共 22 条
[11]
Don't edit the human germ line
[J].
Lanphier, Edward
;
Urnov, Fyodor
;
Haecker, Sarah Ehlen
;
Werner, Michael
;
Smolenski, Joanna
.
NATURE,
2015, 519 (7544)
:410-411

Lanphier, Edward
论文数: 0 引用数: 0
h-index: 0
机构:
Sangamo BioSci, Richmond, CA 94804 USA
Alliance Regenerat Med, Washington, DC USA Sangamo BioSci, Richmond, CA 94804 USA

Urnov, Fyodor
论文数: 0 引用数: 0
h-index: 0
机构:
Sangamo BioSci, Richmond, CA 94804 USA Sangamo BioSci, Richmond, CA 94804 USA

Haecker, Sarah Ehlen
论文数: 0 引用数: 0
h-index: 0
机构:
Alliance Regenerat Med, Technol Sect, Washington, DC USA Sangamo BioSci, Richmond, CA 94804 USA

Werner, Michael
论文数: 0 引用数: 0
h-index: 0
机构:
Alliance Regenerat Med, Washington, DC USA Sangamo BioSci, Richmond, CA 94804 USA

Smolenski, Joanna
论文数: 0 引用数: 0
h-index: 0
机构:
CUNY, Grad Ctr, Philosophy, New York, NY USA Sangamo BioSci, Richmond, CA 94804 USA
[12]
Efficient genetic manipulation of the NOD-Rag1-/-IL2RgammaC-null mouse by combining in vitro fertilization and CRISPR/Cas9 technology
[J].
Li, Feng
;
Cowley, Dale O.
;
Banner, Debra
;
Holle, Eric
;
Zhang, Liguo
;
Su, Lishan
.
SCIENTIFIC REPORTS,
2014, 4

Li, Feng
论文数: 0 引用数: 0
h-index: 0
机构:
Univ N Carolina, Lineberger Comprehens Canc Ctr, Dept Microbiol & Immunol, Chapel Hill, NC 27599 USA Univ N Carolina, Lineberger Comprehens Canc Ctr, Dept Microbiol & Immunol, Chapel Hill, NC 27599 USA

Cowley, Dale O.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ N Carolina, Anim Models Core Facil, Chapel Hill, NC 27599 USA
TransViragen Inc, Res Triangle Pk, NC 27709 USA Univ N Carolina, Lineberger Comprehens Canc Ctr, Dept Microbiol & Immunol, Chapel Hill, NC 27599 USA

Banner, Debra
论文数: 0 引用数: 0
h-index: 0
机构:
TransViragen Inc, Res Triangle Pk, NC 27709 USA Univ N Carolina, Lineberger Comprehens Canc Ctr, Dept Microbiol & Immunol, Chapel Hill, NC 27599 USA

Holle, Eric
论文数: 0 引用数: 0
h-index: 0
机构:
Univ N Carolina, Anim Models Core Facil, Chapel Hill, NC 27599 USA Univ N Carolina, Lineberger Comprehens Canc Ctr, Dept Microbiol & Immunol, Chapel Hill, NC 27599 USA

Zhang, Liguo
论文数: 0 引用数: 0
h-index: 0
机构:
Chinese Acad Sci, Inst Biophys, Key Lab Infect & Immun, Beijing 100101, Peoples R China Univ N Carolina, Lineberger Comprehens Canc Ctr, Dept Microbiol & Immunol, Chapel Hill, NC 27599 USA

Su, Lishan
论文数: 0 引用数: 0
h-index: 0
机构:
Univ N Carolina, Lineberger Comprehens Canc Ctr, Dept Microbiol & Immunol, Chapel Hill, NC 27599 USA
Chinese Acad Sci, Inst Biophys, Key Lab Infect & Immun, Beijing 100101, Peoples R China
Jilin Univ, Hosp 1, Dept Translat Med, Dept Surg, Changchun 130061, Peoples R China Univ N Carolina, Lineberger Comprehens Canc Ctr, Dept Microbiol & Immunol, Chapel Hill, NC 27599 USA
[13]
CRISPR/Cas9-mediated gene editing in human tripronuclear zygotes
[J].
Liang, Puping
;
Xu, Yanwen
;
Zhang, Xiya
;
Ding, Chenhui
;
Huang, Rui
;
Zhang, Zhen
;
Lv, Jie
;
Xie, Xiaowei
;
Chen, Yuxi
;
Li, Yujing
;
Sun, Ying
;
Bai, Yaofu
;
Songyang, Zhou
;
Ma, Wenbin
;
Zhou, Canquan
;
Huang, Junjiu
.
PROTEIN & CELL,
2015, 6 (05)
:363-372

