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- [11] A randomized, double-blind, placebo-controlled trial of coenzyme Q10 in Huntington diseaseNEUROLOGY, 2017, 88 (02) : 152 - 159McGarry, Andrew论文数: 0 引用数: 0 h-index: 0机构: Rowan Univ, Cooper Univ Healthcare, Camden, NJ 08102 USA Rowan Univ, Cooper Univ Healthcare, Camden, NJ 08102 USA论文数: 引用数: h-index:机构:论文数: 引用数: h-index:机构:de Blieck, Elisabeth A.论文数: 0 引用数: 0 h-index: 0机构: Univ Rochester, Rochester, NY 14627 USA Rowan Univ, Cooper Univ Healthcare, Camden, NJ 08102 USABeal, Flint论文数: 0 引用数: 0 h-index: 0机构: Weill Cornell Med Ctr, New York, NY USA Rowan Univ, Cooper Univ Healthcare, Camden, NJ 08102 USAMarder, Karen论文数: 0 引用数: 0 h-index: 0机构: Columbia Presbyterian Med Ctr, New York, NY 10032 USA Rowan Univ, Cooper Univ Healthcare, Camden, NJ 08102 USARoss, Christopher论文数: 0 引用数: 0 h-index: 0机构: Johns Hopkins Med Ctr, Baltimore, MD USA Rowan Univ, Cooper Univ Healthcare, Camden, NJ 08102 USAShoulson, Ira论文数: 0 引用数: 0 h-index: 0机构: Georgetown Univ, Washington, DC USA Rowan Univ, Cooper Univ Healthcare, Camden, NJ 08102 USAGilbert, Peter论文数: 0 引用数: 0 h-index: 0机构: NINDS, Bldg 36,Rm 4D04, Bethesda, MD 20892 USA Rowan Univ, Cooper Univ Healthcare, Camden, NJ 08102 USAMallonee, William M.论文数: 0 引用数: 0 h-index: 0机构: Hereditary Neurol Dis Ctr, Wichita, KS USA Rowan Univ, Cooper Univ Healthcare, Camden, NJ 08102 USAGuttman, Mark论文数: 0 引用数: 0 h-index: 0机构: Ctr Movement Disorders, Toronto, ON, Canada Rowan Univ, Cooper Univ Healthcare, Camden, NJ 08102 USAWojcieszek, Joanne论文数: 0 引用数: 0 h-index: 0机构: Indiana Univ Sch Med, Indianapolis, IN 46202 USA Rowan Univ, Cooper Univ Healthcare, Camden, NJ 08102 USAKumar, Rajeev论文数: 0 引用数: 0 h-index: 0机构: Colorado Neurol Inst, Englewood, CO USA Rowan Univ, Cooper Univ Healthcare, Camden, NJ 08102 USALeDoux, Mark S.论文数: 0 引用数: 0 h-index: 0机构: Univ Tennessee, Ctr Hlth Sci, Memphis, TN 38163 USA Rowan Univ, Cooper Univ Healthcare, Camden, NJ 08102 USAJenkins, Mary论文数: 0 引用数: 0 h-index: 0机构: London Hlth Sci Ctr, London, ON, Canada Rowan Univ, Cooper Univ Healthcare, Camden, NJ 08102 USARosas, H. Diana论文数: 0 引用数: 0 h-index: 0机构: Massachusetts Gen Hosp, Boston, MA 02114 USA Rowan Univ, Cooper Univ Healthcare, Camden, NJ 08102 USANance, Martha论文数: 0 引用数: 0 h-index: 0机构: Struthers Parkinsons Ctr, Minneapolis, MN USA Rowan Univ, Cooper Univ Healthcare, Camden, NJ 08102 USA论文数: 引用数: h-index:机构:Como, Peter论文数: 0 引用数: 0 h-index: 0机构: Univ Rochester, Rochester, NY 14627 USA Rowan Univ, Cooper Univ Healthcare, Camden, NJ 08102 USADubinsky, Richard M.论文数: 0 引用数: 0 h-index: 0机构: Univ Kansas Med Ctr, Kansas City, KS USA Rowan Univ, Cooper Univ Healthcare, Camden, NJ 08102 USAShannon, Kathleen M.