AAV-mediated gene therapy restores retinal function and vision in the RPGRIP1-deficient dog

被引：0
|
作者：
Petit, Lolita [1 ]
Lheriteau, Elsa [1 ]
Weber, Michel [2 ]
Le Meur, Guylene [2 ]
Deschamps, Jack-Yves [3 ]
Moullier, Philippe [1 ,4 ]
Rolling, Fabienne [1 ]
机构：
[1] INSERM, UMR 1089, Lab Therapie Genique, Inst Rech Therapeut 1, Nantes, France
[2] CHU Hotel Dieu, Serv Opthalmol, Nantes, France
[3] Nantes Atlantic Coll Vet Med Food Sci & Engn, ONIRIS, Emergency & Crit Care Unit, Nantes, France
[4] Univ Florida, Coll Med, Dept Mol Genet & Microbiol, Gainesville, FL USA
来源：
INVESTIGATIVE OPHTHALMOLOGY & VISUAL SCIENCE | 2013年 / 54卷 / 15期
关键词：
538 gene transfer/gene therapy; 688; retina; 648; photoreceptors;
D O I：
暂无
中图分类号：
R77 [眼科学];
学科分类号：
100212 ;
摘要：
5968
引用
收藏
页数：2
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