Liang, Puping
论文数: 0 引用数: 0
h-index: 0
机构: Sun Yat Sen Univ, Affiliated Hosp 1, Guangdong Prov Key Lab Reprod Med, Guangzhou 510275, Guangdong, Peoples R China

Xu, Yanwen
论文数: 0 引用数: 0
h-index: 0
机构: Sun Yat Sen Univ, Affiliated Hosp 1, Guangdong Prov Key Lab Reprod Med, Guangzhou 510275, Guangdong, Peoples R China

Zhang, Xiya
论文数: 0 引用数: 0
h-index: 0
机构: Sun Yat Sen Univ, Affiliated Hosp 1, Guangdong Prov Key Lab Reprod Med, Guangzhou 510275, Guangdong, Peoples R China

Ding, Chenhui
论文数: 0 引用数: 0
h-index: 0
机构: Sun Yat Sen Univ, Affiliated Hosp 1, Guangdong Prov Key Lab Reprod Med, Guangzhou 510275, Guangdong, Peoples R China

Huang, Rui
论文数: 0 引用数: 0
h-index: 0
机构: Sun Yat Sen Univ, Affiliated Hosp 1, Guangdong Prov Key Lab Reprod Med, Guangzhou 510275, Guangdong, Peoples R China

Zhang, Zhen
论文数: 0 引用数: 0
h-index: 0
机构: Sun Yat Sen Univ, Affiliated Hosp 1, Guangdong Prov Key Lab Reprod Med, Guangzhou 510275, Guangdong, Peoples R China

Lv, Jie
论文数: 0 引用数: 0
h-index: 0
机构: Sun Yat Sen Univ, Affiliated Hosp 1, Guangdong Prov Key Lab Reprod Med, Guangzhou 510275, Guangdong, Peoples R China

Xie, Xiaowei
论文数: 0 引用数: 0
h-index: 0
机构: Sun Yat Sen Univ, Affiliated Hosp 1, Guangdong Prov Key Lab Reprod Med, Guangzhou 510275, Guangdong, Peoples R China

Chen, Yuxi
论文数: 0 引用数: 0
h-index: 0
机构: Sun Yat Sen Univ, Affiliated Hosp 1, Guangdong Prov Key Lab Reprod Med, Guangzhou 510275, Guangdong, Peoples R China

Li, Yujing
论文数: 0 引用数: 0
h-index: 0
机构: Sun Yat Sen Univ, Affiliated Hosp 1, Guangdong Prov Key Lab Reprod Med, Guangzhou 510275, Guangdong, Peoples R China

Sun, Ying
论文数: 0 引用数: 0
h-index: 0
机构: Sun Yat Sen Univ, Affiliated Hosp 1, Guangdong Prov Key Lab Reprod Med, Guangzhou 510275, Guangdong, Peoples R China

Bai, Yaofu
论文数: 0 引用数: 0
h-index: 0
机构: Sun Yat Sen Univ, Affiliated Hosp 1, Guangdong Prov Key Lab Reprod Med, Guangzhou 510275, Guangdong, Peoples R China

Songyang, Zhou
论文数: 0 引用数: 0
h-index: 0
机构: Sun Yat Sen Univ, Affiliated Hosp 1, Guangdong Prov Key Lab Reprod Med, Guangzhou 510275, Guangdong, Peoples R China

Ma, Wenbin
论文数: 0 引用数: 0
h-index: 0
机构: Sun Yat Sen Univ, Affiliated Hosp 1, Guangdong Prov Key Lab Reprod Med, Guangzhou 510275, Guangdong, Peoples R China

Zhou, Canquan
论文数: 0 引用数: 0
h-index: 0
机构:
Sun Yat Sen Univ, Affiliated Hosp 1, Guangdong Prov Key Lab Reprod Med, Guangzhou 510275, Guangdong, Peoples R China Sun Yat Sen Univ, Affiliated Hosp 1, Guangdong Prov Key Lab Reprod Med, Guangzhou 510275, Guangdong, Peoples R China