论文数: 0 引用数: 0 h-index: 0机构: Rush Univ Med Ctr, Chicago, IL USA Rowan Univ, Cooper Univ Healthcare, Camden, NJ 08102 USAO'Suilleabhain, Padraig论文数: 0 引用数: 0 h-index: 0机构: Univ Texas Southwestern Med Ctr, Dallas, TX USA Rowan Univ, Cooper Univ Healthcare, Camden, NJ 08102 USA论文数: 引用数: h-index:机构:Walker, Francis论文数: 0 引用数: 0 h-index: 0机构: Wake Forest Univ, Winston Salem, NC 27109 USA Rowan Univ, Cooper Univ Healthcare, Camden, NJ 08102 USAMartin, Wayne论文数: 0 引用数: 0 h-index: 0机构: Univ Alberta, Edmonton, AB, Canada Rowan Univ, Cooper Univ Healthcare, Camden, NJ 08102 USAWheelock, Vicki L.论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Davis, Sacramento, CA 95817 USA Rowan Univ, Cooper Univ Healthcare, Camden, NJ 08102 USAMcCusker, Elizabeth论文数: 0 引用数: 0 h-index: 0机构: Westmead Hosp, Westmead, NSW, Australia Rowan Univ, Cooper Univ Healthcare, Camden, NJ 08102 USAJankovic, Joseph论文数: 0 引用数: 0 h-index: 0机构: Baylor Coll Med, Houston, TX 77030 USA Rowan Univ, Cooper Univ Healthcare, Camden, NJ 08102 USASinger, Carlos论文数: 0 引用数: 0 h-index: 0机构: Univ Miami, Miller Sch Med, Coral Gables, FL 33124 USA Rowan Univ, Cooper Univ Healthcare, Camden, NJ 08102 USASanchez-Ramos, Juan论文数: 0 引用数: 0 h-index: 0机构: Univ S Florida, Tampa, FL USA Rowan Univ, Cooper Univ Healthcare, Camden, NJ 08102 USA论文数: 引用数: h-index:机构:Suchowersky, Oksana论文数: 0 引用数: 0 h-index: 0机构: Univ Calgary, Calgary, AB T2N 1N4, Canada Rowan Univ, Cooper Univ Healthcare, Camden, NJ 08102 USAFactor, Stewart A.论文数: 0 引用数: 0 h-index: 0机构: Emory Univ, Sch Med, Atlanta, GA USA Rowan Univ, Cooper Univ Healthcare, Camden, NJ 08102 USAHiggins, Donald S., Jr.论文数: 0 引用数: 0 h-index: 0机构: Albany Med Coll, Albany, NY 12208 USA Rowan Univ, Cooper Univ Healthcare, Camden, NJ 08102 USAMolho, Eric论文数: 0 引用数: 0 h-index: 0机构: Albany Med Coll, Albany, NY 12208 USA Rowan Univ, Cooper Univ Healthcare, Camden, NJ 08102 USARevilla, Fredy论文数: 0 引用数: 0 h-index: 0机构: Univ Cincinnati, Cincinnati, OH 45221 USA Rowan Univ, Cooper Univ Healthcare, Camden, NJ 08102 USACaviness, John N.论文数: 0 引用数: 0 h-index: 0机构: Mayo Clin Arizona, Scottsdale, AZ USA Rowan Univ, Cooper Univ Healthcare, Camden, NJ 08102 USAFriedman, Joseph H.论文数: 0 引用数: 0 h-index: 0机构: Butler Hosp, Providence, RI 02906 USA Rowan Univ, Cooper Univ Healthcare, Camden, NJ 08102 USAPerlmutter, Joel S.论文数: 0 引用数: 0 h-index: 0机构: Washington Univ, St Louis, MO USA Rowan Univ, Cooper Univ Healthcare, Camden, NJ 08102 USAFeigin, Andrew论文数: 0 引用数: 0 h-index: 0机构: Feinstein Inst Med Res, Manhasset, NY USA Rowan Univ, Cooper Univ Healthcare, Camden, NJ 08102 USAAnderson, Karen论文数: 0 引用数: 0 h-index: 0机构: Georgetown Univ, Washington, DC USA Rowan Univ, Cooper Univ Healthcare, Camden, NJ 08102 USARodriguez, Ramon论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Gainesville, FL USA Rowan Univ, Cooper Univ Healthcare, Camden, NJ 08102 USAMcFarland, Nikolaus R.