univ Childrens Hosp Basel, Basel, Switzerland
[10] Inselspital Bern, Bern, Switzerland
[11] Harvard Med Sch, Boston Childrens Hosp, Boston, MA 02115 USA
[12] Roche Innovat Ctr Basel, Roche Pharmaceut Res & Early Dev, Basel, Switzerland
[13] Roche Prod Ltd, Welwyn Garden City, Herts, England
来源：
NEUROLOGY | 2019年 / 92卷 / 15期
关键词：
D O I：
暂无
中图分类号：
R74 [神经病学与精神病学];
学科分类号：
摘要：
S25.008
引用
收藏
页数：4
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    Servais, L.
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