Huang, Junjiu
论文数: 0 引用数: 0
h-index: 0
机构: Sun Yat Sen Univ, Affiliated Hosp 1, Guangdong Prov Key Lab Reprod Med, Guangzhou 510275, Guangdong, Peoples R China
[14]
Heritable Multiplex Genetic Engineering in Rats Using CRISPR/Cas9
[J].
Ma, Yuanwu
;
Shen, Bin
;
Zhang, Xu
;
Lu, Yingdong
;
Chen, Wei
;
Ma, Jing
;
Huang, Xingxu
;
Zhang, Lianfeng
.
PLOS ONE,
2014, 9 (03)

Ma, Yuanwu
论文数: 0 引用数: 0
h-index: 0
机构:
Chinese Acad Med Sci, Inst Lab Anim Sci, Minist Hlth, Key Lab Human Dis Comparat Med, Beijing 100730, Peoples R China Chinese Acad Med Sci, Inst Lab Anim Sci, Minist Hlth, Key Lab Human Dis Comparat Med, Beijing 100730, Peoples R China

Shen, Bin
论文数: 0 引用数: 0
h-index: 0
机构:
Nanjing Univ, Nanjing Biomed Res Inst, Key Lab Model Anim Dis Study, MOE,Model Anim Res Ctr,Natl Resource Ctr Mutant M, Nanjing, Jiangsu, Peoples R China Chinese Acad Med Sci, Inst Lab Anim Sci, Minist Hlth, Key Lab Human Dis Comparat Med, Beijing 100730, Peoples R China

Zhang, Xu
论文数: 0 引用数: 0
h-index: 0
机构:
Chinese Acad Med Sci, Inst Lab Anim Sci, Minist Hlth, Key Lab Human Dis Comparat Med, Beijing 100730, Peoples R China Chinese Acad Med Sci, Inst Lab Anim Sci, Minist Hlth, Key Lab Human Dis Comparat Med, Beijing 100730, Peoples R China

Lu, Yingdong
论文数: 0 引用数: 0
h-index: 0
机构:
Chinese Acad Med Sci, Inst Lab Anim Sci, Minist Hlth, Key Lab Human Dis Comparat Med, Beijing 100730, Peoples R China Chinese Acad Med Sci, Inst Lab Anim Sci, Minist Hlth, Key Lab Human Dis Comparat Med, Beijing 100730, Peoples R China

Chen, Wei
论文数: 0 引用数: 0
h-index: 0
机构:
Chinese Acad Med Sci, Inst Lab Anim Sci, Minist Hlth, Key Lab Human Dis Comparat Med, Beijing 100730, Peoples R China Chinese Acad Med Sci, Inst Lab Anim Sci, Minist Hlth, Key Lab Human Dis Comparat Med, Beijing 100730, Peoples R China

Ma, Jing
论文数: 0 引用数: 0
h-index: 0
机构:
Chinese Acad Med Sci, Inst Lab Anim Sci, Minist Hlth, Key Lab Human Dis Comparat Med, Beijing 100730, Peoples R China Chinese Acad Med Sci, Inst Lab Anim Sci, Minist Hlth, Key Lab Human Dis Comparat Med, Beijing 100730, Peoples R China

Huang, Xingxu
论文数: 0 引用数: 0
h-index: 0
机构:
Nanjing Univ, Nanjing Biomed Res Inst, Key Lab Model Anim Dis Study, MOE,Model Anim Res Ctr,Natl Resource Ctr Mutant M, Nanjing, Jiangsu, Peoples R China Chinese Acad Med Sci, Inst Lab Anim Sci, Minist Hlth, Key Lab Human Dis Comparat Med, Beijing 100730, Peoples R China

Zhang, Lianfeng
论文数: 0 引用数: 0
h-index: 0
机构:
Chinese Acad Med Sci, Inst Lab Anim Sci, Minist Hlth, Key Lab Human Dis Comparat Med, Beijing 100730, Peoples R China Chinese Acad Med Sci, Inst Lab Anim Sci, Minist Hlth, Key Lab Human Dis Comparat Med, Beijing 100730, Peoples R China
[15]
CAS9 transcriptional activators for target specificity screening and paired nickases for cooperative genome engineering
[J].
Mali, Prashant
;
Aach, John
;
Stranges, P. Benjamin
;
Esvelt, Kevin M.
;
Moosburner, Mark
;
Kosuri, Sriram
;
Yang, Luhan
;
Church, George M.
.
NATURE BIOTECHNOLOGY,
2013, 31 (09)
:833-+