论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Gainesville, FL USA Rowan Univ, Cooper Univ Healthcare, Camden, NJ 08102 USAMargolis, Russell L.论文数: 0 引用数: 0 h-index: 0机构: Johns Hopkins Univ, Baltimore, MD USA Rowan Univ, Cooper Univ Healthcare, Camden, NJ 08102 USAFarbman, Eric S.论文数: 0 引用数: 0 h-index: 0机构: Univ Nevada, Sch Med, Reno, NV 89557 USA Rowan Univ, Cooper Univ Healthcare, Camden, NJ 08102 USARaymond, Lynn A.论文数: 0 引用数: 0 h-index: 0机构: Univ British Columbia, Vancouver, BC, Canada Rowan Univ, Cooper Univ Healthcare, Camden, NJ 08102 USASuski, Valerie论文数: 0 引用数: 0 h-index: 0机构: Univ Pittsburgh, Pittsburgh, PA 15260 USA Rowan Univ, Cooper Univ Healthcare, Camden, NJ 08102 USA论文数: 引用数: h-index:机构:Colcher, Amy论文数: 0 引用数: 0 h-index: 0机构: Cooper Univ Hlth Syst, Camden, NJ USA Rowan Univ, Cooper Univ Healthcare, Camden, NJ 08102 USASeeberger, Lauren论文数: 0 引用数: 0 h-index: 0机构: Idaho Elks Rehabil Hosp, Boise, ID USA Rowan Univ, Cooper Univ Healthcare, Camden, NJ 08102 USA
- [12] Garetosmab in fibrodysplasia ossificans progressiva: a randomized, double-blind, placebo-controlled phase 2 trialNATURE MEDICINE, 2023, 29 (10) : 2615 - +Di Rocco, Maja论文数: 0 引用数: 0 h-index: 0机构: IRCCS Ist Giannina Gaslini, Dept Pediat, Unit Rare Dis, Genoa, Italy IRCCS Ist Giannina Gaslini, Dept Pediat, Unit Rare Dis, Genoa, ItalyForleo-Neto, Eduardo论文数: 0 引用数: 0 h-index: 0机构: Regeneron Pharmaceut, Tarrytown, NY 10591 USA IRCCS Ist Giannina Gaslini, Dept Pediat, Unit Rare Dis, Genoa, ItalyPignolo, Robert J.论文数: 0 引用数: 0 h-index: 0机构: Mayo Clin, Dept Med, Rochester, MN USA IRCCS Ist Giannina Gaslini, Dept Pediat, Unit Rare Dis, Genoa, ItalyKeen, Richard论文数: 0 引用数: 0 h-index: 0机构: Royal Natl Orthopaed Hosp NHS Trust, Ctr Metab Bone Dis, London, England IRCCS Ist Giannina Gaslini, Dept Pediat, Unit Rare Dis, Genoa, Italy论文数: 引用数: h-index:机构:论文数: 引用数: h-index:机构:Roux, Christian论文数: 0 引用数: 0 h-index: 0机构: Cochin Hosp, Assistance Publ Hop Paris, Dept Rheumatol, Paris, France IRCCS Ist Giannina Gaslini, Dept Pediat, Unit Rare Dis, Genoa, ItalyKolta, Sami论文数: 0 引用数: 0 h-index: 0机构: Cochin Hosp, Assistance Publ Hop Paris, Dept Rheumatol, Paris, France IRCCS Ist Giannina Gaslini, Dept Pediat, Unit Rare Dis, Genoa, ItalyMadeo, Annalisa论文数: 0 引用数: 0 h-index: 0机构: IRCCS Ist Giannina Gaslini, Dept Pediat, Unit Rare Dis, Genoa, Italy IRCCS Ist Giannina Gaslini, Dept Pediat, Unit Rare Dis, Genoa, ItalyBubbear, Judith S.论文数: 0 引用数: 0 h-index: 0机构: Royal Natl Orthopaed Hosp NHS Trust, Ctr Metab Bone Dis, London, England IRCCS Ist Giannina Gaslini, Dept Pediat, Unit Rare Dis, Genoa, ItalyTabarkiewicz, Jacek论文数: 0 引用数: 0 h-index: 0机构: Rzeszow Univ, Med Coll, Inst Med Sci, Rzeszow, Poland IRCCS Ist Giannina Gaslini, Dept Pediat, Unit Rare Dis, Genoa, ItalySzczepanek, Malgorzata论文数: 0 引用数: 0 h-index: 0机构: Rzeszow Univ, Med Coll, Inst Med Sci, Rzeszow, Poland IRCCS Ist Giannina Gaslini, Dept Pediat, Unit Rare Dis, Genoa, ItalyBachiller-Corral, Javier论文数: 0 引用数: 0 h-index: 0机构: Hosp Univ Ramon & Cajal, Dept Rheumatol, Madrid, Spain IRCCS Ist Giannina Gaslini, Dept Pediat, Unit Rare Dis, Genoa, ItalyCheung, Angela M.