Non-viral DNA delivery associated to TALEN® gene editing leads to highly efficient correction of sickle cell mutation in long-term repopulating hematopoietic stem cells

被引：0

作者：

Moiani, A. ^{[1
]}

Letort, G. ^{[1
]}

Lizot, S. ^{[1
]}

Hong, P. ^{[1
]}

Temburni-Blake, S. ^{[1
]}

Felix, T. ^{[2
]}

Chalumeau, A. ^{[2
]}

Miccio, A. ^{[2
]}

Gouble, A. ^{[1
]}

Juillerat, A. ^{[1
]}

Duclert, A. ^{[1
]}

Duchateau, P. ^{[1
]}

Valton, J. ^{[1
]}

机构：

[1] Cellectis Therapeut, Paris, France

[2] Imagine Inst, Paris, France

来源：

HUMAN GENE THERAPY | 2022年 / 33卷 / 23-24期

关键词：

D O I：

暂无

中图分类号：

Q81 [生物工程学（生物技术）]; Q93 [微生物学];

学科分类号：

071005 ; 0836 ; 090102 ; 100705 ;

摘要：

OR46

引用

页码：A17 / A17

页数：1

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