Mali, Prashant
论文数: 0 引用数: 0
h-index: 0
机构:
Harvard Univ, Sch Med, Dept Genet, Boston, MA 02114 USA Harvard Univ, Sch Med, Dept Genet, Boston, MA 02114 USA

Aach, John
论文数: 0 引用数: 0
h-index: 0
机构:
Harvard Univ, Sch Med, Dept Genet, Boston, MA 02114 USA Harvard Univ, Sch Med, Dept Genet, Boston, MA 02114 USA

Stranges, P. Benjamin
论文数: 0 引用数: 0
h-index: 0
机构:
Harvard Univ, Sch Med, Dept Genet, Boston, MA 02114 USA Harvard Univ, Sch Med, Dept Genet, Boston, MA 02114 USA

Esvelt, Kevin M.
论文数: 0 引用数: 0
h-index: 0
机构:
Harvard Univ, Wyss Inst Biol Inspired Engn, Cambridge, MA 02138 USA Harvard Univ, Sch Med, Dept Genet, Boston, MA 02114 USA

Moosburner, Mark
论文数: 0 引用数: 0
h-index: 0
机构:
Harvard Univ, Sch Med, Dept Genet, Boston, MA 02114 USA Harvard Univ, Sch Med, Dept Genet, Boston, MA 02114 USA

Kosuri, Sriram
论文数: 0 引用数: 0
h-index: 0
机构:
Harvard Univ, Wyss Inst Biol Inspired Engn, Cambridge, MA 02138 USA Harvard Univ, Sch Med, Dept Genet, Boston, MA 02114 USA

Yang, Luhan
论文数: 0 引用数: 0
h-index: 0
机构:
Harvard Univ, Sch Med, Biol & Biomed Sci Program, Boston, MA USA Harvard Univ, Sch Med, Dept Genet, Boston, MA 02114 USA

Church, George M.
论文数: 0 引用数: 0
h-index: 0
机构:
Harvard Univ, Sch Med, Dept Genet, Boston, MA 02114 USA
Harvard Univ, Wyss Inst Biol Inspired Engn, Cambridge, MA 02138 USA Harvard Univ, Sch Med, Dept Genet, Boston, MA 02114 USA
[16]
Double Nicking by RNA-Guided CRISPR Cas9 for Enhanced Genome Editing Specificity
[J].
Ran, F. Ann
;
Hsu, Patrick D.
;
Lin, Chie-Yu
;
Gootenberg, Jonathan S.
;
Konermann, Silvana
;
Trevino, Alexandro E.
;
Scott, David A.
;
Inoue, Azusa
;
Matoba, Shogo
;
Zhang, Yi
;
Zhang, Feng
.
CELL,
2013, 154 (06)
:1380-1389

Ran, F. Ann
论文数: 0 引用数: 0
h-index: 0
机构:
Broad Inst MIT & Harvard, Cambridge Ctr 7, Cambridge, MA 02142 USA
MIT, McGovern Inst Brain Res, Cambridge, MA 02139 USA
MIT, Dept Brain & Cognit Sci, Cambridge, MA 02139 USA
MIT, Dept Biol Engn, Cambridge, MA 02139 USA
Harvard Univ, Dept Mol & Cellular Biol, Cambridge, MA 02138 USA Broad Inst MIT & Harvard, Cambridge Ctr 7, Cambridge, MA 02142 USA

Hsu, Patrick D.
论文数: 0 引用数: 0
h-index: 0
机构:
Broad Inst MIT & Harvard, Cambridge Ctr 7, Cambridge, MA 02142 USA
MIT, McGovern Inst Brain Res, Cambridge, MA 02139 USA
MIT, Dept Brain & Cognit Sci, Cambridge, MA 02139 USA
MIT, Dept Biol Engn, Cambridge, MA 02139 USA
Harvard Univ, Dept Mol & Cellular Biol, Cambridge, MA 02138 USA Broad Inst MIT & Harvard, Cambridge Ctr 7, Cambridge, MA 02142 USA