论文数: 0 引用数: 0 h-index: 0机构: Univ Toronto, Univ Hlth Network, Toronto, ON, Canada IRCCS Ist Giannina Gaslini, Dept Pediat, Unit Rare Dis, Genoa, ItalyDahir, Kathryn M.论文数: 0 引用数: 0 h-index: 0机构: Vanderbilt Univ, Med Ctr, Program Metab Bone Disorders, Nashville, TN USA IRCCS Ist Giannina Gaslini, Dept Pediat, Unit Rare Dis, Genoa, ItalyBotman, Esmee论文数: 0 引用数: 0 h-index: 0机构: Vrije Univ, Amsterdam Univ Med Ctr UMC, Amsterdam UMC Expert Ctr Rare Bone Dis, Dept Endocrinol & Metab, Amsterdam, Netherlands IRCCS Ist Giannina Gaslini, Dept Pediat, Unit Rare Dis, Genoa, ItalyRaijmakers, Pieter G.论文数: 0 引用数: 0 h-index: 0机构: Vrije Univ, Dept Radiol & Nucl Med, Amsterdam UMC, Amsterdam, Netherlands IRCCS Ist Giannina Gaslini, Dept Pediat, Unit Rare Dis, Genoa, ItalyMukaddam, Mona Al论文数: 0 引用数: 0 h-index: 0机构: Univ Penn, Perelman Sch Med, Dept Orthopaed Med, Philadelphia, PA USA Univ Penn, Perelman Sch Med, Ctr Res FOP & Related Disorders, Philadelphia, PA USA IRCCS Ist Giannina Gaslini, Dept Pediat, Unit Rare Dis, Genoa, ItalyTile, Lianne论文数: 0 引用数: 0 h-index: 0机构: Univ Toronto, Univ Hlth Network, Toronto, ON, Canada IRCCS Ist Giannina Gaslini, Dept Pediat, Unit Rare Dis, Genoa, ItalyPortal-Celhay, Cynthia论文数: 0 引用数: 0 h-index: 0机构: Regeneron Pharmaceut, Tarrytown, NY 10591 USA IRCCS Ist Giannina Gaslini, Dept Pediat, Unit Rare Dis, Genoa, ItalySarkar, Neena论文数: 0 引用数: 0 h-index: 0机构: Regeneron Pharmaceut, Tarrytown, NY 10591 USA IRCCS Ist Giannina Gaslini, Dept Pediat, Unit Rare Dis, Genoa, ItalyHou, Peijie论文数: 0 引用数: 0 h-index: 0机构: Regeneron Pharmaceut, Tarrytown, NY 10591 USA IRCCS Ist Giannina Gaslini, Dept Pediat, Unit Rare Dis, Genoa, ItalyMusser, Bret J.论文数: 0 引用数: 0 h-index: 0机构: Regeneron Pharmaceut, Tarrytown, NY 10591 USA IRCCS Ist Giannina Gaslini, Dept Pediat, Unit Rare Dis, Genoa, ItalyBoyapati, Anita论文数: 0 引用数: 0 h-index: 0机构: Regeneron Pharmaceut, Tarrytown, NY 10591 USA IRCCS Ist Giannina Gaslini, Dept Pediat, Unit Rare Dis, Genoa, ItalyMohammadi, Kusha论文数: 0 引用数: 0 h-index: 0机构: Regeneron Pharmaceut, Tarrytown, NY 10591 USA IRCCS Ist Giannina Gaslini, Dept Pediat, Unit Rare Dis, Genoa, ItalyMellis, Scott J.论文数: 0 引用数: 0 h-index: 0机构: Regeneron Pharmaceut, Tarrytown, NY 10591 USA IRCCS Ist Giannina Gaslini, Dept Pediat, Unit Rare Dis, Genoa, ItalyRankin, Andrew J.论文数: 0 引用数: 0 h-index: 0机构: Regeneron Pharmaceut, Tarrytown, NY 10591 USA IRCCS Ist Giannina Gaslini, Dept Pediat, Unit Rare Dis, Genoa, ItalyEconomides, Aris N.