Lin, Chie-Yu
论文数: 0 引用数: 0
h-index: 0
机构:
Broad Inst MIT & Harvard, Cambridge Ctr 7, Cambridge, MA 02142 USA
MIT, McGovern Inst Brain Res, Cambridge, MA 02139 USA
MIT, Dept Brain & Cognit Sci, Cambridge, MA 02139 USA
MIT, Dept Biol Engn, Cambridge, MA 02139 USA
Harvard Univ, Sch Med, Harvard MIT Div Hlth Sci & Technol, Boston, MA 02115 USA Broad Inst MIT & Harvard, Cambridge Ctr 7, Cambridge, MA 02142 USA

Gootenberg, Jonathan S.
论文数: 0 引用数: 0
h-index: 0
机构:
Broad Inst MIT & Harvard, Cambridge Ctr 7, Cambridge, MA 02142 USA
MIT, McGovern Inst Brain Res, Cambridge, MA 02139 USA
MIT, Dept Brain & Cognit Sci, Cambridge, MA 02139 USA
MIT, Dept Biol Engn, Cambridge, MA 02139 USA Broad Inst MIT & Harvard, Cambridge Ctr 7, Cambridge, MA 02142 USA

Konermann, Silvana
论文数: 0 引用数: 0
h-index: 0
机构:
Broad Inst MIT & Harvard, Cambridge Ctr 7, Cambridge, MA 02142 USA
MIT, McGovern Inst Brain Res, Cambridge, MA 02139 USA
MIT, Dept Brain & Cognit Sci, Cambridge, MA 02139 USA
MIT, Dept Biol Engn, Cambridge, MA 02139 USA Broad Inst MIT & Harvard, Cambridge Ctr 7, Cambridge, MA 02142 USA

Trevino, Alexandro E.
论文数: 0 引用数: 0
h-index: 0
机构:
Broad Inst MIT & Harvard, Cambridge Ctr 7, Cambridge, MA 02142 USA Broad Inst MIT & Harvard, Cambridge Ctr 7, Cambridge, MA 02142 USA

Scott, David A.
论文数: 0 引用数: 0
h-index: 0
机构:
Broad Inst MIT & Harvard, Cambridge Ctr 7, Cambridge, MA 02142 USA
MIT, McGovern Inst Brain Res, Cambridge, MA 02139 USA
MIT, Dept Brain & Cognit Sci, Cambridge, MA 02139 USA
MIT, Dept Biol Engn, Cambridge, MA 02139 USA Broad Inst MIT & Harvard, Cambridge Ctr 7, Cambridge, MA 02142 USA

Inoue, Azusa
论文数: 0 引用数: 0
h-index: 0
机构:
Harvard Univ, Sch Med, Howard Hughes Med Inst, Boston, MA 02115 USA
Harvard Univ, Sch Med, Program Cellular & Mol Med, Boston, MA 02115 USA
Harvard Univ, Sch Med, Dept Genet, Boston, MA 02115 USA
Harvard Univ, Sch Med, Harvard Stem Cell Inst, Boston, MA 02115 USA Broad Inst MIT & Harvard, Cambridge Ctr 7, Cambridge, MA 02142 USA

Matoba, Shogo
论文数: 0 引用数: 0
h-index: 0
机构:
Harvard Univ, Sch Med, Howard Hughes Med Inst, Boston, MA 02115 USA
Harvard Univ, Sch Med, Program Cellular & Mol Med, Boston, MA 02115 USA
Harvard Univ, Sch Med, Dept Genet, Boston, MA 02115 USA
Harvard Univ, Sch Med, Harvard Stem Cell Inst, Boston, MA 02115 USA Broad Inst MIT & Harvard, Cambridge Ctr 7, Cambridge, MA 02142 USA

Zhang, Yi
论文数: 0 引用数: 0
h-index: 0
机构:
Harvard Univ, Sch Med, Howard Hughes Med Inst, Boston, MA 02115 USA
Harvard Univ, Sch Med, Program Cellular & Mol Med, Boston, MA 02115 USA
Harvard Univ, Sch Med, Dept Genet, Boston, MA 02115 USA
Harvard Univ, Sch Med, Harvard Stem Cell Inst, Boston, MA 02115 USA Broad Inst MIT & Harvard, Cambridge Ctr 7, Cambridge, MA 02142 USA

Zhang, Feng
论文数: 0 引用数: 0
h-index: 0
机构:
Broad Inst MIT & Harvard, Cambridge Ctr 7, Cambridge, MA 02142 USA
MIT, McGovern Inst Brain Res, Cambridge, MA 02139 USA
MIT, Dept Brain & Cognit Sci, Cambridge, MA 02139 USA
MIT, Dept Biol Engn, Cambridge, MA 02139 USA Broad Inst MIT & Harvard, Cambridge Ctr 7, Cambridge, MA 02142 USA
[17]
In vivo genome editing of the albumin locus as a platform for protein replacement therapy
[J].
Sharma, Rajiv
;
Anguela, Xavier M.
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Doyon, Yannick
;
Wechsler, Thomas
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DeKelver, Russell C.
;
Sproul, Scott
;
Paschon, David E.
;
Miller, Jeffrey C.
;
Davidson, Robert J.
;
Shivak, David
;
Zhou, Shangzhen
;
Rieders, Julianne
;
Gregory, Philip D.
;
Holmes, Michael C.
;
Rebar, Edward J.
;
High, Katherine A.
.
BLOOD,
2015, 126 (15)
:1777-1784

Sharma, Rajiv
论文数: 0 引用数: 0
h-index: 0
机构:
Childrens Hosp Philadelphia, Div Hematol, Philadelphia, PA 19104 USA Childrens Hosp Philadelphia, Div Hematol, Philadelphia, PA 19104 USA

Anguela, Xavier M.
论文数: 0 引用数: 0
h-index: 0
机构:
Childrens Hosp Philadelphia, Div Hematol, Philadelphia, PA 19104 USA
Howard Hughes Med Inst, Philadelphia, PA USA Childrens Hosp Philadelphia, Div Hematol, Philadelphia, PA 19104 USA

Doyon, Yannick
论文数: 0 引用数: 0
h-index: 0
机构:
Sangamo BioSci, Richmond, CA USA Childrens Hosp Philadelphia, Div Hematol, Philadelphia, PA 19104 USA

Wechsler, Thomas
论文数: 0 引用数: 0
h-index: 0
机构:
Sangamo BioSci, Richmond, CA USA Childrens Hosp Philadelphia, Div Hematol, Philadelphia, PA 19104 USA

DeKelver, Russell C.
论文数: 0 引用数: 0
h-index: 0
机构:
Sangamo BioSci, Richmond, CA USA Childrens Hosp Philadelphia, Div Hematol, Philadelphia, PA 19104 USA

Sproul, Scott
论文数: 0 引用数: 0
h-index: 0
机构:
Sangamo BioSci, Richmond, CA USA Childrens Hosp Philadelphia, Div Hematol, Philadelphia, PA 19104 USA

Paschon, David E.
论文数: 0 引用数: 0
h-index: 0
机构:
Sangamo BioSci, Richmond, CA USA Childrens Hosp Philadelphia, Div Hematol, Philadelphia, PA 19104 USA

Miller, Jeffrey C.
论文数: 0 引用数: 0
h-index: 0
机构:
Sangamo BioSci, Richmond, CA USA Childrens Hosp Philadelphia, Div Hematol, Philadelphia, PA 19104 USA

Davidson, Robert J.
论文数: 0 引用数: 0
h-index: 0
机构:
Childrens Hosp Philadelphia, Div Hematol, Philadelphia, PA 19104 USA Childrens Hosp Philadelphia, Div Hematol, Philadelphia, PA 19104 USA

Shivak, David
论文数: 0 引用数: 0
h-index: 0
机构:
Sangamo BioSci, Richmond, CA USA Childrens Hosp Philadelphia, Div Hematol, Philadelphia, PA 19104 USA

Zhou, Shangzhen
论文数: 0 引用数: 0
h-index: 0
机构:
Childrens Hosp Philadelphia, Div Hematol, Philadelphia, PA 19104 USA Childrens Hosp Philadelphia, Div Hematol, Philadelphia, PA 19104 USA

Rieders, Julianne
论文数: 0 引用数: 0
h-index: 0
机构:
Childrens Hosp Philadelphia, Div Hematol, Philadelphia, PA 19104 USA Childrens Hosp Philadelphia, Div Hematol, Philadelphia, PA 19104 USA

Gregory, Philip D.
论文数: 0 引用数: 0
h-index: 0
机构:
Sangamo BioSci, Richmond, CA USA Childrens Hosp Philadelphia, Div Hematol, Philadelphia, PA 19104 USA