论文数: 0 引用数: 0 h-index: 0机构: Regeneron Pharmaceut, Tarrytown, NY 10591 USA IRCCS Ist Giannina Gaslini, Dept Pediat, Unit Rare Dis, Genoa, ItalyTrotter, Dinko Gonzalez论文数: 0 引用数: 0 h-index: 0机构: Regeneron Pharmaceut, Tarrytown, NY 10591 USA IRCCS Ist Giannina Gaslini, Dept Pediat, Unit Rare Dis, Genoa, ItalyHerman, Gary A.论文数: 0 引用数: 0 h-index: 0机构: Regeneron Pharmaceut, Tarrytown, NY 10591 USA IRCCS Ist Giannina Gaslini, Dept Pediat, Unit Rare Dis, Genoa, ItalyO'Meara, Sarah J.论文数: 0 引用数: 0 h-index: 0机构: Regeneron Pharmaceut, Tarrytown, NY 10591 USA IRCCS Ist Giannina Gaslini, Dept Pediat, Unit Rare Dis, Genoa, ItalyDelgizzi, Richard论文数: 0 引用数: 0 h-index: 0机构: Regeneron Pharmaceut, Tarrytown, NY 10591 USA IRCCS Ist Giannina Gaslini, Dept Pediat, Unit Rare Dis, Genoa, ItalyWeinreich, David M.论文数: 0 引用数: 0 h-index: 0机构: Regeneron Pharmaceut, Tarrytown, NY 10591 USA IRCCS Ist Giannina Gaslini, Dept Pediat, Unit Rare Dis, Genoa, ItalyYancopoulos, George D.论文数: 0 引用数: 0 h-index: 0机构: Regeneron Pharmaceut, Tarrytown, NY 10591 USA IRCCS Ist Giannina Gaslini, Dept Pediat, Unit Rare Dis, Genoa, ItalyEekhoff, E. Marelise W.论文数: 0 引用数: 0 h-index: 0机构: Vrije Univ, Amsterdam Univ Med Ctr UMC, Amsterdam UMC Expert Ctr Rare Bone Dis, Dept Endocrinol & Metab, Amsterdam, Netherlands IRCCS Ist Giannina Gaslini, Dept Pediat, Unit Rare Dis, Genoa, ItalyKaplan, Frederick S.论文数: 0 引用数: 0 h-index: 0机构: Univ Penn, Perelman Sch Med, Dept Orthopaed Med, Philadelphia, PA USA Univ Penn, Perelman Sch Med, Ctr Res FOP & Related Disorders, Philadelphia, PA USA IRCCS Ist Giannina Gaslini, Dept Pediat, Unit Rare Dis, Genoa, Italy
- [13] Serlopitant for psoriatic pruritus: A phase 2 randomized, double-blind, placebo-controlled clinical trialJOURNAL OF THE AMERICAN ACADEMY OF DERMATOLOGY, 2020, 82 (06) : 1314 - 1320Pariser, David M.论文数: 0 引用数: 0 h-index: 0机构: Eastern Virginia Med Sch, Dept Dermatol, Norfolk, VA 23501 USA Virginia Clin Res Inc, Norfolk, VA USA Eastern Virginia Med Sch, Dept Dermatol, Norfolk, VA 23501 USABagel, Jerry论文数: 0 引用数: 0 h-index: 0机构: Psoriasis Treatment Ctr Cent New Jersey, East Windsor, NJ USA Eastern Virginia Med Sch, Dept Dermatol, Norfolk, VA 23501 USALebwohl, Mark论文数: 0 引用数: 0 h-index: 0机构: Icahn Sch Med Mt Sinai, Dept Dermatol, New York, NY 10029 USA Eastern Virginia Med Sch, Dept Dermatol, Norfolk, VA 23501 USAYosipovitch, Gil论文数: 0 引用数: 0 h-index: 0机构: Univ Miami, Miller Sch Med, Dept Dermatol, Miami Itch Ctr, Miami, FL 33136 USA Eastern Virginia Med Sch, Dept Dermatol, Norfolk, VA 23501 USAChien, Elaine论文数: 0 引用数: 0 h-index: 0机构: Eastern Virginia Med Sch, Dept Dermatol, Norfolk, VA 23501 USASpellman, Mary C.论文数: 0 引用数: 0 h-index: 0机构: Menlo Therapeut Inc, Redwood City, CA USA Eastern Virginia Med Sch, Dept Dermatol, Norfolk, VA 23501 USA
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