Holmes, Michael C.
论文数: 0 引用数: 0
h-index: 0
机构:
Sangamo BioSci, Richmond, CA USA Childrens Hosp Philadelphia, Div Hematol, Philadelphia, PA 19104 USA

Rebar, Edward J.
论文数: 0 引用数: 0
h-index: 0
机构:
Sangamo BioSci, Richmond, CA USA Childrens Hosp Philadelphia, Div Hematol, Philadelphia, PA 19104 USA

High, Katherine A.
论文数: 0 引用数: 0
h-index: 0
机构:
Childrens Hosp Philadelphia, Div Hematol, Philadelphia, PA 19104 USA
Howard Hughes Med Inst, Philadelphia, PA USA Childrens Hosp Philadelphia, Div Hematol, Philadelphia, PA 19104 USA
[18]
Rationally engineered Cas9 nucleases with improved specificity
[J].
Slaymaker, Ian M.
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Gao, Linyi
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Zetsche, Bernd
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Scott, David A.
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Yan, Winston X.
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Zhang, Feng
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SCIENCE,
2016, 351 (6268)
:84-88

Slaymaker, Ian M.
论文数: 0 引用数: 0
h-index: 0
机构:
Broad Inst MIT & Harvard, Cambridge, MA 02142 USA
MIT, McGovern Inst Brain Res, Cambridge, MA 02139 USA
MIT, Dept Brain & Cognit Sci, Cambridge, MA 02139 USA
MIT, Dept Biol Engn, Cambridge, MA 02139 USA Broad Inst MIT & Harvard, Cambridge, MA 02142 USA

Gao, Linyi
论文数: 0 引用数: 0
h-index: 0
机构:
Broad Inst MIT & Harvard, Cambridge, MA 02142 USA
MIT, Dept Biol Engn, Cambridge, MA 02139 USA Broad Inst MIT & Harvard, Cambridge, MA 02142 USA

Zetsche, Bernd
论文数: 0 引用数: 0
h-index: 0
机构:
Broad Inst MIT & Harvard, Cambridge, MA 02142 USA
MIT, McGovern Inst Brain Res, Cambridge, MA 02139 USA
MIT, Dept Brain & Cognit Sci, Cambridge, MA 02139 USA
MIT, Dept Biol Engn, Cambridge, MA 02139 USA Broad Inst MIT & Harvard, Cambridge, MA 02142 USA

Scott, David A.
论文数: 0 引用数: 0
h-index: 0
机构:
Broad Inst MIT & Harvard, Cambridge, MA 02142 USA
MIT, McGovern Inst Brain Res, Cambridge, MA 02139 USA
MIT, Dept Brain & Cognit Sci, Cambridge, MA 02139 USA
MIT, Dept Biol Engn, Cambridge, MA 02139 USA Broad Inst MIT & Harvard, Cambridge, MA 02142 USA

Yan, Winston X.
论文数: 0 引用数: 0
h-index: 0
机构:
Broad Inst MIT & Harvard, Cambridge, MA 02142 USA
Harvard Univ, Sch Med, Grad Program Biophys, Boston, MA 02115 USA
Harvard Univ, Sch Med, Harvard MIT Div Hlth Sci & Technol, Boston, MA 02115 USA Broad Inst MIT & Harvard, Cambridge, MA 02142 USA

Zhang, Feng
论文数: 0 引用数: 0
h-index: 0
机构:
Broad Inst MIT & Harvard, Cambridge, MA 02142 USA
MIT, McGovern Inst Brain Res, Cambridge, MA 02139 USA
MIT, Dept Brain & Cognit Sci, Cambridge, MA 02139 USA
MIT, Dept Biol Engn, Cambridge, MA 02139 USA Broad Inst MIT & Harvard, Cambridge, MA 02142 USA
[19]
Gene Editing of CCR5 in Autologous CD4 T Cells of Persons Infected with HIV
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Tebas, Pablo
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Stein, David
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Tang, Winson W.
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Frank, Ian
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Wang, Shelley Q.
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Lee, Gary
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Spratt, S. Kaye
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Surosky, Richard T.
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Giedlin, Martin A.
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Nichol, Geoff
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Holmes, Michael C.
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Gregory, Philip D.
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Ando, Dale G.
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Kalos, Michael
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Collman, Ronald G.
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Binder-Scholl, Gwendolyn
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Plesa, Gabriela
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Hwang, Wei-Ting
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Levine, Bruce L.
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June, Carl H.
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NEW ENGLAND JOURNAL OF MEDICINE,
2014, 370 (10)
:901-910

Tebas, Pablo
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Penn, Perelman Sch Med, Philadelphia, PA 19104 USA Univ Penn, Perelman Sch Med, Philadelphia, PA 19104 USA

Stein, David
论文数: 0 引用数: 0
h-index: 0
机构:
Albert Einstein Coll Med, Bronx, NY 10467 USA Univ Penn, Perelman Sch Med, Philadelphia, PA 19104 USA

Tang, Winson W.
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h-index: 0
机构:
Sangamo BioSci, Richmond, CA USA Univ Penn, Perelman Sch Med, Philadelphia, PA 19104 USA

Frank, Ian
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h-index: 0
机构:
Univ Penn, Perelman Sch Med, Philadelphia, PA 19104 USA Univ Penn, Perelman Sch Med, Philadelphia, PA 19104 USA

Wang, Shelley Q.
论文数: 0 引用数: 0
h-index: 0
机构:
Sangamo BioSci, Richmond, CA USA Univ Penn, Perelman Sch Med, Philadelphia, PA 19104 USA

Lee, Gary
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h-index: 0
机构:
Sangamo BioSci, Richmond, CA USA Univ Penn, Perelman Sch Med, Philadelphia, PA 19104 USA

Spratt, S. Kaye
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h-index: 0
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Sangamo BioSci, Richmond, CA USA Univ Penn, Perelman Sch Med, Philadelphia, PA 19104 USA

Surosky, Richard T.
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Sangamo BioSci, Richmond, CA USA Univ Penn, Perelman Sch Med, Philadelphia, PA 19104 USA

Giedlin, Martin A.
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h-index: 0
机构:
Sangamo BioSci, Richmond, CA USA Univ Penn, Perelman Sch Med, Philadelphia, PA 19104 USA

Nichol, Geoff
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h-index: 0
机构:
Sangamo BioSci, Richmond, CA USA Univ Penn, Perelman Sch Med, Philadelphia, PA 19104 USA

Holmes, Michael C.
论文数: 0 引用数: 0
h-index: 0
机构:
Sangamo BioSci, Richmond, CA USA Univ Penn, Perelman Sch Med, Philadelphia, PA 19104 USA

Gregory, Philip D.
论文数: 0 引用数: 0
h-index: 0
机构:
Sangamo BioSci, Richmond, CA USA Univ Penn, Perelman Sch Med, Philadelphia, PA 19104 USA

Ando, Dale G.
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h-index: 0
机构:
Sangamo BioSci, Richmond, CA USA Univ Penn, Perelman Sch Med, Philadelphia, PA 19104 USA

Kalos, Michael
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h-index: 0
机构:
Univ Penn, Perelman Sch Med, Philadelphia, PA 19104 USA Univ Penn, Perelman Sch Med, Philadelphia, PA 19104 USA

Collman, Ronald G.
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h-index: 0
机构:
Univ Penn, Perelman Sch Med, Philadelphia, PA 19104 USA Univ Penn, Perelman Sch Med, Philadelphia, PA 19104 USA

Binder-Scholl, Gwendolyn
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Univ Penn, Perelman Sch Med, Philadelphia, PA 19104 USA Univ Penn, Perelman Sch Med, Philadelphia, PA 19104 USA

Plesa, Gabriela
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Univ Penn, Perelman Sch Med, Philadelphia, PA 19104 USA Univ Penn, Perelman Sch Med, Philadelphia, PA 19104 USA

Hwang, Wei-Ting
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Univ Penn, Perelman Sch Med, Philadelphia, PA 19104 USA Univ Penn, Perelman Sch Med, Philadelphia, PA 19104 USA

Levine, Bruce L.
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Univ Penn, Perelman Sch Med, Philadelphia, PA 19104 USA Univ Penn, Perelman Sch Med, Philadelphia, PA 19104 USA

June, Carl H.
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Univ Penn, Perelman Sch Med, Philadelphia, PA 19104 USA Univ Penn, Perelman Sch Med, Philadelphia, PA 19104 USA
[20]
The National Academies of Sciences Engineering and Medicine, 2015, AC CONS STUD HUM GEN